NCT06588478

Brief Summary

The main purpose of Part 1 of this study is to assess the efficacy and safety of 3 dose levels of Pirtobrutinib in participants with chronic lymphocytic leukemia (CLL) or small lymphocytic lymphoma (SLL), who have received 1-3 lines of treatment including a covalent Bruton tyrosine kinase (BTK) inhibitor. The purpose of Part 2 of this study is to evaluate pirtobrutinib monotherapy in participants with treatment-naïve CLL/SLL with 17p deletions. Participation in Part 1 is expected to last approximately 3 years. Participation in Part 2 is expected to last up to 2 years.

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
249

participants targeted

Target at P75+ for phase_2

Timeline
32mo left

Started Jan 2025

Typical duration for phase_2

Geographic Reach
18 countries

133 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress34%
Jan 2025Dec 2028

First Submitted

Initial submission to the registry

September 6, 2024

Completed
13 days until next milestone

First Posted

Study publicly available on registry

September 19, 2024

Completed
4 months until next milestone

Study Start

First participant enrolled

January 3, 2025

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2028

Expected
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2028

Last Updated

March 24, 2026

Status Verified

March 1, 2026

Enrollment Period

3.4 years

First QC Date

September 6, 2024

Last Update Submit

March 22, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate

    Overall response rate is defined as the proportion of participants who achieve the best overall response at or before the initiation of subsequent anticancer therapy of CR, CRi, nPR, or PR. ORR will be assessed using International Workshop on Chronic Lymphocytic Leukemia (iwCLL) 2018 response criteria.

    Baseline up to 3 years

Secondary Outcomes (1)

  • Duration of Response

    Baseline up to 3 years

Study Arms (4)

Pirtobrutinib Standard Dose (Dose 1)-Part 1

ACTIVE COMPARATOR

Pirtobrutinib administered orally.

Drug: Pirtobrutinib

Pirtobrutinib Dose 2-Part 1

EXPERIMENTAL

Pirtobrutinib administered orally.

Drug: Pirtobrutinib

Pirtobrutinib Dose 3-Part 1

EXPERIMENTAL

Pirtobrutinib administered orally.

Drug: Pirtobrutinib

Pirtobrutinib Standard Dose-Part 2

EXPERIMENTAL

Pirtobrutinib administered orally.

Drug: Pirtobrutinib

Interventions

Administered Orally.

Pirtobrutinib Dose 2-Part 1Pirtobrutinib Dose 3-Part 1Pirtobrutinib Standard Dose (Dose 1)-Part 1Pirtobrutinib Standard Dose-Part 2

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have confirmed diagnosis of CLL/SLL as defined by iwCLL 2018 criteria.
  • Part 1: Have received prior CLL/SLL treatment
  • Have received at least 1, but not more than 3 lines of prior treatment for CLL/SLL
  • Have received a covalent BTK inhibitor
  • Part 2: Have received no prior treatment for CLL/SLL
  • Part 1 - Known 17p deletion status (positive or negative)
  • Part 2 - Must have 17p deletion (positive)
  • Have a requirement for therapy consistent with iwCLL 2018 criteria for initiation of therapy
  • Capable of swallowing oral study medication.
  • Have an Eastern Cooperative Oncology Group Performance Status (ECOG) score of 0 to 2.

You may not qualify if:

  • Have received prior treatment with a BTK degrader or a noncovalent BTK inhibitor
  • Have a history of greater than or equal to (\>=) Grade 3 bleeding due to treatment with a BTK inhibitor
  • Have known or suspected Richter's transformation
  • Have known or suspected history of central nervous system involvement by CLL/SLL
  • Previous or concurrent cancer distinct from CLL/SLL within 3 years before randomization. Exceptions may occur with documented sponsor approval. Examples include:
  • nonmelanoma skin cancer or lentigo malignant melanoma
  • cervical carcinoma in situ
  • localized prostate cancer undergoing active surveillance, and
  • localized (for example, lymph node negative) breast cancer with no evidence of active disease present for more than 3 years. Individual may be receiving adjuvant hormonal therapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (133)

Ironwood Cancer & Research Centers

Chandler, Arizona, 85224, United States

RECRUITING

City of Hope National Medical Center

Duarte, California, 91010, United States

RECRUITING

City of Hope National Medical Center

Irvine, California, 92618, United States

RECRUITING

Palo Alto Medical Foundation Research Institute (PAMFRI)

Palo Alto, California, 94304, United States

RECRUITING

Stanford Cancer Center

Palo Alto, California, 94304, United States

RECRUITING

Rocky Mountain Cancer Center

Aurora, Colorado, 80012, United States

RECRUITING

University of Miami Hospital and Clinics, Sylvester Cancer Center

Miami, Florida, 33136, United States

RECRUITING

City of Hope National Medical Center, Atlanta Cancer Center

Newnan, Georgia, 30265, United States

RECRUITING

Mission Cancer + Blood

Waukee, Iowa, 50263, United States

RECRUITING

Saint Elizabeth Medical Center Edgewood

Edgewood, Kentucky, 41017, United States

RECRUITING

American Oncology Partners, PA

Bethesda, Maryland, 20817, United States

RECRUITING

Boston Medical Center

Boston, Massachusetts, 02118, United States

RECRUITING

Gulfport Memorial Hospital

Gulfport, Mississippi, 39501, United States

RECRUITING

Comprehensive Cancer Centers of Nevada

Henderson, Nevada, 89074, United States

RECRUITING

East Carolina University

Greenville, North Carolina, 27834, United States

RECRUITING

Williamette Valley Cancer Institute & Research Center

Eugene, Oregon, 97401, United States

RECRUITING

Cancer Care Associates Of York

York, Pennsylvania, 17403, United States

RECRUITING

The West Clinic, PLLC dba West Cancer Center

Germantown, Tennessee, 38138, United States

RECRUITING

USO-Texas Oncology-Central/South Texas

Austin, Texas, 78705, United States

RECRUITING

Sarah Cannon Research Institute/SCRI

The Woodlands, Texas, 77380, United States

RECRUITING

USO-Virginia Oncology Associates

Hampton, Virginia, 23666, United States

RECRUITING

Flinders Medical Centre

Adelaide, 5042, Australia

RECRUITING

Bankstown-Lidcombe Hospital

Bankstown, 2200, Australia

RECRUITING

Box Hill Hospital

Box Hill, 3128, Australia

RECRUITING

Coffs Harbour Health Campus

Coffs Harbour, 2450, Australia

RECRUITING

Royal Hobart Hospital

Hobart, 7000, Australia

RECRUITING

ICON Cancer Centre - Kurralta Park

Kurralta Park, 5037, Australia

RECRUITING

Latrobe Regional Health

Traralgon, 3844, Australia

RECRUITING

Calvary Mater Newcastle

Waratah, 2298, Australia

RECRUITING

The Perth Blood Institute - West Perth

West Perth, 6005, Australia

RECRUITING

Princess Alexandra Hospital

Woolloongabba, 4102, Australia

RECRUITING

Institut Jules Bordet

Anderlecht, 1070, Belgium

RECRUITING

AZ Sint-Jan Brugge-Oostende AV

Bruges, 8000, Belgium

RECRUITING

UZ Gent

Ghent, 9000, Belgium

RECRUITING

Groupe Jolimont

La Louvière, 7100, Belgium

RECRUITING

UZ Leuven

Leuven, 3000, Belgium

RECRUITING

Clinique Saint Pierre

Ottignies, 1340, Belgium

RECRUITING

AZ Delta vzw

Roeselare, 8800, Belgium

RECRUITING

AZ Nikolaas

Sint-Niklaas, B-9100, Belgium

RECRUITING

CHR Verviers - La Tourelle

Verviers, 4800, Belgium

RECRUITING

Royal Victoria Regional Health Centre

Barrie, L4M 6M2, Canada

RECRUITING

Saskatoon Cancer Centre

Saskatoon, S7N4H4, Canada

RECRUITING

Fakultní nemocnice Brno Bohunice

Brno, 625 00, Czechia

RECRUITING

Fakultni nemocnice Hradec Kralove

Hradec Králové, 500 05, Czechia

RECRUITING

Fakultni nemocnice Kralovske Vinohrady

Prague, 100 34, Czechia

RECRUITING

Vseobecna fakultni nemocnice v Praze

Prague, 12808, Czechia

RECRUITING

Aarhus Universitetshospital, Skejby

Aarhus, 8200, Denmark

RECRUITING

Odense Universitetshospital

Odense, 5000, Denmark

RECRUITING

Centre Hospitalier d'Argenteuil Victor Dupouy

Argenteuil, 95107, France

RECRUITING

Centre Hospitalier Universitaire de Caen - Hôpital Côte de Nacre

Caen, 14033, France

RECRUITING

Centre Hospitalier du Mans

Le Mans, 72000, France

RECRUITING

Groupe Hospitalier de la Région de Mulhouse et Sud Alsace - Hôpital Emile Muller

Mulhouse, 68100, France

RECRUITING

Centre Antoine-Lacassagne

Nice, 06189, France

RECRUITING

Centre Hospitalier Régional Universitaire de Tours - Hôpital Bretonneau

Tours, 37044 Cedex 9, France

RECRUITING

MV-Zentrum für Onkologie und Hämatologie

Cologne, 50677, Germany

RECRUITING

Centrum für Hämatologie und Onkologie Bethanien

Frankfurt, 60389, Germany

RECRUITING

OSP Göttingen

Göttingen, 37073, Germany

RECRUITING

Onkologisches Ambulanzzentrum Hannover

Hanover, 30171, Germany

RECRUITING

Klinikum Aschaffenburg-Alzenau

Hösbach, 63768, Germany

RECRUITING

InVO Institut für Versorgungsforschung in der Onkologie

Koblenz, 56068, Germany

RECRUITING

Evangelismos General Hospital of Athens

Athens, 106 76, Greece

RECRUITING

Attikon General University Hospital

Chaïdári, 12462, Greece

RECRUITING

G. Papanikolaou General Hospital

Thessaloniki, 570 10, Greece

RECRUITING

General Hospital of Athens "Laiko"

Αthens, 11526, Greece

RECRUITING

Semmelweis Egyetem

Budapest, 1088, Hungary

RECRUITING

Dél-Pesti Centrumkórház

Budapest, 1097, Hungary

RECRUITING

Pécsi Tudományegyetem Klinikai Központ

Pécs, 7624, Hungary

RECRUITING

Szegedi Tudományegyetem Szent-Györgyi Albert Klinikai Központ

Szeged, 6725, Hungary

RECRUITING

A.O.U.C. Policlinico di Bari

Bari, 70124, Italy

RECRUITING

Azienda Ospedaliero Universitaria S.Anna

Cona, 44124, Italy

RECRUITING

Azienda Ospedaliera Universitaria Careggi

Florence, 50134, Italy

RECRUITING

ASST Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

RECRUITING

Azienda Ospedaliero Universitaria Maggiore della Carità

Novara, 28100, Italy

RECRUITING

Azienda Ospedale - Università Padova

Padua, 35128, Italy

RECRUITING

Az. Osp. Ospedali Riuniti VILLA SOFIA-CERVELLO

Palermo, 90146, Italy

RECRUITING

AO Santa Maria della Misericordia

Perugia, 06132, Italy

RECRUITING

AOU Policlinico Umberto I

Roma, 00161, Italy

RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS - Università Cattolica del Sacro Cuore

Roma, 00168, Italy

RECRUITING

IN VIVO

Bydgoszcz, 85-048, Poland

RECRUITING

Pratia Onkologia Katowice

Katowice, 40-519, Poland

RECRUITING

Pratia MCM Krakow

Krakow, 30-727, Poland

RECRUITING

AIDPORT Sp. z o.o.

Skórzewo, 60-185, Poland

RECRUITING

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wrocławiu

Wroclaw, 50-367, Poland

RECRUITING

Fundeni Clinical Institute

Bucharest, 022328, Romania

RECRUITING

Spitalul Clinic Colțea

Bucharest, 030171, Romania

RECRUITING

Institutul Oncologic Cluj

Cluj-Napoca, 400015, Romania

RECRUITING

Spitalul Clinic Municipal Filantropia Craiova

Craiova, 200143, Romania

RECRUITING

Institutul Regional de Oncologie

Iași, 700483, Romania

RECRUITING

Ovidius Clinical Hospital OCH

Ovidiu, 905900, Romania

RECRUITING

Fakultna nemocnica s poliklinikou F.D.Roosevelta Banska Bystrica

Banská Bystrica, 975 17, Slovakia

RECRUITING

Narodny onkologicky ustav

Bratislava, 833 10, Slovakia

RECRUITING

Univerzitna Nemocnica L. Pasteura Kosice

Košice, 040 11, Slovakia

RECRUITING

Univerzitna nemocnica Martin

Martin, 036 59, Slovakia

RECRUITING

Pusan National University Hospital

Busan, 49241, South Korea

RECRUITING

Chonnam National University Hwasun Hospital

Hwasun-gun, 58128, South Korea

RECRUITING

Seoul National University Hospital

Seoul, 03080, South Korea

RECRUITING

Samsung Medical Center

Seoul, 06351, South Korea

RECRUITING

The Catholic Univ. of Korea Seoul St. Mary's Hospital

Seoul, 06591, South Korea

RECRUITING

The Catholic University of Korea, Yeouido St. Mary's Hospital

Seoul, 07345, South Korea

RECRUITING

Institut Català d'Oncologia (ICO) - Badalona

Badalona, 08916, Spain

RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

RECRUITING

Hospital Clínic de Barcelona

Barcelona, 08036, Spain

RECRUITING

Institut Català d'Oncologia - L'Hospitalet

L'Hospitalet Del Llobregat, 08908, Spain

RECRUITING

Clinica Universidad de Navarra

Madrid, 28027, Spain

RECRUITING

Hospital Universitario Infanta Leonor

Madrid, 28031, Spain

RECRUITING

MD Anderson Cancer Center

Madrid, 28033, Spain

RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

RECRUITING

Hospital Universitario Quironsalud Madrid

Madrid, 28223, Spain

RECRUITING

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, 28222, Spain

RECRUITING

Hospital Costa del Sol

Marbella, 29603, Spain

RECRUITING

Hospital Universitario Central de Asturias

Oviedo, 33011, Spain

RECRUITING

Hospital Universitario de Salamanca - Complejo Asistencial Universitario de Salamanca

Salamanca, 37007, Spain

RECRUITING

Hospital Universitario Marqués de Valdecilla

Santander, 39008, Spain

RECRUITING

Hospital Universitario Virgen Macarena

Seville, 41009, Spain

RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, 41013, Spain

RECRUITING

Sakarya University School of Medicine

Adapazarı, 54100, Turkey (Türkiye)

RECRUITING

Dr. Abdurrahman Yurtaslan Ankara Onkoloji Egitim ve Arastırma Hastanesi

Ankara, 06200, Turkey (Türkiye)

RECRUITING

Ankara University Health Practice and Research Hospitals

Ankara, 06620, Turkey (Türkiye)

RECRUITING

Memorial Antalya Hospital

Antalya, 07090, Turkey (Türkiye)

RECRUITING

Yeditepe Üniversitesi Koşuyolu Hastanesi

Istanbul, 34718, Turkey (Türkiye)

RECRUITING

Ege Universitesi Hastanesi

Izmir, 35100, Turkey (Türkiye)

RECRUITING

Kocaeli Üniversitesi

İzmit, 41380, Turkey (Türkiye)

RECRUITING

VM Medical Park Mersin Hastanesi

Mersin, 33200, Turkey (Türkiye)

RECRUITING

Ondokuz Mayıs Universitesi

Samsun, 55139, Turkey (Türkiye)

RECRUITING

Heartlands Hospital

Birmingham, B9 5SS, United Kingdom

RECRUITING

The Beatson West of Scotland Cancer Centre

Glasgow, G12 0YN, United Kingdom

RECRUITING

Northwick Park Hospital

Harrow, HA1 3UJ, United Kingdom

RECRUITING

St James's University Hospital

Leeds, LS9 7TF, United Kingdom

RECRUITING

Lincoln County Hospital

Lincoln, LN2 5QY, United Kingdom

RECRUITING

Clatterbridge Cancer Centre - Liverpool

Liverpool, L7 8YA, United Kingdom

RECRUITING

Hammersmith Hospital

London, W12 0HS, United Kingdom

RECRUITING

Maidstone Hospital

Maidstone, ME16 9QQ, United Kingdom

RECRUITING

Singleton Hospital

Swansea, SA2 8QA, United Kingdom

RECRUITING

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-Cell

Interventions

pirtobrutinib

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 8 AM - 8 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Central Study Contacts

Trial questions or participation questions: 1-877-CTLILLY (1-877-285-4559) or

CONTACT

Physicians interested in becoming principal investigators please contact

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Masking Details
Part 2 is non-randomized
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 6, 2024

First Posted

September 19, 2024

Study Start

January 3, 2025

Primary Completion (Estimated)

June 1, 2028

Study Completion (Estimated)

December 1, 2028

Last Updated

March 24, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Anonymized individual patient level data will be provided in a secure access environment upon approval of a research proposal and a signed data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Data are available 6 months after the primary publication and approval of the indication studied in the US and EU, whichever is later. Data will be indefinitely available for requesting.
Access Criteria
A research proposal must be approved by an independent review panel and researchers must sign a data sharing agreement.
More information

Locations