NCT06453668

Brief Summary

The purpose of this study is to investigate the safety, pharmacokinetics (PK), and pharmacodynamics (PD) of TCD601 (siplizumab) in newly diagnosed adult ALS patients.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
7

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Apr 2024

Typical duration for phase_1

Geographic Reach
1 country

3 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 16, 2024

Completed
20 days until next milestone

First Submitted

Initial submission to the registry

May 6, 2024

Completed
1 month until next milestone

First Posted

Study publicly available on registry

June 12, 2024

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 2, 2026

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 2, 2026

Completed
Last Updated

July 17, 2026

Status Verified

July 1, 2026

Enrollment Period

2.2 years

First QC Date

May 6, 2024

Last Update Submit

July 16, 2026

Conditions

Keywords

Amyotrophic Lateral SclerosisNeuroinflammatory

Outcome Measures

Primary Outcomes (1)

  • Evaluation of the safety of TCD601 in adult patients with ALS

    Assess the incidence of treatment-emergent Adverse Events \[Safety and Tolerability\]

    12 Months

Secondary Outcomes (7)

  • Evaluation of the pharmacokinetics (PK)

    12 Months

  • Correlation of ALS disease status with leucocyte phenotypic profiles

    12 Months

  • Evaluation of levels of biomarkers

    12 Months

  • Length of time from trial entry to tracheostomy / death

    12 Months

  • Assessment of clinically relevant changes in laboratory measurements

    12 Months

  • +2 more secondary outcomes

Study Arms (1)

Treatment

EXPERIMENTAL

TCD601 (siplizumab) administered with the contemporary standard of care regimen.

Biological: TCD601

Interventions

TCD601BIOLOGICAL

Investigational Product

Also known as: siplizumab
Treatment

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female patients ≥ 18 to 80 years of age.
  • Diagnosis of ALS by revised El Escorial Criteria, at study entry within 24 months of first symptoms.
  • Patients on existing ALS treatment must have been on a stable dose for 28 days.

You may not qualify if:

  • Patient with severe systemic infections, current or within the two weeks prior to randomization.
  • Subjects who, in the opinion of the investigator, are not capable of giving informed consent for the study or who are unable or unwilling to adhere to the study requirements outlined in the protocol.
  • Use of other investigational products or treatment in another investigational drug study within 30 days of screening
  • Pregnant or nursing (lactating) women.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Skåne University Hospital Malmö

Malmö, 205 02, Sweden

Location

Studieenheten Akademiskt Specialistcentrum

Stockholm, 171 77, Sweden

Location

Umeå University Hospital

Umeå, 901 85, Sweden

Location

MeSH Terms

Conditions

Amyotrophic Lateral Sclerosis

Interventions

siplizumab

Condition Hierarchy (Ancestors)

Spinal Cord DiseasesCentral Nervous System DiseasesNervous System DiseasesMotor Neuron DiseaseNeurodegenerative DiseasesTDP-43 ProteinopathiesNeuromuscular DiseasesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic Diseases

Study Officials

  • Fredrik Julin

    ITB-Med LLC

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
BASIC SCIENCE
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 6, 2024

First Posted

June 12, 2024

Study Start

April 16, 2024

Primary Completion

July 2, 2026

Study Completion

July 2, 2026

Last Updated

July 17, 2026

Record last verified: 2026-07

Locations