NCT06408402

Brief Summary

The primary objective of the PGL.EXPO-2 study is to test the hypothesis that exposure (occupational, environmental and/or domestic) to succinate dehydrogenase inhibitors (SDHi) could contribute to tumor emergence in subjects carrying a germline mutation in one of the SDHx genes.The primary endpoint will be the proportion of subjects (cases or controls) exposed to SDHi and the association with paraganglioma risk. In addition, a blood sample (10 ml on EDTA) will be proposed to the participants to the study

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,300

participants targeted

Target at P75+ for all trials

Timeline
24mo left

Started May 2024

Longer than P75 for all trials

Geographic Reach
1 country

20 active sites

Status
not yet recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress50%
May 2024May 2028

First Submitted

Initial submission to the registry

March 27, 2024

Completed
1 month until next milestone

Study Start

First participant enrolled

May 1, 2024

Completed
9 days until next milestone

First Posted

Study publicly available on registry

May 10, 2024

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2028

Last Updated

May 10, 2024

Status Verified

April 1, 2024

Enrollment Period

4 years

First QC Date

March 27, 2024

Last Update Submit

May 6, 2024

Conditions

Keywords

hereditary paragangliomaSDHx gene mutationenvironmental exposure

Outcome Measures

Primary Outcomes (1)

  • Impact of SDHi exposure in paraganglioma occurence

    Association between exposures and tumor occurrence measure with Odd ratio

    36 months

Secondary Outcomes (2)

  • Spatial distribution of cases

    48 months

  • Incidence rate in France of pathologies linked to SDHx gene mutations

    48 months

Study Arms (2)

Cases

Cases: SDHx mutation carriers diagnosed for a SDHx-related tumor

Controls

Controls : SDHx mutation carriers with no SDHx-related tumor

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

650 cases and 650 controls will be enrolled in different French referral centers where they are regularly managed and followed for a SDHx-related tumor risk. They will be matched on their date of birth

You may qualify if:

  • Cases: SDHx mutation carriers diagnosed for a SDHx-related tumor
  • Controls: SDHx mutation carriers with no SDHx-related tumor

You may not qualify if:

  • Incapacity to exercise free and informed consent for the study
  • Patient under tutorship or guardianship or legal safeguard

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

CHU d'Angers

Angers, 49000, France

Location

CHU Jean Minjoz Besançon

Besançon, 25030, France

Location

Hôpital Louis Pradel

Bron, 69677, France

Location

CHU de Caen

Caen, 14033, France

Location

Hôpital Michalon - CHU Grenoble

Grenoble, 38043, France

Location

CHU de Lille - Hôpital HURIEZ

Lille, 59037, France

Location

Hopital de la Conception - Marseille

Marseille, 13385, France

Location

CHU de Montpellier - Hôpital Lapeyronie

Montpellier, 34295, France

Location

CHU de Nantes

Nantes, 44093, France

Location

CHU de Nice -Hôpital Archet 2

Nice, 06202, France

Location

Hôpital Pitié-Salpêtrière - APHP

Paris, 75013, France

Location

Hôpital Cochin - APHP

Paris, 75014, France

Location

Hôpital européen Georges Pompidou - APHP

Paris, 75015, France

Location

Hôpital européen Georges Pompidou - APHP

Paris, 75015, France

Location

CHU de Poitiers

Poitiers, 86021, France

Location

CHU de Rennes - Hôpital Sud

Rennes, 35000, France

Location

Hôpitaux universitaire de Strasbourg - Hôpital de Hautepierre

Strasbourg, 67098, France

Location

CHU de Toulouse - Hôpita Larrey

Toulouse, 31059, France

Location

CHU Bretonneau

Tours, 37000, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Biospecimen

Retention: SAMPLES WITH DNA

A blood sample (10 ml on EDTA) will be proposed to the participants to the study

Study Officials

  • Anne-Paule Gimenez-Roqueplo, MD, PhD

    Hôpital européen Georges Pompidou - APHP

    STUDY DIRECTOR

Central Study Contacts

Alexandre Buffet, MD, PhD

CONTACT

Anne-Paule Gimenez-Roqueplo, MD, PhD

CONTACT

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 27, 2024

First Posted

May 10, 2024

Study Start

May 1, 2024

Primary Completion (Estimated)

May 1, 2028

Study Completion (Estimated)

May 1, 2028

Last Updated

May 10, 2024

Record last verified: 2024-04

Data Sharing

IPD Sharing
Will share

Individual participant data (IPD) that underlie results in publication could be shared. IPD detailed in the protocol of a planned metaanalysis could be shared

Shared Documents
STUDY PROTOCOL
Time Frame
Two years after the last publication
Access Criteria
Data sharing must be accepted by the sponsor and the PI based on a scientific project and scientific involvement of the PI team. Collaboration will be fostered. The founder could be involved in the decision. Teams wishing obtain IPD must meet the sponsor and IP team to present scientifics (and commercial) purpose, IPD needed, format of data transmission, and timeframe. Technical feasibility and financial support will be discussed before mandatory contractualization. Processing of shared data must comply with European General Data Protection Regulation (GDPR).

Locations