NCT06137144

Brief Summary

This study is designed to evaluate the safety, tolerability, PK, pharmacodynamics, and preliminary efficacy following oral administration of AZD3470 as a monotherapy, and in combination with other anticancer agents in participants with haematologic malignancies.

Trial Health

88
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
161

participants targeted

Target at P75+ for phase_1 lymphoma

Timeline
36mo left

Started Jan 2024

Typical duration for phase_1 lymphoma

Geographic Reach
10 countries

33 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress43%
Jan 2024Apr 2029

First Submitted

Initial submission to the registry

November 2, 2023

Completed
16 days until next milestone

First Posted

Study publicly available on registry

November 18, 2023

Completed
2 months until next milestone

Study Start

First participant enrolled

January 23, 2024

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2029

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2029

Last Updated

April 21, 2026

Status Verified

April 1, 2026

Enrollment Period

5.3 years

First QC Date

November 2, 2023

Last Update Submit

April 16, 2026

Conditions

Keywords

Haematologic MalignanciesHodgkin lymphomaPeripheral T-cell lymphoma (PTCL)Methylthioadenosine Phosphorylase (MTAP) deficientProtein Arginine Methyltransferase 5 (PRMT5)

Outcome Measures

Primary Outcomes (2)

  • Incidence and severity of adverse events (AEs) and serious adverse events (SAEs)

    AEs: Number of patients with adverse events by system organ class and preferred term. SAEs: Number of patients with serious adverse events by system organ class and preferred term.

    From Screening continuously until 28 days after the last dose of study medication.

  • Incidence of DLTs (Dose Escalation Cohorts only)

    In the Dose Escalation cohorts in Part A, the number of participants with at least 1 dose-limiting toxicity (DLT), which is any toxicity defined as a DLT in the Clinical Study Protocol.

    From first dose of AZD3470 to end of Cycle 1 (each cycle is 21 days).

Secondary Outcomes (10)

  • Response endpoints as assessed by the investigator according to the Lugano Classification: Objective Response Rate (ORR)/Complete Response Rate (CRR)

    From first dose (Cycle 1 Day 1, each cycle is 21 days) until disease progression or the last evaluable assessment in the absence of progression.

  • Response Endpoints as assessed by investigator according to the Lugano Classification: Conversation rate of Partial Response (PR) to Complete Response (CR)

    From First dose (Cycle 1 Day 1, each cycle is 21 days) until disease progression or the last evaluable assessment in the absence of progression.

  • Response endpoints as assessed by the investigator according to the Lugano Classification: Duration of Response (DoR)

    From date of first objective response until documented progression or death due to any cause or censoring (if progression or death have not occurred)

  • Response endpoints as assessed by the investigator according to the Lugano Classification for CHL: The rate of durable CR

    From date of first complete response until documented progression or death due to any cause or censoring (if progression or death have not occurred)

  • Response Endpoints as assessed by the investigator according to the Lugano Classification: Progression-free Survival (PFS)

    From first dose (each cycle is 21 days)/from randomisation (for non-randomized & randomized study parts respectively) until disease progression or death, or censoring (if progression or death have not occurred) whichever is first

  • +5 more secondary outcomes

Study Arms (2)

AZD3470 Monotherapy

EXPERIMENTAL

Module 1 Cohort 1 evaluates safety, tolerability, efficacy of AZD3470 in r/r cHL participants with 2 prior lines of systemic anticancer therapy (including BV and anti-PD1). Participants will be treated according to protocol-defined windows. Part A (dose escalation) assesses AZD3470 at increasing doses in participants aged ≥18 years, r/r cHL. Part B (dose optimization/ expansion) includes participants at certain dose levels evaluated as tolerable in Part A and may include adolescent patients aged ≥12 years, upon SRC agreement. Module 1 Cohort 2 evaluates the safety, tolerability, efficacy of AZD3470 as consolidation for Stage III/IV cHL participants aged ≥50 years after CR or PR to frontline SOC therapy (either N-AVD, A-AVD, AVD, ABVD) Module 1 Cohort 3 evaluates the safety, tolerability, preliminary efficacy of AZD3470 in participants aged ≥18 years with r/r PTCL (PTCL NOS, ALCL, AITL subtypes) with at least 1 prior line of systemic anticancer therapy.

Drug: AZD3470

AZD3470 in combination with Pembrolizumab

EXPERIMENTAL

Module 2 Cohort 1 will assess participants aged ≥18 years with r/r cHL who have received at least one prior line of anticancer therapy. Participants will receive treatment according to the protocol-defined limit, or until disease progression, unacceptable toxicity as judged by the investigator or until meeting any other discontinuation criteria, as defined in the clinical study protocol, whichever occurs first. Part A (dose escalation) will evaluate the safety and tolerability of AZD3470 in combination with Pembrolizumab. Part B (dose optimization/expansion) will evaluate dose optimization/expansion in certain dose levels of AZD3470 in combination with Pembrolizumab, based on cumulative data from dose escalation part (Part A).

Drug: AZD3470Drug: Pembrolizumab

Interventions

AZD3470 is a novel, potent and selective, second-generation, Methylthioadenosine (MTA)-selective, small molecule inhibitor of PRMT5.

AZD3470 MonotherapyAZD3470 in combination with Pembrolizumab

Pembrolizumab (CAS nr: 1374853-91-4 )

Also known as: Keytruda
AZD3470 in combination with Pembrolizumab

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Adequate adult (ECOG) or adolescent (Karnofsy or Lanksy) Performance Score assessments
  • Adequate organ and bone marrow function.
  • Module 1 Cohort 1:
  • Age:
  • Part A (dose escalation): aged ≥ 18 years at the time of signing the informed consent.
  • Part B (optimization): aged ≥ 12 years of age. Adolescent participants must weigh ≥ 40 kg.
  • Histologically confirmed diagnosis of cHL based on WHO criteria
  • Previous treatment with at least 2 prior lines of therapy for the treatment of cHL (including at least 2 cycles of BV and anti-PD1) and have documented r/r active disease requiring treatment.
  • Participants must provide FFPE baseline tumour tissue.
  • At least 1 radiographically measurable, and/or FDG-avid lymphoma lesion ( \>1.5 cm for nodal lesion and \>1 cm for extranodal lesion).
  • Module 1 Cohort 2:
  • Participants must be at least 50 years of age or older at study entry.
  • Histologically confirmed diagnosis of cHL based on WHO criteria
  • Ann Arbor stages III or IV.
  • Participant must have previously received at least 4 cycles of SoC combination therapy with A-AVD, N-AVD, AVD, or ABVD (based on regional SOC, per investigator) as finite first-line induction therapy, and achieved at least a PR post-induction therapy.
  • +14 more criteria

You may not qualify if:

  • Any significant laboratory finding or any severe and uncontrolled medical condition.
  • Active CNS involvement by lymphoma, leptomeningeal disease, or spinal cord compression.
  • Serologic active HBV or HCV infection.
  • Known to have tested positive for HIV.
  • Active gastrointestinal disease or other condition that will interfere with oral therapy.
  • Any of the following ECG cardiac criteria: Mean resting QTcF \> 470 msec, clinically important abnormalities in rhythm, conduction or morphology, and/or any factors that increase the risk of QTc prolongation or risk of arrhythmic events.
  • Undergone any of the following procedures within 6 months prior to first dose:
  • Coronary artery bypass graft,
  • Percutaneous coronary intervention or heart valve replacement or repairment,
  • Vascular stent implantation (venous stent is eligible),
  • Acute coronary syndrome / myocardial infarction,
  • Unstable or poorly controlled angina pectoris,
  • Ventricular arrhythmias requiring continuous therapy,
  • Uncontrolled atrial fibrillation,
  • Haemorrhagic or thrombotic stroke (including transient ischaemic attacks) or any other CNS bleeding.
  • +20 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (33)

Research Site

Duarte, California, 91010, United States

NOT YET RECRUITING

Research Site

Miami, Florida, 33136, United States

RECRUITING

Research Site

Atlanta, Georgia, 30322, United States

WITHDRAWN

Research Site

Boston, Massachusetts, 02215, United States

RECRUITING

Research Site

New York, New York, 10016, United States

NOT YET RECRUITING

Research Site

Philadelphia, Pennsylvania, 19104, United States

RECRUITING

Research Site

Houston, Texas, 77030, United States

RECRUITING

Research Site

Adelaide, 5000, Australia

WITHDRAWN

Research Site

Fitzroy, 3065, Australia

NOT YET RECRUITING

Research Site

Nedlands, 6009, Australia

RECRUITING

Research Site

South Brisbane, 4101, Australia

WITHDRAWN

Research Site

Waratah, 2298, Australia

WITHDRAWN

Research Site

Beijing, 100191, China

NOT YET RECRUITING

Research Site

Guangzhou, 510060, China

NOT YET RECRUITING

Research Site

Shanghai, 20032, China

NOT YET RECRUITING

Research Site

Créteil, 94010, France

TERMINATED

Research Site

Lille, 59000, France

RECRUITING

Research Site

Pierre-Bénite, 69310, France

RECRUITING

Research Site

Villejuif, 94805, France

RECRUITING

Research Site

Berlin, 12203, Germany

NOT YET RECRUITING

Research Site

Cologne, 50937, Germany

RECRUITING

Research Site

Erlangen, 91054, Germany

NOT YET RECRUITING

Research Site

Würzburg, 97080, Germany

NOT YET RECRUITING

Research Site

Alessandria, 15100, Italy

RECRUITING

Research Site

Bologna, 40138, Italy

RECRUITING

Research Site

Milan, 20141, Italy

RECRUITING

Research Site

Kōtoku, 135-8550, Japan

NOT YET RECRUITING

Research Site

Seoul, 03080, South Korea

RECRUITING

Research Site

Seoul, 06351, South Korea

RECRUITING

Research Site

L'Hospitalet de Llobregat, 08908, Spain

RECRUITING

Research Site

Madrid, 28041, Spain

RECRUITING

Research Site

Manchester, M20 4BX, United Kingdom

RECRUITING

Research Site

Oxford, OX3 7LE, United Kingdom

RECRUITING

MeSH Terms

Conditions

LymphomaLymphoma, Non-HodgkinHodgkin DiseaseLymphoma, T-Cell, Peripheral

Interventions

pembrolizumab

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesLymphoma, T-Cell

Central Study Contacts

AstraZeneca Clinical Study Information Center

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 2, 2023

First Posted

November 18, 2023

Study Start

January 23, 2024

Primary Completion (Estimated)

April 30, 2029

Study Completion (Estimated)

April 30, 2029

Last Updated

April 21, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All requests will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com /ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please refer to our disclosure commitment at: https://astrazenecagrouptrials.pharmacm.com /ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patientlevel data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at: https://astrazenecagrouptrials.pharmacm.com /ST/Submission/Disclosure.
More information

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