NCT05952037

Brief Summary

This study will evaluate the safety and efficacy of the BCL2 inhibitor sonrotoclax (BGB-11417) in participants with relapsed/refractory Waldenström's Macroglobulinemia (R/R WM) and in combination with zanubrutinib in adult participants with previously untreated WM.

Trial Health

82
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
114

participants targeted

Target at P50-P75 for phase_2

Timeline
27mo left

Started Oct 2023

Longer than P75 for phase_2

Geographic Reach
9 countries

72 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress53%
Oct 2023Aug 2028

First Submitted

Initial submission to the registry

July 11, 2023

Completed
8 days until next milestone

First Posted

Study publicly available on registry

July 19, 2023

Completed
3 months until next milestone

Study Start

First participant enrolled

October 23, 2023

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 22, 2026

Expected
1.9 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2028

Last Updated

January 2, 2026

Status Verified

December 1, 2025

Enrollment Period

2.9 years

First QC Date

July 11, 2023

Last Update Submit

December 30, 2025

Conditions

Keywords

Waldenström's macroglobulinemiaWaldenstrom's Macroglobulinemia RecurrentWaldenstrom's Macroglobulinemia RefractoryLymphomaBGB-11417BCL-2i

Outcome Measures

Primary Outcomes (1)

  • Cohort 1: Major Response Rate (MRR)

    MRR is defined as the percentage of participants achieving partial response (PR) or better, as assessed by the Independent Review Committee (IRC) per the 11th International Workshop on Waldenström Macroglobulinemia (IWWM-11) WM response criteria.

    Up to approximately 4 years

Secondary Outcomes (17)

  • Cohorts 2 and 3: MRR as assessed by the IRC

    Up to approximately 5 years

  • All Cohorts: MRR as assessed by the Investigator

    Up to approximately 5 years

  • Cohorts 1, 2, and 3: Duration of Major Response (DoMR) as assessed by the IRC

    Up to approximately 5 years

  • All Cohorts: DoMR as assessed by the Investigator

    Up to approximately 5 years

  • Cohorts 1, 2, and 3: Complete Response (CR) + Very Good Partial Response (VGPR) as assessed by the IRC

    Up to approximately 5 years

  • +12 more secondary outcomes

Study Arms (4)

Cohort 1

EXPERIMENTAL

Participants with R/R disease to both Bruton tyrosine kinase (BTK) inhibitor and anti-CD20 antibody-based systemic therapy containing chemotherapy or proteasome inhibitor will receive sonrotoclax at a standard dose, given orally once daily.

Drug: Sonrotoclax

Cohort 2

EXPERIMENTAL

Participants with R/R disease to anti-CD20 antibody-based systemic therapy containing chemotherapy or proteasome inhibitor and were intolerant to BTK inhibitor will receive sonrotoclax at a standard dose, given orally once daily.

Drug: Sonrotoclax

Cohort 3

EXPERIMENTAL

Participants with R/R disease to a BTK inhibitor treatment and are unsuitable for chemoimmunotherapy will receive sonrotoclax at a standard dose, given orally once daily.

Drug: Sonrotoclax

Cohort 4

EXPERIMENTAL

Participants with previously untreated WM will receive sonrotoclax and zanubrutinib combination therapy for a fixed duration.

Drug: SonrotoclaxDrug: Zanubrutinib

Interventions

Administered orally as a capsule.

Also known as: BRUKINSA, BGB-3111
Cohort 4

Administered orally as a tablet.

Also known as: BGB-11417
Cohort 1Cohort 2Cohort 3Cohort 4

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Clinical and definitive histologic diagnosis of WM.
  • Meeting ≥ 1 criterion for treatment according to consensus panel criteria from the 2nd International Workshop on Waldenström's Macroglobulinemia (IWWM).
  • For Cohorts 1-3, refractory or relapsed disease at study entry unless participants had intolerance to the most recent therapy. Refractory disease is defined as not attaining at least a major response, or progressing while on or within 6 months of completing therapy. Relapsed disease is defined as attaining at least a major response to therapy and meeting the criteria for disease progression beyond 6 months after completing therapy.
  • For Cohort 4, patients must not have received prior therapy for WM (except for plasmapheresis).
  • Adequate organ function.

You may not qualify if:

  • Central nervous system (CNS) involvement by WM.
  • Transformation to aggressive lymphoma, such as diffuse large B-cell lymphoma.
  • History of other malignancies ≤ 2 years before study entry.
  • Uncontrolled active systemic infection or recent infection requiring parenteral antimicrobial therapy that was completed ≤ 14 days before the first dose of the study drug.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (72)

City of Hope National Medical Center

Duarte, California, 91010-3012, United States

Location

Colorado Blood Cancer Institute

Denver, Colorado, 80218, United States

Location

Medstar Georgetown University Hospital

Washington D.C., District of Columbia, 20007-2113, United States

Location

University of Miami

Miami, Florida, 33136-2107, United States

Location

Northwestern Medicine Cancer Center

Warrenville, Illinois, 60555-3269, United States

Location

Mission Cancer and Blood

Waukee, Iowa, 50263, United States

Location

University of Maryland Greenebaum Comprehensive Cancer Center

Baltimore, Maryland, 21201-1544, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215-5418, United States

Location

Mayo Clinic Rochester

Rochester, Minnesota, 55905-0001, United States

Location

Hattiesburg Hematology and Oncology Clinic

Hattiesburg, Mississippi, 39401-7233, United States

Location

Memorial Sloan Kettering Cancer Center Mskcc

New York, New York, 10065-6800, United States

Location

Atrium Health Levine Cancer Institute (Lci)

Charlotte, North Carolina, 28204-2990, United States

Location

Ohio State University Comprehensive Cancer Center

Columbus, Ohio, 43210-1280, United States

Location

Ut Southwestern Medical Center

Dallas, Texas, 75390-7208, United States

Location

Huntsman Cancer Institute

Salt Lake City, Utah, 84112-5550, United States

Location

Virginia Commonwealth University Massey Cancer Center

Richmond, Virginia, 23298, United States

Location

University of Washington

Seattle, Washington, 98195, United States

Location

Concord Repatriation General Hospital

Concord, New South Wales, NSW 2139, Australia

Location

Genesiscare North Shore

St Leonards, New South Wales, NSW 2065, Australia

Location

Princess Alexandra Hospital

Woolloongabba, Queensland, QLD 4102, Australia

Location

Flinders Medical Centre

Bedford PK, South Australia, SA 5042, Australia

Location

Monash Health

Clayton, Victoria, VIC 3168, Australia

Location

St Vincents Hospital Melbourne

Fitzroy, Victoria, VIC 3065, Australia

Location

Linear Clinical Research

Nedlands, Western Australia, WA 6009, Australia

Location

Royal Perth Hospital

Perth, Western Australia, WA 6000, Australia

Location

Cross Cancer Institute

Edmonton, Alberta, T6G 1Z2, Canada

Location

Lions Gate Hospital Chemotherapy Clinic

North Vancouver, British Columbia, V7L 2L7, Canada

Location

Qeii Health Science Center

Halifax, Nova Scotia, B3H 2Y9, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

The First Affiliated Hospital of Xiamen University

Xiamen, Fujian, 361003, China

Location

Guangdong Provincial Peoples Hospital

Guangzhou, Guangdong, 510080, China

Location

Henan Cancer Hospital

Zhengzhou, Henan, 450000, China

Location

Tongji Hospital of Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, 430030, China

Location

Yancheng First Peoples Hospital

Yancheng, Jiangsu, 224006, China

Location

Shengjing Hospital of China Medical Universityshenbei Branch

Shenyang, Liaoning, 110134, China

Location

The Affiliated Hospital of Qingdao University Branch South

Qingdao, Shandong, 266000, China

Location

Affiliated Zhongshan Hospital of Fudan University

Shanghai, Shanghai Municipality, 200032, China

Location

The Third Peoples Hospital of Datong

Datong, Shanxi, 037008, China

Location

Institute of Hematology and Hospital of Blood Disease

Tianjin, Tianjin Municipality, 300020, China

Location

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310003, China

Location

The First Hospital of Jiaxing

Jiaxing, Zhejiang, 314001, China

Location

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, Zhejiang, 325000, China

Location

Centre Hospitalier Universitaire Damiens Hopital Sud

Amiens, 80054, France

Location

Chu Clermont Ferrand Therapie Cellulaire and Hematolo

Clermontferrand, 63100, France

Location

Institut Paoli Calmettes

Marseille, 13009, France

Location

Hopital de La Pitie Salpetriere

Paris, 75013, France

Location

Chu Hopital Lyon Sud

PierreBenite, 69495, France

Location

Hopital Robert Debre

Reims, 51100, France

Location

General Hospital of Athens Alexandra

Athens, 115 28, Greece

Location

Irccs Azienda Ospedaliero Universitaria Bologna

Bologna, 40138, Italy

Location

Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia

Brescia, 25123, Italy

Location

Istituto Europeo Di Oncologia

Milan, 20141, Italy

Location

Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

Irccs Policlinico San Matteo, Universita Degli Studi Di Pavi

Pavia, 27100, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli

Roma, 00168, Italy

Location

Azienda Sanitaria Universitaria Friuli Centrale Presidio Ospedaliero Universitario Santa Maria Del

Udine, 33100, Italy

Location

Hospital Universitario Vall Dhebron

Barcelona, 08035, Spain

Location

Institut Catala Doncologia

Barcelona, 08908, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 8036, Spain

Location

Hospital Universitario Fundacion Jimenez Diaz

Madrid, 28040, Spain

Location

Hospital Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario Virgen Del Rocio

Seville, 41013, Spain

Location

Hospital Universitari Mutua Terrassa

Terrassa, 8221, Spain

Location

University Hospitals Dorset

Bournemouth, BH7 7DW, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasgow, G12 0YN, United Kingdom

Location

Churchill Hospital Oxford University Hospital Nhs Trust

Headington, OX3 7LE, United Kingdom

Location

Nhs Highland

Inverness, IV2 3BW, United Kingdom

Location

St Jamess University Hospital

Leeds, LS9 7TF, United Kingdom

Location

University College Hospital

London, NW1 2PG, United Kingdom

Location

The Christie Nhs Foundation Trust Manchester

Manchester, M20 4BX, United Kingdom

Location

Plymouth Hospitals Nhs Trust

Plymouth, PL6 8DH, United Kingdom

Location

Royal Marsden Nhs Foundation Royal Marsden Hospital

Sutton, SM2 5PT, United Kingdom

Location

MeSH Terms

Conditions

Waldenstrom MacroglobulinemiaLymphoma

Interventions

zanubrutinib

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Study Officials

  • Study Director

    BeOne Medicines

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 11, 2023

First Posted

July 19, 2023

Study Start

October 23, 2023

Primary Completion (Estimated)

September 22, 2026

Study Completion (Estimated)

August 1, 2028

Last Updated

January 2, 2026

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will share

BeOne shares data on completed studies responsibly and provides qualified scientific and medical researchers access to data and supporting documentation for clinical trials in dossiers for medicines and indications after submission and approval in the United States, China, and Europe. Clinical trials supporting subsequent local approvals, new indications, or combination products are eligible for sharing once corresponding regulatory approvals are achieved. BeOne shares data only when permitted by applicable data privacy and security laws and regulations, when it is feasible to do so without compromising the privacy of study participants, and other considerations. Qualified researchers with appropriate competencies who are engaged in novel scientific research may submit a request for participant-level data with a research proposal for BeOne review. Research teams must include a biostatistician and sign a Data Sharing Agreement prior to receiving access to clinical trial data.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
See plan description
Access Criteria
See plan description
More information

Locations