NCT05861297

Brief Summary

Immune thrombocytopenia treatment has evolved recently. However, none of treatments have only benefits without drawbacks. This study compares the clinical outcomes and adverse drug patterns of different treatment options. Medications which will be assessed during the current study are High Dose-dexamethasone (HD-DXM) (control group), Prednisolone + Azathioprine, Rituximab, Eltrombopag, and Romiplostim.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
467

participants targeted

Target at P75+ for phase_4

Timeline
Completed

Started May 2020

Longer than P75 for phase_4

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 5, 2020

Completed
3 years until next milestone

First Submitted

Initial submission to the registry

April 27, 2023

Completed
19 days until next milestone

First Posted

Study publicly available on registry

May 16, 2023

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 18, 2024

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 2, 2024

Completed
Last Updated

May 16, 2023

Status Verified

May 1, 2023

Enrollment Period

3.7 years

First QC Date

April 27, 2023

Last Update Submit

May 6, 2023

Conditions

Keywords

Primary Immune ThrombocytopeniaEtrombopagDexamethasoneRomiplostimRituximabAutoimmune Disorder

Outcome Measures

Primary Outcomes (1)

  • total patients who achieved sustained and overall response

    The primary outcomes were the total percentage of patients achieving a sustained response (SR) till the end of the study, complete response (CR), and partial response (PR). CR was characterized by the absence of bleeding and an increase in the platelet count to above 100×109/L after one month of the treatment. SR was defined as achieving CR or partial response (PR) until the end of the study with a 2-fold upsurge from starting point \[20, 21\]. PR was represented as PLTs count ≥ 30×109/L after one month following therapy, and no response (NR) was defined as platelets \< 30×109/L or bleeding

    18 months

Secondary Outcomes (1)

  • number of patients relapsed and adverse events

    18 months

Study Arms (5)

Control group

ACTIVE COMPARATOR

The first (control )group includes patients with confirmed diagnosed who received IV pulse (High Dose-Dexamethasone) therapy

Drug: Dexamethasone

PSL - AZA group

EXPERIMENTAL

The second group includes patients with confirmed diagnosed who received Prednisolone -Azathioprine therapy

Drug: Prednisolone and Azathioprine

The RTX group

EXPERIMENTAL

The third group includes patients with confirmed diagnosed who received Prednisolone -Azathioprine therapy

Drug: Rituximab

The ELTRO group

EXPERIMENTAL

The fourth group includes patients with confirmed diagnosed who received E therapy

Drug: Eltrombopag

The ROMP group

EXPERIMENTAL

The fifth group includes patients with confirmed diagnosed who received Romiplostim therapy

Drug: Romiplostim

Interventions

Patients were initiated with High Dose-Dexamethasone with a dose of 40 mg/m2 daily for four days per week immediately after the diagnosis of ITP for 6 months

Control group

the second group received 20 mg of Prednisolone three times daily and 1 mg/kg of oral Azathioprine once daily for two weeks, then tapering the Prednisolone dose through the subsequent weeks (6 weeks). While continuing treatment with Azathioprine for a total of six months.

PSL - AZA group

The third group received 500 mg/m2 intravenously of Rituximab once weekly for one month

The RTX group

The fourth group received 50 mg of Eltrombopag four hours before or after meals as oral daily doses for 6 months

The ELTRO group

The fifth group received 3μg/kg subcutaneous injection of Romiplostim once a week for 6 months

The ROMP group

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may not qualify if:

  • Patients with a confirmed secondary ITP diagnoses such as (chemicals induced, systemic lupus erythematosus, immune thyroid diseases, a lymphoproliferative disease, or chronic infection, such as Helicobacter pylori, human immunodeficiency virus (HIV) or hepatitis C virus (HCV); with cardiac, renal, or liver disease; who had received NSAIDs or anti-platelets within one month before the initiation of the enrollment were excluded from the study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

EL-Kasr elineiy

Cairo, 52611, Egypt

RECRUITING

Related Publications (1)

  • Hamed EM, Ibrahim ARN, Meabed MH, Khalaf AM, El Demerdash DM, Elgendy MO, Saeed H, Salem HF, Rabea H. Therapeutic Outcomes of High Dose-Dexamethasone versus Prednisolone + Azathioprine, Rituximab, Eltrombopag, and Romiplostim Strategies in Persistent, Chronic, Refractory, and Relapsed Immune Thrombocytopenia Patients. Pharmaceuticals (Basel). 2023 Aug 29;16(9):1215. doi: 10.3390/ph16091215.

MeSH Terms

Conditions

Purpura, Thrombocytopenic, IdiopathicAutoimmune Diseases

Interventions

DexamethasonePrednisoloneAzathioprineRituximabeltrombopagromiplostim

Condition Hierarchy (Ancestors)

Purpura, ThrombocytopenicPurpuraBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesThrombotic MicroangiopathiesThrombocytopeniaBlood Platelet DisordersCytopeniaHemorrhagic DisordersImmune System DiseasesHemorrhagePathologic ProcessesPathological Conditions, Signs and SymptomsSkin ManifestationsSigns and Symptoms

Intervention Hierarchy (Ancestors)

PregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, FluorinatedThionucleosidesSulfur CompoundsOrganic ChemicalsMercaptopurinePurinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsNucleosidesNucleic Acids, Nucleotides, and NucleosidesAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Mohamed Hussein Meabed, professor

    faculty of medicine beni-suef university

    STUDY CHAIR

Central Study Contacts

Eman Mostafa Hamed, master

CONTACT

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
FACTORIAL
Model Details: comparsion between five groups
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Teaching Assistant clinical pharmacy department, faculty of pharmacy

Study Record Dates

First Submitted

April 27, 2023

First Posted

May 16, 2023

Study Start

May 5, 2020

Primary Completion

January 18, 2024

Study Completion

April 2, 2024

Last Updated

May 16, 2023

Record last verified: 2023-05

Data Sharing

IPD Sharing
Will not share

Locations