NCT05750498

Brief Summary

The Autoimmune Liver disease Network for Kids (A-LiNK) is a multi-institutional group with the mission to deliver the best care to kids with pediatric autoimmune liver disease (AILD). This study will establish a shared clinical registry and a learning health network for the participating sites focusing on collecting and transmitting clinical measurement data, information about processes, and participation in an improvement collaborative. Pediatric Autoimmune Hepatitis (AIH) and Primary Sclerosing Cholangitis (PSC), represent a spectrum of AILD which present unique diagnostic and therapeutic challenges.A lack of accepted guidelines for disease monitoring or symptom management results in wide treatment variation with liver transplants indicated in refractory, progressive disease. The aims of A-LiNK are to: 1.) Create a learning health network focused on patient-centered outcomes research characterized by transparent sharing among centers, common priorities, and feasible plans for implementing new practices; 2) shift from traditional investigator-driven study to a patient and family-centered approach, and 3.) improve clinical outcomes and quality of life for pediatric AILD patients.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
800

participants targeted

Target at P75+ for all trials

Timeline
87mo left

Started Apr 2022

Longer than P75 for all trials

Geographic Reach
1 country

8 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress36%
Apr 2022Jun 2033

Study Start

First participant enrolled

April 28, 2022

Completed
10 months until next milestone

First Submitted

Initial submission to the registry

February 13, 2023

Completed
16 days until next milestone

First Posted

Study publicly available on registry

March 1, 2023

Completed
9.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2032

Expected
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2033

Last Updated

July 24, 2025

Status Verified

July 1, 2025

Enrollment Period

10.7 years

First QC Date

February 13, 2023

Last Update Submit

July 21, 2025

Conditions

Keywords

PediatricsAutoimmune HepatitisPrimary Sclerosing CholangitisAutoimmune Sclerosing CholangitisChronic Liver DiseaseEnd-stage Liver DiseaseClinical RegistryResearch RegistryQuality ImprovementOutcomes ResearchComparative Effectiveness ResearchPatient Reported OutcomesHealth Services Research

Outcome Measures

Primary Outcomes (6)

  • Baseline disease characteristics in the population

    2034

  • Disease relapse and biochemical remission rates

    Biochemical remission = transaminases (ALT/AST) within the upper limit of normal for age

    2034

  • Complications of disease

    Including ascites, esophageal variceal bleeding, cholangitis, hepatic encephalopathy, listed for liver transplant, hepatocellular carcinoma, or cholangiocarcinoma

    2034

  • Side-effects of steroids

    Including hypertension, diabetes mellitus, low bone mineral density, glaucoma, cataract, overweight, obesity

    2034

  • Pediatric Quality of Life Inventory (PedsQL 4.0) Generic Core Scales Short Form 15

    Health-related quality of life

    2034

  • Racial and ethnic disparities

    2034

Study Arms (1)

Children and adolescents with Autoimmune Liver Disease

Pediatric patients with a diagnosis of autoimmune hepatitis, or primary sclerosing cholangitis.

Other: No interventions

Interventions

There are no interventions

Children and adolescents with Autoimmune Liver Disease

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

All patients with a clinical diagnosis of Autoimmune Hepatitis (AIH), Primary Sclerosing Cholangitis (PSC), and Autoimmune Sclerosing Cholangitis (ASC). Patient recruitment will be conducted by the care centers participating in the registry. This also includes the recruitment of Spanish and other language-speaking patients. Participants who are enrolled in ImproveCareNow and who are eligible for A-LiNK will be separately consented to this study.

You may qualify if:

  • Clinical diagnosis of autoimmune hepatitis (AIH)
  • Clinical diagnosis of primary sclerosing cholangitis (PSC)
  • Clinical diagnosis of autoimmune sclerosing cholangitis (ASC)

You may not qualify if:

  • History of liver transplant

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

Stanford University

Palo Alto, California, 94304, United States

RECRUITING

Riley Children's Health

Indianapolis, Indiana, 46202, United States

RECRUITING

St. Louis Children's Hospital

St Louis, Missouri, 63110, United States

RECRUITING

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

RECRUITING

Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

RECRUITING

UPMC Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, 15224, United States

RECRUITING

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

RECRUITING

Seattle Children's Hospital

Seattle, Washington, 98105, United States

RECRUITING

MeSH Terms

Conditions

Hepatitis, AutoimmuneCholangitis, SclerosingEnd Stage Liver Disease

Condition Hierarchy (Ancestors)

Hepatitis, ChronicHepatitisLiver DiseasesDigestive System DiseasesAutoimmune DiseasesImmune System DiseasesCholangitisBile Duct DiseasesBiliary Tract DiseasesLiver FailureHepatic Insufficiency

Study Officials

  • Amy E Taylor, MD

    Children's Hospital Medical Center, Cincinnati

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Amy E Taylor, MD

CONTACT

Cyd M Castro-Rojas, PhD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Target Duration
10 Years
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 13, 2023

First Posted

March 1, 2023

Study Start

April 28, 2022

Primary Completion (Estimated)

December 31, 2032

Study Completion (Estimated)

June 30, 2033

Last Updated

July 24, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

To expand the possibilities for conducting outcomes research beyond the A-LiNK network of investigators, data will be shared, following an internal review process, with qualified investigators external to the network who are employed at, or affiliated with, institutions that are interested in conducting health services or comparative effectiveness research. Following a merit review and legal agreement, a de-identified data set will be shared with investigators following a workflow documented in the data-sharing procedure. To share data with investigators in and outside the network, the A-LiNK Leadership Committee will ensure that any requests that constitute research involving human subjects have received appropriate institutional review board (IRB) review and approval prior the sharing of data.

Locations