NCT05631912

Brief Summary

The team has developed a chimeric antigen receptor (CAR) based on T cell receptor (TCR) complex, called synthetic TCR and antigen receptor (STAR). Further, the researchers disrupted the endogenous T-cell receptor α constant (TRAC) locus by CRISPR/cas9, and then knocked in the anti-CD19-STAR construct through TRAC endogenous promoter. In this single center, prospective, open-label, single-arm, phase 1/2 study, the safety and efficacy of autologous CD19-targeting STAR-T cell therapy will be evaluated in patients with relapsed or refractory (r/r) B-cell non-Hodgkin's lymphoma (B-NHL) . A total of 19 to 38 patients are planned to be enrolled and receive CD19-STAR-T cell infusion. Phase 1 (9 to 18 cases) is dose escalation part, and phase 2 (10 to 20 cases) is expansion cohort part.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
38

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Jun 2023

Typical duration for phase_1

Geographic Reach
1 country

2 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 21, 2022

Completed
9 days until next milestone

First Posted

Study publicly available on registry

November 30, 2022

Completed
7 months until next milestone

Study Start

First participant enrolled

June 30, 2023

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 15, 2024

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

December 15, 2025

Completed
Last Updated

July 6, 2023

Status Verified

July 1, 2023

Enrollment Period

1.5 years

First QC Date

November 21, 2022

Last Update Submit

July 3, 2023

Conditions

Outcome Measures

Primary Outcomes (5)

  • Phase 1: Incidence of Adverse Events (AEs)

    AE is defined as any adverse medical event from the date of randomization to 12 months after CD19-STAR-T cells infusion. Among them, CRS and ICANS were graded according to American Society for Transplantation and Cellular Therapy (ASTCT) criteria. Other AEs were graded according to common terminology criteria for adverse events (CTCAE) v5.0.

    12 months

  • Phase 1: Incidence of Dose-Limiting Toxicities (DLTs)

    DLT was defined as CD19-STAR-T cells-related events with onset within first 28 days following infusion: The development of Grade (G) 3 or higher grade CRS lasting \> 2 weeks; Any CD19-STAR-T cells-related AE requiring intubation; All G4 non-hematologic toxicities.

    First infusion date of CD19-STAR-T cells up to 28 days

  • Phase 1: Maximum tolerated dose (MTD)

    MTD is defined as the highest dose level of less than or equal to 2 DLT among the 6 subjects finally determined.

    12 months

  • Phase 1: Recommended phase 2 dose (RP2D)

    The recommended dose for phase 2 was determined through phase 1 study.

    12 months

  • Phase 2: Best objective Response Rate

    The incidence of complete response (CR), partial response (PR), stable disease (SD), progressive disease (PD), or unevaluable (UE) as the best response to treatment assessed by investigators and based on the Lugano 2014 assessment criterion.

    12 months

Secondary Outcomes (7)

  • Phase 2: Overall Survival (OS)

    12 months after the first infusion of CD19-STAR-T cells

  • Phase 2: Progression Free Survival (PFS)

    12 months after the first infusion of CD19-STAR-T cells

  • Phase 2: Time to response (TTR)

    12 months

  • Phase 2: Duration of Response (DOR)

    12 months

  • Pharmacokinetics: Number and copy number of CD19-STAR-T cells (phase 1 and phase 2)

    12 months

  • +2 more secondary outcomes

Other Outcomes (2)

  • Relationship between infusion dose of CD19-STAR-T cells and efficacy

    12 months

  • To analyze the dynamic changes of STAR-T cells after infusion

    12 months

Study Arms (1)

Autologous TRAC locus-inserted CD19-targeting STAR-T cells

EXPERIMENTAL

A conditioning chemotherapy regimen of fludarabine and cyclophosphamide (FC regimen) will be administered followed by investigational treatment, autologous targeting CD19 synthetic T-cell receptor antigen receptor T cells. Post leukapheresis, administration of short half-life chemo-agents, Bruton tyrosine kinase inhibitor (BTKi) and/or dexamethasone should be considered to bridge the following FC regimen in patients with bulky tumor burden, rapidly aggressive progression, and/or indications of imperious symptom control.

Biological: Autologous CD19-STAR-T cellDrug: FludarabineDrug: Cyclophosphamide

Interventions

Phase 1 dose escalation (3+3) : dose 1 (1×10\^6 cells/kg) ,dose 2 (3×10\^6 cells/kg) ,dose 3 (1×10\^7 cells/kg); Phase 2 : Appropriate dose

Also known as: Autologous CD19-targeting synthetic T-cell receptor antigen receptor T cells
Autologous TRAC locus-inserted CD19-targeting STAR-T cells

Intravenous fludarabine 25-30 mg/m\^2/day on days -5, -4, and -3.

Also known as: Fludarabine Phosphate for Injection
Autologous TRAC locus-inserted CD19-targeting STAR-T cells

Intravenous cyclophosphamide 300-500 mg/m\^2/day on days -5, -4, and -3.

Also known as: Cyclophosphamide for Injection
Autologous TRAC locus-inserted CD19-targeting STAR-T cells

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18-75 (inclusive).
  • Patients with histologically confirmed CD19-positive B-cell NHL, including the following types defined by the World Health Organization (WHO) 2016:
  • Diffuse large B-cell lymphoma not otherwise specified (DLBCL-NOS), including Activated B-cell type (ABC) / Germinal center B-cell Type (GCB);
  • Primary mediastinal (thymic) large B-cell lymphoma (PMBCL);
  • Transformed follicular lymphoma (TFL);
  • High-grade B-cell lymphoma with MYC and BCL2 and/or BCL6 rearrangements (HGBCL);
  • Follicular lymphoma (FL);
  • Mantle cell lymphoma (MCL) \[pathologically confirmed, with documentation of monoclonal B cells that have a chromosome translocation t(11;14)(q13;q32) and/or overexpress cyclin D1\];
  • Marginal zone lymphoma (MZL), including nodal or splenic marginal zone B-cell lymphoma and mucosa-associated lymphoid tissue (MALT) lymphoma.
  • Relapse after treatment with ≥2 lines systemic therapy for all the above disease types, or refractory disease for aggressive types (DLBCL-NOS, PMBCL, TFL and HGBCL). Relapse disease is defined as disease progression after last regimen. Refractory disease is defined as no CR to first-line therapy:
  • PD as best response to first-line therapy, or
  • SD as best response after at least 4 cycles of first-line therapy (eg, 4 cycles of R-CHOP), or
  • PR as best response after at least 6 cycles and biopsy-proven residual disease or disease progression ≤ 6 months of therapy, or
  • Refractory post-autologous stem cell transplant (ASCT) i. Disease progression or relapsed less than or equal to 12 months of ASCT (must have biopsy proven recurrence in relapsed individuals) ii. If salvage therapy is given post-ASCT, the individual must have had no response to or relapsed after the last line of therapy.
  • Individuals must have received adequate prior therapy:
  • +15 more criteria

You may not qualify if:

  • No obvious hereditary diseases.
  • Able to understand the requirements and matters of the trial, and willing to participate in clinical research as required.
  • Informed consent must be signed.
  • During the screening period, there was central nervous system (CNS) invasion or a history of clinically significant central nervous system diseases, such as epilepsy and cerebrovascular diseases.
  • Women who are pregnant or breastfeeding, or who do not agree to use effective contraception during treatment and during the subsequent 1 year.
  • History of allogeneic hematopoietic stem cell transplantation, or organ transplantation.
  • History of other malignancies that have not been in remission.
  • Patients with primary immunodeficiency or autoimmune diseases requiring immunosuppressive therapy.
  • Received radiotherapy within 3 months before enrollment.
  • Received immunotherapy drugs within 4 weeks before enrollment, such as anti-programmed death 1 (PD-1) antibody, anti-programmed death ligand 1 (PD-L1) antibody, CD19/CD3-bispecific antibody, and so on.
  • Patients who received any immunocellular therapy within 6 months before enrollment.
  • Confirmed evidence showing positiveness of anti-CD19 scFv reaction in patient serum.
  • Patients who participated in other clinical trials within 4 weeks prior to enrollment.
  • Uncontrolled infectious diseases or other serious illnesses, including but not limited to infections \[e.g., human immunodeficiency virus (HIV) infection or acute or chronic active hepatitis B (HBV) or C (HCV) infection\], congestive heart failure, unstable angina, arrhythmias, or that pose an unpredictable risk in the opinion of the attending physician.
  • The presence of uncontrollable serous membrane fluid, such as massive pleural effusion or ascites.
  • +7 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Biotherapeutic Department, Chinese PLA General Hospital

Beijing, Beijing Municipality, 100853, China

RECRUITING

School of medicine, Tsinghua University & Changping Laboratory

Beijing, Beijing Municipality, China

RECRUITING

MeSH Terms

Interventions

fludarabinefludarabine phosphateInjectionsCyclophosphamide

Intervention Hierarchy (Ancestors)

Drug Administration RoutesDrug TherapyTherapeuticsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus Compounds

Study Officials

  • Weidong Han, Ph.D

    Biotherapeutic Department, Chinese PLA General Hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Director of Biotherapeutic Department

Study Record Dates

First Submitted

November 21, 2022

First Posted

November 30, 2022

Study Start

June 30, 2023

Primary Completion

December 15, 2024

Study Completion

December 15, 2025

Last Updated

July 6, 2023

Record last verified: 2023-07

Data Sharing

IPD Sharing
Will not share

Locations