NCT05568264

Brief Summary

Study Aims Pilot study: Due to the large recruitment goal and length of the project, the study team/PIs will evaluate the first cohort of 6-10 participants to refine study procedures and study-related materials. If no major modifications are made to the protocol as a result of this evaluation, data from these participants will be included for analysis. Aim 1: Evaluate the efficacy of an early, evidence-based, clinical experience-based therapeutic intervention (from the NICU to 12-months corrected age) on improving motor function and reducing severity of motor delays in infants at 12-months corrected age. The investigators hypothesize that the intervention group will demonstrate an average 8-point difference (0.5 standard deviation) compared to the standard of care group. \[an 8-point difference is considered a clinically meaningful difference\] Aim 2: Evaluate the early effects (i.e., before 12 months) of a therapeutic intervention, provided from NICU to 12-months corrected age, on motor function and severity of motor delay. The Investigators hypothesize that a statistically significant higher percentage of infants in the intervention group will demonstrate improved motor function and reduced severity of motor delays, compared to the standard of care group-assessed using sensors, the NSMDA and TIMP-as early as 3-months corrected age. Aim 3: Evaluate whether an early intervention that focuses on caregiver engagement improves caregiver well-being. The invetigators hypothesize that an intervention that focuses on supporting and addressing the individual needs of the caregiver will improve caregiver well-being. The investigators will evaluate these effects using the PedsQL (Family Impact Module).

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
222

participants targeted

Target at P75+ for not_applicable

Timeline
8mo left

Started Oct 2022

Longer than P75 for not_applicable

Geographic Reach
1 country

3 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress85%
Oct 2022Dec 2026

First Submitted

Initial submission to the registry

September 27, 2022

Completed
4 days until next milestone

Study Start

First participant enrolled

October 1, 2022

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 5, 2022

Completed
3.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 31, 2026

Expected
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2026

Last Updated

May 21, 2025

Status Verified

May 1, 2025

Enrollment Period

3.7 years

First QC Date

September 27, 2022

Last Update Submit

May 19, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Bayley-4 motor score at 12-months corrected age

    The Bayley-4 is an individually administered instrument that assesses the developmental functioning of infants and young children, aged between 16 days and 42 months, by observing the child's interaction with stimuli designed to engage them. It assesses five domains: Motor, Cognitive, Language, Social-emotional, and Adaptive behavior. The primary outcome will be the Bayley-4 motor score at 12-months corrected age. The standard scores range from 45-155 for the motor domain. Higher scores indicate better outcomes.

    Bayley-4 motor score assessed at 12-months CA will be the primary outcome

Secondary Outcomes (3)

  • Movement quality assessed by wearable sensors

    At each assessment timepoint, including study enrollment, monthly up to 3 months corrected age (CA), 3-month CA, 6-months CA, 9-months CA, 12-months CA, 18-months CA (optional), and 24-months CA (optional).

  • Pediatric Quality of Life Inventory (PedsQL)

    PedsQL will be completed once during NICU stay (up to 45 days post enrolment), at one-and two-month intervals after enrollment; at 3-month corrected age (CA), 6-months CA, 9-months CA, 12-months CA, 18-months CA (optional), and 24-months CA (optional).

  • Bayley-4 Cognitive score Bayley-4 Cognitive score Bayley-4 Cognitive score

    The Bayley-4 cognitive score will be assessed at 6-months corrected age (CA), 12-months CA, 18-months CA (optional), and 24-months CA (optional).

Other Outcomes (8)

  • Pediatric Evaluation of Disability Inventory-Computer Adaptive Test (PEDI-CAT) Mobility Domain

    The PEDI-CAT will be administered at 12-months corrected age (CA), at 18-months CA (optional), and at 24-months CA (optional).

  • Warner Initial Developmental Evaluation of Adaptive and Functional Skills (WIDEA-FS)

    The WIDEA-FS will be administered at 12-months corrected age (CA), and at 18-months CA (optional) and 24-months CA (optional).

  • Hammersmith Infant Neurological Exam (HINE)

    The HINE will be performed at 3-months corrected age (CA), 6-months CA, 9-months CA, and 12-months CA.

  • +5 more other outcomes

Study Arms (2)

Physical Therapy Intervention

EXPERIMENTAL

Infants enrolled in this arm will receive the intervention in addition to standard of care

Other: Physical Therapy intervention

Standard of Care

NO INTERVENTION

Infants enrolled in this arm will receive standard of care

Interventions

The intervention is based on five principles: active learning, caregiver engagement, environmental enrichment, strengths-based approach, and dose. The intervention will start in the NICU and continue until 12-months corrected age. Infants in the intervention group will receive up to two therapist visits per week in addition to standard of care physical therapy. Caregivers will be asked to work with their infant on activities provided by the therapist. The therapist will provide resources to support the caregiver in working on these activities with their child, and caregivers will be asked to complete the activities for as much time as possible, throughout the day. Therapists will work with caregivers to identify ways to incorporate activities into their day. Caregiver engagement and caregiver ability to complete sessions and activity recommendations will be monitored.

Physical Therapy Intervention

Eligibility Criteria

Age33 Weeks - 48 Weeks
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • NICU admission and qualifies for Early Childhood Clinic (NICU high-risk follow up clinic) or Early Intervention due to:
  • BW \<1500 grams
  • Disorders of the central nervous system
  • Brain injury (including but not limited to extra axial hemorrhage, any grade intraventricular or intraparenchymal hemorrhage, stroke, hypoxic ischemic encephalopathy (HIE), meningitis)
  • HIE includes mild, moderate, severe exam on modified Sarnat exam, both cooled and non-cooled
  • includes "at risk for HIE" with 10-minute Apgar \<7 plus pH\<7.15 or base deficit \>/=12.
  • Brain developmental abnormalities (hydrocephalus, microcephaly, cortical dysgenesis)
  • Cramped synchronous movements at term PMA
  • Bronchopulmonary dysplasia (BPD) defined as need for respiratory support at 36 weeks postmenstrual age in an infant born at \<32 weeks of gestation.
  • AND
  • Medically stable AND able to start intervention between 34-48 weeks PMA.

You may not qualify if:

  • (related to inability to complete intervention, sensor placement, or clinic assessments)
  • open wounds, skin condition precluding sensor placement
  • immune deficiencies requiring protective isolation
  • limb reduction defects
  • followed primarily in another clinic (including but not limited to meningomyelocele and related conditions/trisomy 21)
  • bleeding disorders or ongoing need for anticoagulation
  • palliative or hospice care (for life limiting conditions including, but not limited to trisomy 18, 13)
  • known visual impairment at the time of enrollment
  • DCFS custody
  • no English-speaking caregivers
  • any other condition that would preclude participation in the study, as determined by the PI
  • previously enrolled in competing randomized trial with developmental outcome variables
  • Each child's enrollment in the study will be approved by the child's neonatologist.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, 60611, United States

RECRUITING

Northwestern Medicine Prentice Children's Hospital

Chicago, Illinois, 60611, United States

RECRUITING

Children's Hospital at the University of Illinois

Chicago, Illinois, 60612, United States

RECRUITING

Related Publications (1)

  • Deng W, Anastasopoulos S, deRegnier RA, Pouppirt N, Barlow AK, Patrick C, O'Brien MK, Babula S, Sukal-Moulton T, Peyton C, Morgan C, Rogers JA, Lieber RL, Jayaraman A. Protocol for a randomized controlled trial to evaluate a year-long (NICU-to-home) evidence-based, high dose physical therapy intervention in infants at risk of neuromotor delay. PLoS One. 2023 Sep 19;18(9):e0291408. doi: 10.1371/journal.pone.0291408. eCollection 2023.

MeSH Terms

Conditions

Psychomotor DisordersPremature BirthHypoxia-Ischemia, BrainBronchopulmonary Dysplasia

Condition Hierarchy (Ancestors)

Neurobehavioral ManifestationsNeurologic ManifestationsNervous System DiseasesSigns and SymptomsPathological Conditions, Signs and SymptomsObstetric Labor, PrematureObstetric Labor ComplicationsPregnancy ComplicationsFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesBrain IschemiaCerebrovascular DisordersBrain DiseasesCentral Nervous System DiseasesHypoxia, BrainVascular DiseasesCardiovascular DiseasesHypoxiaSigns and Symptoms, RespiratoryVentilator-Induced Lung InjuryLung InjuryLung DiseasesRespiratory Tract DiseasesInfant, Premature, DiseasesInfant, Newborn, DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Arun Jayaraman, PT, PhD

    Shirley Ryan AbilityLab

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Elizabeth Hoffman, DPT

CONTACT

Sara Prokup, DPT

CONTACT

Study Design

Study Type
interventional
Phase
not applicable
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Masking Details
Clinicians involved in clinical assessments are blinded to study group
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Stratified randomized block design, two-arm, parallel assignment
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Investigator

Study Record Dates

First Submitted

September 27, 2022

First Posted

October 5, 2022

Study Start

October 1, 2022

Primary Completion (Estimated)

May 31, 2026

Study Completion (Estimated)

December 31, 2026

Last Updated

May 21, 2025

Record last verified: 2025-05

Data Sharing

IPD Sharing
Will not share

Locations