NCT05465941

Brief Summary

This phase II trial tests whether pegylated SN-38 conjugate PLX038 (PLX038) works to shrink tumors in patients with ovarian, primary peritoneal, and fallopian tube cancers that has spread from where it first started (primary site) to other places in the body (metastatic). PLX038 may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
43

participants targeted

Target at P25-P50 for phase_2

Timeline
69mo left

Started Sep 2022

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress39%
Sep 2022Dec 2031

First Submitted

Initial submission to the registry

July 18, 2022

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 20, 2022

Completed
2 months until next milestone

Study Start

First participant enrolled

September 14, 2022

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 15, 2027

Expected
4.9 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2031

Last Updated

February 9, 2026

Status Verified

February 1, 2026

Enrollment Period

4.4 years

First QC Date

July 18, 2022

Last Update Submit

February 5, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Proportion of confirmed tumor responses

    A confirmed tumor response is defined to be either a complete response or partial response noted as the objective status on 2 consecutive evaluations at least 4 weeks apart. Confirmed tumor response will be evaluated using the first 6 cycles of treatment. All patients meeting the eligibility criteria who have signed a consent form, have begun treatment, and who have had at least one post-baseline tumor assessment will be evaluable for response. Patients not having met the criteria of having one post-baseline tumor assessment will be considered evaluable if they have discontinued the study due to disease progression.

    Up to first 6 cycles of treatment (1 cycle = 21 days)

Secondary Outcomes (3)

  • Progression-free survival (PFS)

    From study entry to the first of either disease progression or death from any cause, assessed up to 5 years

  • Overall survival (OS)

    From study entry to death from any cause, assessed up to 5 years

  • Incidence of adverse event rates

    Up to 30 days

Other Outcomes (5)

  • TOP1-deoxyribonucleic acid covalent complexes (TOP1cc)

    Up to cycle 1 day 8 (1 cycle = 21 days)

  • Homologous recombination (HR) status

    Up to cycle 1 day 8 (1 cycle = 21 days)

  • Protein expression

    Up to cycle 1 day 8 (1 cycle = 21 days)

  • +2 more other outcomes

Study Arms (1)

Treatment (pegylated SN-38 conjugate PLX038)

EXPERIMENTAL

Patients receive PLX038 IV over 1 hour on day 1 of each cycle. Cycles repeat every 21 days in the absence of disease progression or unacceptable toxicity. Patients also undergo CT, biopsy, as well as blood and stool sample collection during screening and on the trial.

Procedure: BiopsyDrug: Pegylated SN-38 Conjugate PLX038Procedure: Computed TomographyProcedure: Biospecimen Collection

Interventions

BiopsyPROCEDURE

Undergo biopsy

Also known as: Bx, BIOPSY_TYPE
Treatment (pegylated SN-38 conjugate PLX038)

Given IV

Also known as: Pegylated SN-38 PLX038, PLX 038, PLX-038, PLX038
Treatment (pegylated SN-38 conjugate PLX038)

Undergo CT

Also known as: CAT, CAT Scan, Computed Axial Tomography, computerized axial tomography, Computerized axial tomography (procedure), Computerized Tomography, CT, CT SCAN, tomography
Treatment (pegylated SN-38 conjugate PLX038)

Undergo blood and stool sample collection

Also known as: Biological Sample Collection, Biospecimen Collected, Specimen Collection
Treatment (pegylated SN-38 conjugate PLX038)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age \>= 18 years NOTE: Because no dosing or adverse event data are currently available on the use of PLX038 in patients \< 18 years of age, children are excluded from this study, but will be eligible for future pediatric trials
  • Histological confirmed high grade serous ovarian cancer consistent with ovarian, fallopian tube, or primary peritoneal carcinoma (NOTE: Any of these diseases are referred to in this protocol as "ovarian cancer")
  • Recurrent high grade serous ovarian cancer that was initially platinum sensitive (i.e., had at least one platinum-free interval of at least 6 months before progression) is now platinum resistant
  • No more than one prior line of therapy for platinum resistant disease. NOTE: Prior poly adenosine diphosphate-ribose polymerase (PARP) inhibitor therapy is allowed
  • Measurable disease per Response Evaluation Criteria in Solid Tumors (RECIST) 1.1
  • Disease that is amenable to two biopsies
  • Life expectancy greater \>= 12 weeks
  • Eastern Cooperative Oncology Group (ECOG) performance status (PS) 0, 1 or 2
  • Hemoglobin \>= 8.0 g/dL (obtained =\< 28 days prior to registration)
  • Absolute neutrophil count (ANC) \>= 1500/mm\^3 (obtained =\< 28 days prior to registration)
  • Platelet count \>= 100,000/mm\^3 (obtained =\< 28 days prior to registration)
  • Total bilirubin \>= 1.5 x upper limit of normal (ULN) (obtained =\< 28 days prior to registration)
  • Alanine aminotransferase (ALT) and aspartate transaminase (AST) =\< 3 x ULN (=\< 5 x ULN for patients with liver involvement) (obtained =\< 28 days prior to registration)
  • Calculated creatinine clearance \>= 45 ml/min using the Cockcroft-Gault formula (obtained =\< 28 days prior to registration)
  • Negative pregnancy test done =\< 7 days prior to registration, for persons of childbearing potential only
  • +4 more criteria

You may not qualify if:

  • Any of the following because this study involves an agent that has known genotoxic, mutagenic and teratogenic effects:
  • Pregnant persons
  • Nursing persons
  • Persons of childbearing potential who are unwilling to employ adequate contraception
  • Histology other than high grade serous carcinoma
  • Prior treatment restrictions
  • Chemotherapy =\< 4 weeks prior to registration
  • Immunotherapy =\< 4 weeks prior to registration
  • Radiotherapy =\< 4 weeks prior to registration
  • Any other investigational therapy =\< 4 weeks prior to registration
  • History of prior or concurrent malignancy =\< 2 years prior to registration
  • Exceptions: If natural history or treatment does not have the potential to interfere with the safety or efficacy assessment of the investigational regimen
  • Uncontrolled intercurrent illness including, but not limited to:
  • Myocardial infarction within 6 months of study entry
  • New York Heart Association (NYHA) class III or IV heart failure
  • +14 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Mayo Clinic

Rochester, Minnesota, 55905, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Fallopian Tube NeoplasmsOvarian Neoplasms

Interventions

BiopsySpecimen Handling

Condition Hierarchy (Ancestors)

Genital Neoplasms, FemaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsFallopian Tube DiseasesAdnexal DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesEndocrine Gland NeoplasmsOvarian DiseasesEndocrine System DiseasesGonadal Disorders

Intervention Hierarchy (Ancestors)

CytodiagnosisCytological TechniquesClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisDiagnostic Techniques, SurgicalSurgical Procedures, OperativeInvestigative Techniques

Study Officials

  • Andrea E. Wahner Hendrickson, M.D.

    Mayo Clinic in Rochester

    PRINCIPAL INVESTIGATOR
  • Scott H. Kaufmann, M.D., Ph.D.

    Mayo Clinic in Rochester

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Clinical Trials Referral Office

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Masking Details
Staining will be read independently by two individuals blinded to treatment, who will score each sample for the percentage of cells that are positive for \>8 nucleoplasmic TOP1ccs.
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 18, 2022

First Posted

July 20, 2022

Study Start

September 14, 2022

Primary Completion (Estimated)

February 15, 2027

Study Completion (Estimated)

December 31, 2031

Last Updated

February 9, 2026

Record last verified: 2026-02

Locations