NCT05347238

Brief Summary

Fluid-unresponsive hypotension needing cardiotropic drug treatment is a serious complication in very preterm neonates with suspected late-onset sepsis (LOS; defined as culture positive or negative bloodstream infection or necrotizing enterocolitis occurring \>48 hours of age). In Canada, \~250 very preterm neonates receive cardiotropic drugs for LOS related fluid-unresponsive hypotension every year; of these \~35-40% die. Unlike for adult patients, there is little evidence to inform practice. While several medications are used by clinicians, the most frequently used medications are Dopamine (DA) and Norepinephrine (NE). However, their relative impact on patient outcomes and safety is not known resulting in significant uncertainty and inter- and intra-unit variability in practice. Conducting large randomized trials in this subpopulation can be operationally challenging and expensive. Comparative effectiveness research (CER), is a feasible alternative which can generate high-quality real-world evidence using real-world data, by comparing the impact of different clinical practices. Aim: To conduct an international CER study, using a pragmatic clinical trial design, in conjunction with the existing infrastructure of the Canadian Neonatal Network to identify the optimal management of hypotension in very preterm neonates with suspected LOS. Objective: To compare the relative effectiveness and safety of pharmacologically equivalent dosages of DA versus NE for primary pharmacotherapy for fluid-unresponsive hypotension in preterm infants born ≤ 32 weeks gestational age with suspected LOS. Hypothesis: Primary treatment with NE will be associated with a lower mortality Methods: This CER project will compare management approach at the unit-level allowing inclusion of all eligible patients admitted during the study period. 16 centers in Canada, 2 centers in Ireland, 1 center in each of Israel, Spain and the UK, and 6 centers in the United States have agreed to standardize their practice. All eligible patients deemed circulatory insufficient will receive fluid therapy (minimum 10-20 cc/kg). If hypotension remains unresolved: Dopamine Units: start at 5mics/kg/min, increase every 16-30 minutes by 5 mics/kg/min to a maximum dose of 15 mics/kg/min or adequate response Norepinephrine Units: start at 0.05 mics/kg/min, increase every 16-30 minutes by 0.05 mics/kg/min to maximum dose of 0.15/mics/kg/min or adequate response

Trial Health

83
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
550

participants targeted

Target at P75+ for all trials

Timeline
10mo left

Started Feb 2023

Longer than P75 for all trials

Geographic Reach
5 countries

23 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress78%
Feb 2023Mar 2027

First Submitted

Initial submission to the registry

April 12, 2022

Completed
14 days until next milestone

First Posted

Study publicly available on registry

April 26, 2022

Completed
10 months until next milestone

Study Start

First participant enrolled

February 6, 2023

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2026

Expected
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 31, 2027

Last Updated

July 8, 2025

Status Verified

July 1, 2025

Enrollment Period

3.4 years

First QC Date

April 12, 2022

Last Update Submit

July 3, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • All cause in-hospital mortality

    Death before discharge

    From illness onset to discharge (home or to another hospital) - assessed up to a maximum of 36 weeks after date of birth

Secondary Outcomes (6)

  • Episode-related death

    <14 days from illness onset

  • Treatment failure rate

    90 minutes after initial vasopressor initiation (or sooner if secondary dose added or primary agent replaced as per clinical discretion)

  • New diagnosis of severe neurological injury

    From illness onset to discharge (home or to another hospital) - assessed up to a maximum of 36 weeks after date of birth

  • Bronchopulmonary dysplasia

    Assessed at 36 weeks PMA

  • Retinopathy of prematurity

    From illness onset to discharge (home or to another hospital) - assessed up to a maximum of 36 weeks after date of birth

  • +1 more secondary outcomes

Study Arms (2)

Dopamine Units

Units who have standardized their practice with the use of Dopamine as a first line agent.

Drug: Dopamine

Norepinephrine Units

Units who have standardized their practice with the use of Norepinephrine as a first line agent.

Drug: Norepinephrine

Interventions

Start at 5mics/kg/min, increase every 16-30 minutes by 5 mics/kg/min to a maximum dose of 15 mics/kg/min or adequate response.

Dopamine Units

Start at 0.05 mics/kg/min, increase every 16-30 minutes by 0.05 mics/kg/min to maximum dose of 0.15/mics/kg/min or adequate response

Norepinephrine Units

Eligibility Criteria

Age21 Weeks - 32 Weeks
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)
Sampling MethodProbability Sample
Study Population

All preterm infants born ≤32 weeks gestational age and \> 48 hours of life with suspected sepsis with systemic hypotension admitted to the participating sites and meeting the above eligibility criteria will be included in the study.

You may qualify if:

  • ≤32 weeks gestational age and \> 48 hours of life
  • Receiving primary vasopressor therapy with Dopamine or Norepinephrine in the context of suspected late-onset sepsis or necrotizing enterocolitis with systemic hypotension (defined as: culture positive or negative bloodstream infection)

You may not qualify if:

  • Known chromosomal or genetic anomalies
  • Receiving primary therapy with agents other than Dopamine or Norepinephrine

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

Banner-University Medical Center Phoenix

Phoenix, Arizona, 85006, United States

NOT YET RECRUITING

Dayton Children's Hospital

Dayton, Ohio, 45404, United States

RECRUITING

Methodist Healthcare

San Antonio, Texas, 78229, United States

RECRUITING

Foothill's Medical Centre

Calgary, Alberta, Canada

RECRUITING

BC Women's Hospital

Vancouver, British Columbia, Canada

RECRUITING

Victoria General Hospital

Victoria, British Columbia, V8Z 6R5, Canada

RECRUITING

St.Boniface Hospital

Winnipeg, Manitoba, Canada

NOT YET RECRUITING

Winnipeg Health Sciences Centre

Winnipeg, Manitoba, Canada

RECRUITING

IWK Health Centre

Halifax, Nova Scotia, Canada

RECRUITING

McMaster Children's Hospital

Hamilton, Ontario, Canada

RECRUITING

London Health Sciences Centre

London, Ontario, Canada

RECRUITING

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada

RECRUITING

Hospital for Sick Children

Toronto, Ontario, Canada

RECRUITING

Mount Sinai Hospital

Toronto, Ontario, Canada

RECRUITING

Sunnybrook Health Sciences Centre

Toronto, Ontario, Canada

RECRUITING

Windsor Regional Hospital

Windsor, Ontario, Canada

RECRUITING

CHU Sainte- Justine

Montreal, Quebec, Canada

RECRUITING

Jewish General Hospital

Montreal, Quebec, Canada

RECRUITING

Montreal Children's Hospital

Montreal, Quebec, Canada

RECRUITING

University Cork College

Cork, Ireland

RECRUITING

Coombe Women & Infants University Hospital

Dublin, Ireland

NOT YET RECRUITING

Shamir Medical Center

Be’er Ya‘aqov, Israel

RECRUITING

La Paz University Hospital

Madrid, 28046, Spain

RECRUITING

MeSH Terms

Conditions

Neonatal Sepsis

Interventions

DopamineNorepinephrine

Condition Hierarchy (Ancestors)

SepsisInfectionsInfant, Newborn, DiseasesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesSystemic Inflammatory Response SyndromeInflammationPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Biogenic MonoaminesBiogenic AminesAminesOrganic ChemicalsCatecholaminesCatecholsPhenolsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsEthanolaminesAmino AlcoholsAlcohols

Study Officials

  • Amish Jain, MBBS, MRCPCH, PhD

    Mount Sinai Hospital, Canada

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Amish Jain, MBBS, MRCPCH, PhD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Target Duration
36 Weeks
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 12, 2022

First Posted

April 26, 2022

Study Start

February 6, 2023

Primary Completion (Estimated)

June 30, 2026

Study Completion (Estimated)

March 31, 2027

Last Updated

July 8, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will not share

Locations