NCT05305040

Brief Summary

This is a Phase 3 study to evaluate posoleucel (ALVR105, Viralym-M); an allogeneic, off-the-shelf multi-virus specific T cell therapy that targets six viral pathogens: BK virus, cytomegalovirus, adenovirus, Epstein-Barr virus, human herpesvirus 6 and JC virus.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
451

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2022

Geographic Reach
10 countries

88 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 22, 2022

Completed
2 days until next milestone

Study Start

First participant enrolled

March 24, 2022

Completed
7 days until next milestone

First Posted

Study publicly available on registry

March 31, 2022

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 30, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 30, 2024

Completed
4 months until next milestone

Results Posted

Study results publicly available

May 16, 2024

Completed
Last Updated

May 16, 2024

Status Verified

April 1, 2024

Enrollment Period

1.9 years

First QC Date

March 22, 2022

Results QC Date

April 19, 2024

Last Update Submit

April 19, 2024

Conditions

Keywords

Allogeneic Hematopoietic Cell TransplantALVR105PosoleucelViralym-MVirus-specific T cells (VSTs)Cytotoxic T Lymphocytes (CTLs)

Outcome Measures

Primary Outcomes (1)

  • Average Number of Clinically Significant Infections or Episodes of End-Organ Disease Through Week 14

    The average number of clinically significant infections or episodes of end-organ disease per participant due to Adenovirus (AdV), BK virus (BKV), Cytomegalovirus (CMV), Epstein-Barr virus (EBV), Human herpes virus 6 (HHV-6), or JC virus (JCV).

    Through Week 14

Secondary Outcomes (2)

  • Average Number of Clinically Significant Infections or Episodes of End-Organ Disease Through Week 26

    Through Week 26

  • Number of Participants With Clinically Significant Infections or Episodes of End-Organ Disease Due to Each Virus

    Through Week 14

Study Arms (2)

Posoleucel (ALVR105)

EXPERIMENTAL

Administered as 2-4 milliliter infusion, visually identical to placebo

Biological: Posoleucel (ALVR105)

Placebo

PLACEBO COMPARATOR

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Biological: Placebo

Interventions

Administered as 2-4 milliliter infusion, visually identical to placebo

Also known as: Viralym-M
Posoleucel (ALVR105)
PlaceboBIOLOGICAL

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Placebo

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Any age at the day of screening visit.
  • No known or suspected clinically significant disease from AdV, BKV, CMV, EBV, HHV-6, and/or JCV
  • Within 25 days of receiving a first allogeneic HCT and have demonstrated clinical engraftment at time of dosing
  • Meet one or more of the following criteria at the time of randomization:
  • Related (sibling) donor with at least one mismatch at one of these HLA-gene loci: HLA-A, -B or -DR
  • Haploidentical donor
  • Matched or Mismatched unrelated donor
  • Use of umbilical cord blood as stem cell source
  • Ex vivo graft manipulation resulting in T cell depletion
  • Received anti-thymocyte globulin or alemtuzumab (Campath-1H)

You may not qualify if:

  • History of AdV, BKV, CMV, EBV, HHV-6, and/or JCV end-organ disease within 6 months prior to randomization
  • Evidence of active Grade \>2 acute GVHD
  • Presence of non-minor uncontrolled or progressive bacterial, viral or fungal infections
  • Known history or current (suspected) diagnosis of Grade ≥3 CRS requiring treatment associated with the administration of peptides, proteins, and/or antibodies
  • Ongoing therapy with high-dose systemic corticosteroids (ie, prednisone equivalent dose \>1.0 mg/kg/day) within 24 hours prior to dosing
  • Relapse of primary malignancy other than minimal residual disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (88)

University of Alabama at Birmingham Children's of Alabama

Birmingham, Alabama, 35233, United States

Location

Honor Health Research Institute

Scottsdale, Arizona, 85258, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

University of California, Los Angeles (UCLA)

Los Angeles, California, 90095, United States

Location

Stanford University

Palo Alto, California, 94304, United States

Location

University of California San Francisco - Benioff Children's Hospital

San Francisco, California, 94143, United States

Location

University of Colorado Hospital

Aurora, Colorado, 80045, United States

Location

Yale University School of Medicine - Yale Cancer Center

New Haven, Connecticut, 06520, United States

Location

Childrens National Health System

Washington D.C., District of Columbia, 20010, United States

Location

University of Florida (UF) - Gainesville

Gainesville, Florida, 32610, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Northside Hospital

Atlanta, Georgia, 30342, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Indiana University Hospital Simon Comprehensive Cancer Center

Indianapolis, Indiana, 46202, United States

Location

University of Kansas Hospital

Kansas City, Kansas, 66160, United States

Location

University of Maryland

Baltimore, Maryland, 21201, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Roswell Park Cancer Institute

Buffalo, New York, 14263, United States

Location

Columbia University

New York, New York, 10032, United States

Location

Weill Cornell Medical College

New York, New York, 10065, United States

Location

Stony Brook University Hospital Cancer Center

Stony Brook, New York, 11794, United States

Location

Carolinas Medical Center/Levine

Charlotte, North Carolina, 28203, United States

Location

Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Children's Medical Center Dallas

Dallas, Texas, 75235, United States

Location

University of Utah/Primary Childrens Hospital

Salt Lake City, Utah, 84113, United States

Location

University of Virginia

Charlottesville, Virginia, 22908, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Froedtert Hospital and the Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Royal Adelaide Hospital

Adelaide, Australia

Location

Austin Health

Heidelberg, Australia

Location

Royal Brisbane and Women's Hospital

Herston, Australia

Location

Royal Melbourne Hospital

Parkville, Australia

Location

Queensland Children's Hospital

South Brisbane, Australia

Location

Westmead Hospital

Westmead, Australia

Location

A.Z. Sint-Jan Brugge Oostende AV

Bruges, Belgium

Location

Institut Jules Bordet and the Childrens Hospital

Brussels, Belgium

Location

University Hospital Gasthuisberg and Leuven

Leuven, Belgium

Location

Alberta Children's Hospital

Calgary, Canada

Location

Cellular Therapy Program - CHU Sainte-Justine (McGill)

Montreal, Canada

Location

Hopital Maisonneve Rosemont

Montreal, Canada

Location

The Hospital for Sick Children Blood & Marrow Transplant / Cellular Therapy Program

Toronto, Canada

Location

UHN Blood and Marrow Transplant (BMT) Program (Princess Margaret) Cancer Center

Toronto, Canada

Location

Leukemia/ BMT Program of British Columbia - Vancouver General Hospital

Vancouver, Canada

Location

Centre Hospitalier Regional Universitaire de Lille

Lille, France

Location

CHU de Nantes

Nantes, France

Location

AP-HP Hopital Saint-Louis

Paris, France

Location

Hopital Saint Antoine

Paris, France

Location

Hopital Universitaire Robert Debre

Paris, France

Location

Centre Hospitalier Lyon Sud

Pierre-Bénite, France

Location

IUCT-Oncopole

Toulouse, France

Location

Azienda Ospedaliero-Universitaria Careggi

Florence, Italy

Location

Ospedale San Raffaele

Milan, Italy

Location

Fondazione I.R.C.C.S. Policlinico San Matteo

Pavia, Italy

Location

IRCSS Ospedale Pediatrico Bambino Gesu

Roma, Italy

Location

University of Sacred Heart Policlinico A. Gemelli

Rome, Italy

Location

Humanitas Cancer Center

Rozzano, Italy

Location

Azienda Ospedaliera Universitaria Integrata Verona (AOUI)

Verona, Italy

Location

Pusan National University Hospital

Busan, South Korea

Location

Chonnam National University Hwasun Hospital

Hwasun, South Korea

Location

Samsung Medical Center

Seoul, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

Seoul St. Mary's Hospital

Seoul, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, South Korea

Location

Institut Catala d'Oncologia

Barcelona, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, Spain

Location

Hospital Regional Universitario de Malaga

Málaga, Spain

Location

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, Spain

Location

Acibadem Adana Hospital

Adana, Turkey (Türkiye)

Location

Baskent Adana Hospital

Adana, Turkey (Türkiye)

Location

Ankara Onkoloji Egitim Ve Arastirma Hastanesi

Ankara, Turkey (Türkiye)

Location

Ankara University Hospital

Ankara, Turkey (Türkiye)

Location

Gazi University Medical Faculty Hospital

Ankara, Turkey (Türkiye)

Location

Medical Park Hospital

Antalya, Turkey (Türkiye)

Location

Ege University Medical Faculty

Izmir, Turkey (Türkiye)

Location

Anadolu Medical Center Hospital

Kocaeli, Turkey (Türkiye)

Location

Inonu University Turgut Özal Medical Centre

Malatya, Turkey (Türkiye)

Location

Bristol Haematology and Oncology Centre

Bristol, United Kingdom

Location

University Hospitals Bristol - Bristol Hospital for Children

Bristol, United Kingdom

Location

Addenbrooke's Hospital

Cambridge, United Kingdom

Location

Queen Elizabeth University Hospital - Glasgow

Glasgow, United Kingdom

Location

Great Ormond Street Hospital for Children

London, United Kingdom

Location

Related Publications (3)

  • Posoleucel (ALVR105), an Off-the-Shelf, Multivirus-Specific T-Cell Therapy, for the Prevention of Viral Infections Post-HCT: Results from an Open-Label Cohort of a Phase 2 Trial Sanjeet S Dadwal, Michael Shuster, Gary Douglas Myers, Keith Boundy, Marshelle Warren, Elizabeth Stoner, Thuy Truong, Joshua A. Hill Blood (2021) 138 (Supplement 1): 1760.

    BACKGROUND
  • Tzannou I, Papadopoulou A, Naik S, Leung K, Martinez CA, Ramos CA, Carrum G, Sasa G, Lulla P, Watanabe A, Kuvalekar M, Gee AP, Wu MF, Liu H, Grilley BJ, Krance RA, Gottschalk S, Brenner MK, Rooney CM, Heslop HE, Leen AM, Omer B. Off-the-Shelf Virus-Specific T Cells to Treat BK Virus, Human Herpesvirus 6, Cytomegalovirus, Epstein-Barr Virus, and Adenovirus Infections After Allogeneic Hematopoietic Stem-Cell Transplantation. J Clin Oncol. 2017 Nov 1;35(31):3547-3557. doi: 10.1200/JCO.2017.73.0655. Epub 2017 Aug 7.

    PMID: 28783452BACKGROUND
  • Vasileiou S, Kuvalekar M, Velazquez Y, Watanabe A, Leen AM, Gilmore SA. Phenotypic and functional characterization of posoleucel, a multivirus-specific T cell therapy for the treatment and prevention of viral infections in immunocompromised patients. Cytotherapy. 2024 Aug;26(8):869-877. doi: 10.1016/j.jcyt.2024.03.012. Epub 2024 Mar 19.

MeSH Terms

Conditions

Adenoviridae InfectionsCytomegalovirus InfectionsEpstein-Barr Virus Infections

Condition Hierarchy (Ancestors)

DNA Virus InfectionsVirus DiseasesInfectionsHerpesviridae InfectionsTumor Virus Infections

Limitations and Caveats

The Sponsor decided to discontinue the Phase 3 part of the trial on 22 Dec 2023 following a pre-planned DSMB futility analysis concluding the study was unlikely to meet its primary endpoint; no safety concerns were identified. Data was not collected for efficacy analyses at Week 26 as planned. Participants were monitored through Week 26 for safety analyses.

Results Point of Contact

Title
Kevin Anderson
Organization
AlloVir, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 22, 2022

First Posted

March 31, 2022

Study Start

March 24, 2022

Primary Completion

January 30, 2024

Study Completion

January 30, 2024

Last Updated

May 16, 2024

Results First Posted

May 16, 2024

Record last verified: 2024-04

Data Sharing

IPD Sharing
Will not share

Locations