NCT05054361

Brief Summary

To investigate in a prospective way changes in Mucosal-Associated Invariant T (MAIT) cells frequency, phenotype and function in link with the gut microbiota, gut integrity and the presence of Coxsackie virus B in two cohorts of pediatric patients: patients with a high genetic risk of type 1 diabetes and pediatric patients with recently diagnosed T1D by comparison with control subjects Tasks:

  1. 1.To measure blood MAIT cells frequency, phenotype and function in the three cohorts
  2. 2.To analyze gut microbiota and the presence of Coxsackie B enterovirus (CVB) and their impact on MAIT cell function
  3. 3.To evaluate gut integrity and analyze the gut mucosa
  4. 4.To integrate all the data obtained with T1D development and evolution

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
180

participants targeted

Target at P50-P75 for all trials

Timeline
15mo left

Started Jan 2022

Longer than P75 for all trials

Geographic Reach
1 country

2 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress77%
Jan 2022Aug 2027

First Submitted

Initial submission to the registry

June 8, 2021

Completed
4 months until next milestone

First Posted

Study publicly available on registry

September 23, 2021

Completed
3 months until next milestone

Study Start

First participant enrolled

January 1, 2022

Completed
4.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 11, 2026

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

August 14, 2027

Last Updated

April 13, 2026

Status Verified

April 1, 2026

Enrollment Period

4.6 years

First QC Date

June 8, 2021

Last Update Submit

April 8, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • blood MAIT cells frequency

    percentage of MAIT cells in the peripheral blood

    Sample collected the day of enrollment (Control group and at risk patients) or up to 7 days after diagnosis and day of enrollment (recent onset group)

Secondary Outcomes (8)

  • MAIT cells membrane markers analysis

    Sample collected the day of enrollment (Control group and at risk patients) or up to 7 days after diagnosis and day of enrollment (recent onset group)

  • Cytokines production in the cytoplasm of the MAIT

    Sample collected the day of enrollment (Control group and at risk patients) or up to 7 days after diagnosis and day of enrollment (recent onset group)

  • MAIT cell ligands measurements

    Sample collected the day of enrollment (Control group and at risk patients) or up to 7 days after diagnosis and day of enrollment (recent onset group)

  • Presence of CVB in the stools

    Sample collected the day of enrollment (Control group and at risk patients) or up to 7 days after diagnosis and day of enrollment (recent onset group)

  • Blood immunoglobulins against CVB infection statu

    Sample collected the day of enrollment (Control group and at risk patients) or up to 7 days after diagnosis and day of enrollment (recent onset group)

  • +3 more secondary outcomes

Study Arms (4)

recent onset patients

patients with recently diagnosed type 1 diabetes

Diagnostic Test: MAIT cells analysisDiagnostic Test: MAIT cytokines production analysisDiagnostic Test: Lactulose/Mannitol TestProcedure: UGI EndoscopyDiagnostic Test: Coxsackie virus B infection status

at risk patients

patients with a high genetic risk type 1 diabetes

Diagnostic Test: MAIT cells analysisDiagnostic Test: MAIT cytokines production analysisDiagnostic Test: Lactulose/Mannitol TestDiagnostic Test: Coxsackie virus B infection status

control subjects

control patients (no risk of type 1 diabetes and no diagnosed type 1 diabetes)

Diagnostic Test: MAIT cells analysisDiagnostic Test: MAIT cytokines production analysisDiagnostic Test: Lactulose/Mannitol TestDiagnostic Test: Coxsackie virus B infection status

control subjects for endoscopy

patients without type 1 diabetes requiring UGI endoscopy for any medical reason

Diagnostic Test: MAIT cells analysisDiagnostic Test: MAIT cytokines production analysisProcedure: UGI EndoscopyDiagnostic Test: Coxsackie virus B infection status

Interventions

MAIT cells analysisDIAGNOSTIC_TEST

For FACS analysis, MAIT cells will be identified as CD3+ CD4- CD161high Vα7.2+ T cells. Surface markers will be analyzed to determine their activation status (CD25, CD69, CD44), their exhaustion (PD1, KLRG1, TIM3), their migration capacity (CCR6), and their proliferation and survival will be analyzed by Ki67 and BCL2 expression.

at risk patientscontrol subjectscontrol subjects for endoscopyrecent onset patients

Cytokine production will be assessed after PMA-ionomycin activation, followed by intracytoplasmic staining with antibodies against IL-2, IFN-γ TNF-α, IL-2, IL-4, IL-10, IL-13, IL-17 and granzyme B. To determine the capacity of MAIT cells to response to TCR stimulation (exhaustion), in vitro stimulation will be performed in the presence of specific bacterial ligands. Activation marker expression will be analyzed by FACS and cytokines released in the supernatant by Cytometry based assay.

at risk patientscontrol subjectscontrol subjects for endoscopyrecent onset patients

After an overnight fast, the patients will drink 50 ml solution of 5 g lactulose and 2 g mannitol. Urine will be collected during before and 5 hours later.

at risk patientscontrol subjectsrecent onset patients
UGI EndoscopyPROCEDURE

Duodenal biopsy collection and analysis. Biopsies will be analyzed by qPCR for the expression of key epithelial molecules such as the fucosyl transferase 2 (fut2), tight junction proteins (occludin, claudin4), antimicrobial peptides (Reg3, LL37) and mucus component (mucin 2). Immune cells function will also be assessed by q-PCR for key cytokines/molecules such as IL-23, IL-17, IL-22, Foxp3, IL-10, TGFb and CVB.

control subjects for endoscopyrecent onset patients

Serology against CVB and CVB specific-qPCR measurement in gut microbiota samples will be performed in all patients of the three cohorts, and analysis of the gut mucosa by qPCR and immunochemistry with anti-CVB VP1 protein mAb will be performed on a subset of patients.

at risk patientscontrol subjectscontrol subjects for endoscopyrecent onset patients

Eligibility Criteria

Age12 Months - 15 Years
Sexall
Healthy VolunteersYes
Age GroupsChild (0-17)
Sampling MethodNon-Probability Sample
Study Population

Study population: patients recently diagnosed with type 1 diabetes and patients with a high risk of type 1 diabetes

You may qualify if:

  • Recent onset group
  • age \> 12 months and \< 15 years
  • recently diagnosed type 1 diabetes according ISPAD criteria
  • At risk subjects:
  • age \> 12 months and \< 15 years
  • siblings of type 1 diabetic patient
  • HLA DR3 and DR4 positive
  • Control subjects:
  • age \> 12 months and \< 15 years
  • no HLA associated with high risk type 1 diabetes
  • no antibodies against pancreas antigenes
  • Control subjects for UGI endoscopy:
  • age \> 12 months and \< 15 years
  • suspicion of coeliac disease or gastritis

You may not qualify if:

  • For all groups:
  • no health care insurance
  • parents or tutors unable to sign the consent
  • personal history of autoimmune disease and/or inflammatory disease except from T1D for RD and CE groups
  • pregnant subjects
  • medical contraindication of anesthetic topics
  • For control subjects for UGI endoscopy control and Recent onset-endoscopy group:
  • age below 8 years for Recent onset-endoscopy group
  • age below 4 for UGI endoscopy control group
  • cardiac or respiratory insufficiency, cardiac rhythm disorders, coagulation disease, patients treated with anticoagulant or antiaggregant drug
  • history of allergy to anesthetic drug

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Hopital privé d'Antony

Antony, 92160, France

NOT YET RECRUITING

Hopital Necker enfants malades

Paris, 75015, France

RECRUITING

Related Publications (2)

  • Rouxel O, Da Silva J, Beaudoin L, Nel I, Tard C, Cagninacci L, Kiaf B, Oshima M, Diedisheim M, Salou M, Corbett A, Rossjohn J, McCluskey J, Scharfmann R, Battaglia M, Polak M, Lantz O, Beltrand J, Lehuen A. Cytotoxic and regulatory roles of mucosal-associated invariant T cells in type 1 diabetes. Nat Immunol. 2017 Dec;18(12):1321-1331. doi: 10.1038/ni.3854. Epub 2017 Oct 9.

    PMID: 28991267BACKGROUND
  • Rouland M, Beaudoin L, Rouxel O, Bertrand L, Cagninacci L, Saffarian A, Pedron T, Gueddouri D, Guilmeau S, Burnol AF, Rachdi L, Tazi A, Mouries J, Rescigno M, Vergnolle N, Sansonetti P, Christine Rogner U, Lehuen A. Gut mucosa alterations and loss of segmented filamentous bacteria in type 1 diabetes are associated with inflammation rather than hyperglycaemia. Gut. 2022 Feb;71(2):296-308. doi: 10.1136/gutjnl-2020-323664. Epub 2021 Feb 16.

    PMID: 33593807BACKGROUND

Biospecimen

Retention: SAMPLES WITHOUT DNA

blood, stools, urines and gut mucosa samples

Central Study Contacts

jacques beltrand, MD, PhD

CONTACT

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER GOV
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 8, 2021

First Posted

September 23, 2021

Study Start

January 1, 2022

Primary Completion (Estimated)

August 11, 2026

Study Completion (Estimated)

August 14, 2027

Last Updated

April 13, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will not share

Locations