NCT05037825

Brief Summary

The microbiome has the potential to serve as a robust biomarker of clinical response to immunotherapy. Additionally, microbial manipulation, through diet, exercise, prebiotics, probiotics, or microbially-derived metabolites, may prove to be beneficial in promoting anti-tumor immune responses. However, large prospective studies in humans with longitudinal sample collection and standardized methods are needed to understand how microbiota and their byproducts affect cancer therapies, particularly among patients undergoing identical therapy but experiencing different outcomes. The proposed observational study builds upon these hypotheses by proposing a large cohort design to further assess the associations between the gut microbiota (composition and function), host immune system, and ICI treatment efficacy across multiple cancer types.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
800

participants targeted

Target at P75+ for all trials

Timeline
29mo left

Started Nov 2021

Longer than P75 for all trials

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress65%
Nov 2021Sep 2028

First Submitted

Initial submission to the registry

August 2, 2021

Completed
1 month until next milestone

First Posted

Study publicly available on registry

September 8, 2021

Completed
3 months until next milestone

Study Start

First participant enrolled

November 22, 2021

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 14, 2023

Completed
5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 14, 2028

Expected
Last Updated

April 27, 2022

Status Verified

April 1, 2022

Enrollment Period

1.8 years

First QC Date

August 2, 2021

Last Update Submit

April 25, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in microbiome composition from baseline to after Cycle 2 of checkpoint therapy (6-8 weeks) by analyzing longitudinally-collected stool specimens of 800 patients with primary NSCLC, MM, RCC, and TNBC

    Microbiome evaluation with whole metagenome shotgun sequencing to assess changes in the relative abundance of microbial taxa (measured as percentage abundance per microbial species and changes in percentage abundance between baseline and cycle 2 timepoints) in patients who are receiving checkpoint blockade immunotherapy as the standard of care

    prior to initiation of checkpoint therapy (i.e. "Baseline") and at the end of Cycle 2 of checkpoint blockade immunotherapy (at approximately 6-8 weeks) ]

Secondary Outcomes (3)

  • Microbiome samples correlation

    Time Frame: prior to initiation of checkpoint therapy (i.e. "Baseline") and at the end of Cycle 2 (at approximately 6-8 weeks)

  • Microbiome correlation to blood biomarkers

    Time Frame: prior to initiation of checkpoint therapy (i.e. "Baseline") and at the end of Cycle 2 (at approximately 6-8 weeks)

  • Blood samples correlation

    Time Frame: prior to initiation of checkpoint therapy (i.e. "Baseline") and at the end of Cycle 2 (at approximately 6-8 weeks)

Interventions

anti-PD-1, anti-PD-L1, or anti-CTLA-4 as a single agent or in combination with another checkpoint inhibitor or other treatment agent or modality (e.g., targeted therapy, chemotherapy, surgery, radiation, etc.) in accordance with FDA-labeled use of the agent

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

The investigator propose to enroll 800 cancer patients (NSCLC, MM, RCC, and TNBC; any stage) who are about to begin standard of care ICI therapy into a multi-site prospective observational study of the gut microbiome.

You may qualify if:

  • Men or women ≥18 years of age
  • Screened negative for COVID-19 symptoms at time of consent, as per institutional policy and as applicable for the duration of the COVID-19 pandemic
  • Diagnosed with stages I-IV primary NSCLC, MM, TNBC or RCC
  • Plan to be treated at a partner cancer site with a checkpoint inhibitor (anti-PD-1, anti-PD-L1, or anti-CTLA-4) as a single agent or in combination with another checkpoint inhibitor or other treatment agent or modality (e.g., targeted therapy, chemotherapy, surgery, radiation, etc.) in accordance with FDA-labeled use of the agent
  • Able to provide informed consent and answer study questionnaires in either English or Spanish
  • Able to provide stool specimens for research purposes

You may not qualify if:

  • Mental incapacity
  • Incarcerated individuals
  • Pregnancy (by self-report of pregnancy status)
  • Experiencing active brain metastasis/metastases
  • Treatment with checkpoint inhibitor in off-label capacity or through a clinical/interventional trial
  • Active participation in an immuno-oncology clinical/interventional trial or pharma-sponsored observational study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Baptist Health Clinical Research

Elizabethtown, Kentucky, 42701, United States

RECRUITING

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell LungMelanomaCarcinoma, Renal CellTriple Negative Breast Neoplasms

Interventions

Immune Checkpoint Inhibitors

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract DiseasesNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsSkin DiseasesSkin and Connective Tissue DiseasesAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialKidney NeoplasmsUrologic NeoplasmsUrogenital NeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesKidney DiseasesUrologic DiseasesMale Urogenital DiseasesBreast NeoplasmsBreast Diseases

Intervention Hierarchy (Ancestors)

Molecular Mechanisms of Pharmacological ActionPharmacologic ActionsChemical Actions and UsesAntineoplastic Agents, ImmunologicalAntineoplastic AgentsTherapeutic Uses

Central Study Contacts

Hanane Arib, MS

CONTACT

Peter McCaffrey, MD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 2, 2021

First Posted

September 8, 2021

Study Start

November 22, 2021

Primary Completion

September 14, 2023

Study Completion (Estimated)

September 14, 2028

Last Updated

April 27, 2022

Record last verified: 2022-04

Locations