NCT04966416

Brief Summary

Calcinosis, i.e. crystal-like nodules are troublesome complication of systemic sclerosis, an autoimmune disease. Pyrophosphate inhibits its formation is laborytory. We would like to test if orally administered pyrophosphate prevents calcinosis formation.

Trial Health

65
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
60

participants targeted

Target at P25-P50 for not_applicable

Timeline
1mo left

Started Aug 2023

Typical duration for not_applicable

Status
not yet recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress95%
Aug 2023Jun 2026

First Submitted

Initial submission to the registry

July 14, 2021

Completed
5 days until next milestone

First Posted

Study publicly available on registry

July 19, 2021

Completed
2 years until next milestone

Study Start

First participant enrolled

August 1, 2023

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2025

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2026

Expected
Last Updated

May 25, 2023

Status Verified

May 1, 2023

Enrollment Period

1.9 years

First QC Date

July 14, 2021

Last Update Submit

May 23, 2023

Conditions

Keywords

calcinosispyrophosphate

Outcome Measures

Primary Outcomes (1)

  • Change in the size of calcinosis nodues.

    Volumetric assessment with low energy CT

    52 weeks+ 16 weeks

Secondary Outcomes (3)

  • Change of the severity of sympthoms caused by calcinosis

    52 weeks+ 16 weeks

  • Change of the activity of calcinosis

    52 weeks+ 16 weeks

  • Change of the size of calcinosis by ultrasound

    52 weeks+ 16 weeks

Study Arms (2)

Pyrophosphate

EXPERIMENTAL

Disodium pyrophosphate

Dietary Supplement: Pyrophosphate

Placebo

PLACEBO COMPARATOR

Glucose

Dietary Supplement: Placebo

Interventions

PyrophosphateDIETARY_SUPPLEMENT

50 mg/kg bwt once daily in gelatine capsules.

Pyrophosphate
PlaceboDIETARY_SUPPLEMENT

Glucose in gelatine capsules.

Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • to meet ACR/ EULAR classification criteria

You may not qualify if:

  • severe upper minfestation of SSC
  • hypo- or hyperthyreoidism
  • QT prolongation on ECG

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Related Publications (2)

  • Hsu VM, Kozak E, Li Q, Bocskai M, Schlesinger N, Rosenthal A, McClure ST, Kovacs L, Balint L, Szamosi S, Szucs G, Carns M, Aren K, Goldberg I, Varadi A, Varga J. Inorganic pyrophosphate is reduced in patients with systemic sclerosis. Rheumatology (Oxford). 2022 Mar 2;61(3):1158-1165. doi: 10.1093/rheumatology/keab508.

    PMID: 34152415BACKGROUND
  • Dedinszki D, Szeri F, Kozak E, Pomozi V, Tokesi N, Mezei TR, Merczel K, Letavernier E, Tang E, Le Saux O, Aranyi T, van de Wetering K, Varadi A. Oral administration of pyrophosphate inhibits connective tissue calcification. EMBO Mol Med. 2017 Nov;9(11):1463-1470. doi: 10.15252/emmm.201707532.

    PMID: 28701330BACKGROUND

MeSH Terms

Conditions

Scleroderma, SystemicScleroderma, DiffuseCalcinosis

Interventions

diphosphoric acid

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesSkin DiseasesCalcium Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Study Officials

  • László Kovács, MD, Ph.D.

    Szeged University

    PRINCIPAL INVESTIGATOR
  • András Váradi, PhD, DSc

    Department of Enzymology, Research Centre for Natural Sciences

    STUDY DIRECTOR

Central Study Contacts

László Kovács, MD, PhD

CONTACT

Study Design

Study Type
interventional
Phase
not applicable
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor

Study Record Dates

First Submitted

July 14, 2021

First Posted

July 19, 2021

Study Start

August 1, 2023

Primary Completion

June 30, 2025

Study Completion (Estimated)

June 30, 2026

Last Updated

May 25, 2023

Record last verified: 2023-05