NCT04923594

Brief Summary

This is a double-blind, randomized, placebo-controlled, multicenter trial of NLS-2 in adult patients with narcolepsy. The study will enroll approximately 60 patients and eligible patients will be treated to receive either NLS-2 or placebo for 4-weeks.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
67

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Sep 2021

Shorter than P25 for phase_2

Geographic Reach
1 country

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 9, 2021

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 11, 2021

Completed
3 months until next milestone

Study Start

First participant enrolled

September 13, 2021

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2022

Completed
Last Updated

August 12, 2022

Status Verified

August 1, 2022

Enrollment Period

10 months

First QC Date

June 9, 2021

Last Update Submit

August 11, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in ESS Score From Baseline to Week 4

    Change in Epworth Sleepiness Scale (ESS) score from Baseline to Week 4. A negative change from baseline represents improvement in excessive sleepiness. The ESS is a self-administered questionnaire with 8 questions. Each activity is scored on a scale ranging from 0-3, with 0 = would never fall asleep, and 3 = high chance of falling asleep. The total score ranges from 0-24, with a higher number representing an increased propensity for sleepiness.

    Baseline to Week 4

Secondary Outcomes (1)

  • Subjects Reported Improved on the Patient Global Impression of Change (PGIc) at Week 4

    Baseline to Week 4

Study Arms (2)

NLS-2 (mazindol extended release)

ACTIVE COMPARATOR

2 mg dosed orally, once daily for 1 week; followed by 3 mg dosed orally, once daily for up to 3 weeks (total of 4 weeks)

Drug: mazindol extended release

Placebo

PLACEBO COMPARATOR

Dosed orally, once daily for up to 4 weeks

Drug: Placebo

Interventions

Dosed orally, once daily for up to 3 weeks

Also known as: NLS-2
NLS-2 (mazindol extended release)

Dosed orally, once daily for up to 4 weeks.

Placebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males and females between 18 and 65 years of age, inclusive
  • Diagnosis of narcolepsy according to ICSD-3 (International Classification of Sleep Disorders, 3rd Edition) or Diagnostic and Statistical Manual of Mental Disorders, 5th Edition (DSM-5) criteria
  • Body mass index from 18 to 40 kg/m2, inclusive
  • Consent to use a medically acceptable method of contraception
  • Willing and able to provide written informed consent

You may not qualify if:

  • Female subjects who are pregnant, nursing, or lactating
  • Any other clinically relevant medical, behavioral, or psychiatric disorder other than narcolepsy that is associated with excessive sleepiness
  • History or presence of bipolar disorder, bipolar related disorders, schizophrenia, schizophrenia spectrum disorders, or other psychotic disorders according to DSM-5 criteria
  • Use of any over-the-counter (OTC) or prescription medications that could affect the evaluation of excessive sleepiness
  • Use of any medications that could affect the evaluation of cataplexy
  • Received an investigational drug in the past 30 days or five half-lives (whichever is longer)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Sleep Disorders Center of Alabama

Birmingham, Alabama, 35213, United States

Location

Stanford Sleep Medicine Center

Redwood City, California, 94063, United States

Location

Pacific Research Network

San Diego, California, 92103, United States

Location

St. Francis Sleep Allergy and Lung Institute

Clearwater, Florida, 33765, United States

Location

Sleep Medicine Specialists of South Florida

Miami, Florida, 33126, United States

Location

Ivetmar Medical Group

Miami, Florida, 33155, United States

Location

The Angel Medical Research Corporation

Miami Lakes, Florida, 33016, United States

Location

Treken Primary care

Atlanta, Georgia, 30315, United States

Location

NeuroTrials Research

Atlanta, Georgia, 30328, United States

Location

Clinical Research Institute

Stockbridge, Georgia, 30281, United States

Location

Hawaii Pacific Neuroscience Clinical Research Center

Honolulu, Hawaii, 96817, United States

Location

The Center For Sleep & Wake Disorders

Chevy Chase, Maryland, 20815, United States

Location

Sleep and Attention Disorders

Sterling Heights, Michigan, 48314, United States

Location

Neurology and Sleep Disorders Clinic

Columbia, Missouri, 65212, United States

Location

Carolinas Sleep Specialists

Concord, North Carolina, 28025, United States

Location

Superior Clinical Research, LLC

Goldsboro, North Carolina, 27534, United States

Location

Advanced Respiratory and Sleep Medicine

Huntersville, North Carolina, 28078, United States

Location

Intrepid Research

Cincinnati, Ohio, 45245, United States

Location

Ohio Sleep Medicine Institute

Dublin, Ohio, 43017, United States

Location

Bogan Sleep Consultants

Columbia, South Carolina, 29201, United States

Location

Dharma PA d/b/a Southwest Family Medicine Associates

Dallas, Texas, 75235, United States

Location

Sleep Therapy & Research Center

San Antonio, Texas, 78229, United States

Location

MeSH Terms

Conditions

NarcolepsyDisorders of Excessive Somnolence

Condition Hierarchy (Ancestors)

Sleep Disorders, IntrinsicDyssomniasSleep Wake DisordersNervous System DiseasesMental Disorders

Study Officials

  • Carlos Camozzi, MD

    NLS Pharmaceutics

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 9, 2021

First Posted

June 11, 2021

Study Start

September 13, 2021

Primary Completion

June 30, 2022

Study Completion

June 30, 2022

Last Updated

August 12, 2022

Record last verified: 2022-08

Data Sharing

IPD Sharing
Will not share

Locations