NCT04920344

Brief Summary

This is a non-randomized, open-label phase II clinical trial that studies the effect of reduced dose radiation therapy and chemotherapy after surgery in treating patients with human papillomavirus (HPV) caused throat cancer. Giving reduced dose radiation therapy and chemotherapy after surgery may improve quality of life compared with standard of care primary chemoradiation approach without compromising survival.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
15

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Jul 2021

Typical duration for phase_2

Geographic Reach
1 country

3 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 2, 2021

Completed
7 days until next milestone

First Posted

Study publicly available on registry

June 9, 2021

Completed
1 month until next milestone

Study Start

First participant enrolled

July 19, 2021

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 8, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 8, 2025

Completed
Last Updated

November 3, 2023

Status Verified

November 1, 2023

Enrollment Period

3.8 years

First QC Date

June 2, 2021

Last Update Submit

November 1, 2023

Conditions

Outcome Measures

Primary Outcomes (3)

  • MD Anderson Dysphagia Index (MDADI)

    MDADI is a 20 item quality of life instrument specifically focusing on swallowing aspects. It was originally designed for head and neck cancer patients and has been widely used and validated in this population. The total score ranges from 20 to 100 with the higher score indicating higher level of function.

    At baseline.

  • MD Anderson Dysphagia Index (MDADI)

    MDADI is a 20 item quality of life instrument specifically focusing on swallowing aspects. It was originally designed for head and neck cancer patients and has been widely used and validated in this population. The total score ranges from 20 to 100 with the higher score indicating higher level of function.

    At 24 weeks post completion of therapy.

  • MD Anderson Dysphagia Index (MDADI)

    MDADI is a 20 item quality of life instrument specifically focusing on swallowing aspects. It was originally designed for head and neck cancer patients and has been widely used and validated in this population. The total score ranges from 20 to 100 with the higher score indicating higher level of function.

    At 1 year post completion of therapy.

Secondary Outcomes (9)

  • Locoregional control.

    At 3 years post completion of therapy

  • Disease free survival.

    At 3 years post completion of therapy

  • Progression free survival.

    At 3 years post completion of therapy

  • Overall survival.

    At 3 years post completion of therapy

  • University of Washington Quality of Life Questionnaire

    At baseline, 24 weeks and 1 year post completion of therapy

  • +4 more secondary outcomes

Study Arms (3)

GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))

ACTIVE COMPARATOR

After standard of care transoral surgery, patients whose small tumor was removed completely and have only one lymph node involved will undergo clinical observation.

Procedure: Transoral SurgeryProcedure: Incisional Tumor BiopsyOther: Circulating tumor deoxyribonucleic acid (ctDNA) levels assessmentOther: MD Anderson Dysphagia IndexOther: University of Washington Quality of Life QuestionnaireOther: Euro-QOL 5 dimension scale questionnaireDiagnostic Test: Modified barium swallow (MBS) evaluation with aspiration-penetration scale

GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)

EXPERIMENTAL

Patients whose tumor was removed completely but has certain features that make it more likely to come back such as growth around the nerves or into the vessels, or has more than one lymph nodes involved, will undergo external body radiation therapy (EBRT) RT 50Gy for 5 weeks in the absence of disease progression or unacceptable toxicity.

Procedure: Transoral SurgeryRadiation: External Beam Radiation TherapyProcedure: Incisional Tumor BiopsyOther: Circulating tumor deoxyribonucleic acid (ctDNA) levels assessmentOther: MD Anderson Dysphagia IndexOther: University of Washington Quality of Life QuestionnaireOther: Euro-QOL 5 dimension scale questionnaireDiagnostic Test: Modified barium swallow (MBS) evaluation with aspiration-penetration scale

GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

EXPERIMENTAL

Patients whose tumor has a "positive margin", which means the tumor could not be removed with healthy tissue around it or tumor grows significantly outside the lymph node will undergo EBRT RT 60 Gy for 6 weeks and receive cisplatin intravenously (IV) weekly 30mg/m2 for 6 weeks in the absence of disease progression or unacceptable toxicity.

Procedure: Transoral SurgeryRadiation: External Beam Radiation TherapyDrug: CisplatinProcedure: Incisional Tumor BiopsyOther: Circulating tumor deoxyribonucleic acid (ctDNA) levels assessmentOther: MD Anderson Dysphagia IndexOther: University of Washington Quality of Life QuestionnaireOther: Euro-QOL 5 dimension scale questionnaireDiagnostic Test: Modified barium swallow (MBS) evaluation with aspiration-penetration scale

Interventions

Patients will undergo transoral surgery

Also known as: Therapeutic Conventional Surgery
GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

Patients in Group II and Group III will undergo External Beam Radiation Therapy (EBRT) RT following transoral surgery.

Also known as: EBRT
GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

Patients in Group III will receive cisplatin, 30 mg/m2, administered intravenously weekly per for 6 weeks.

Also known as: Cisplatin Chemotherapy
GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

Incisional biopsy of the primary tumor site will be required to confirm p16/HPV status of the tumor

GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

Assess ctDNA levels at baseline, 2 weeks, 4 weeks, 10 weeks, 24 weeks and 1 year after the surgery.

Also known as: Circulating ctDNA levels assessment
GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

MDADI is a 20 item quality of life questionnaire specifically focusing on swallowing aspects. It was originally designed for head and neck cancer patients. The total score ranges from 20 to 100 with the higher score indicating higher level of function.

Also known as: MDADI
GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

University of Washington Questionnaire is a 15 item quality of life instrument specifically designed for head and neck cancer patients.

Also known as: UW QOL questionnaire
GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

A generic quality of life and cost utility instrument widely used and validated for multiple disease settings, including head and neck cancer.

Also known as: EQ-5D-5L
GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

The videofluoroscopic modified barium swallow (MBS) study is the gold standard for for the evaluation of dysphagia, and specifically, airway protective mechanisms. The penetration/aspiration (PEN/ASP) scale is a routinely used eight-point scale designed to describe the depth of bolus penetration into the airway and the patient response to the penetration or aspiration.

Also known as: MBS with PEN/ASP scale
GROUP I - Low Risk Recurrence (transoral surgery, clinical observation))GROUP II - Medium Risk Recurrence (transoral surgery, EBRT 50Gy)GROUP III - High Risk Recurrence (transoral surgery, EBRT 60Gy, cisplatin 30 mg/m2)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically proven squamous cell carcinoma of the oropharynx
  • Clinical stage T1-2, N0-N3, M0 by American Joint Committee on Cancer (AJCC) 8 criteria
  • Must have tumors deemed surgically resectable with acceptable morbidity
  • Estimated life expectancy of at least 12 weeks
  • Must give informed consent
  • Must have Eastern Cooperative Oncology Group (ECOG) performance status =\< 3
  • Must have detectable circulating HPV DNA levels
  • Platelets \>= 100,000/ul
  • Absolute neutrophil count (ANC) \>= 1,500/ul
  • Hemoglobin \> 8 g/dl (use of transfusion to achieve this is acceptable)
  • Total bilirubin \< 2 X institutional upper limit of normal (ULN)
  • Aspartate aminotransferase (AST) (serum glutamic-oxaloacetic transaminase \[SGOT\])/alanine aminotransferase (ALT) (serum glutamate pyruvate transaminase \[SGPT\]) \< 3 X institutional ULN
  • Serum creatinine \< 2 x institutional ULN or creatinine clearance \> 50 ml/min as determined by 24 hour collection or estimated by Cockcroft-Gault formula
  • Negative pregnancy test, if applicable

You may not qualify if:

  • Patients may not have received previous therapy for their head and neck squamous cell carcinoma (SCC), including chemotherapy, radiation therapy, or surgery beyond biopsy
  • Second primary malignancy. Exceptions are:
  • Patient had a second primary malignancy but has been treated and disease free for at least 3 years
  • In situ carcinoma (e.g. in situ carcinoma of the cervix)
  • Non-melanomatous carcinoma of the skin
  • Patients with metastatic disease beyond the neck will be excluded
  • Serious concomitant systemic disorders (including active infections) that would compromise the safety of the patient or compromise the patient's ability to complete the study, at the discretion of the investigator
  • Age \< 18 years
  • Patients with human immunodeficiency virus (HIV) infection are not automatically excluded, but must meet the following criteria: CD4 count is \> 499/cu mm and their viral load is \< 50 copies/ml. Use of highly active antiretroviral therapy (HAART) is allowed
  • Grade 3-4 electrolyte abnormalities (Common Terminology Criteria for Adverse Events \[CTCAE\], version \[v.\] 5)
  • Serum calcium (ionized or adjusted for albumin) \< 7 mg/dl (1.75 mmol/L) or \> 12.5 mg/dl (\> 3.1 mmol/L) despite intervention to normalize levels
  • Magnesium \< 0.9 mg/dl (\< 0.4 mmol/L) or \> 3 mg/dl (\> 1.23 mmol/L) despite intervention to normalize levels
  • Potassium \< 3.0 mmol/L or \> 6 mmol/L despite intervention to normalize levels
  • Sodium \< 130 mmol/L or \> 155 mmol/L despite intervention to normalize levels
  • Women who are pregnant, due to the teratogenic effects of radiation therapy and chemotherapy on the unborn fetus. Women of childbearing age must agree to undergo a pregnancy test prior to therapy and to use adequate contraception (hormonal or barrier method of birth control; abstinence) prior to study entry, for the duration of study participation and for 6 months after. Should a woman become pregnant or suspect she is pregnant while participating in this study, she should inform her treating physician immediately
  • +7 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08903, United States

Location

RWJBarnabas Health - Robert Wood Johnson University Hospital, New Brunswick

New Brunswick, New Jersey, 08903, United States

Location

Rutgers Cancer Institute of New Jersey at University Hospital

Newark, New Jersey, 07103, United States

Location

MeSH Terms

Conditions

Oropharyngeal Neoplasms

Interventions

CisplatinCirculating Tumor DNAPhysical Examination

Condition Hierarchy (Ancestors)

Pharyngeal NeoplasmsOtorhinolaryngologic NeoplasmsHead and Neck NeoplasmsNeoplasms by SiteNeoplasmsPharyngeal DiseasesStomatognathic DiseasesOtorhinolaryngologic Diseases

Intervention Hierarchy (Ancestors)

Chlorine CompoundsInorganic ChemicalsNitrogen CompoundsPlatinum CompoundsCell-Free Nucleic AcidsNucleic AcidsNucleic Acids, Nucleotides, and NucleosidesDNA, NeoplasmDNADiagnostic Techniques and ProceduresDiagnosis

Study Officials

  • Matin Imanguli, MD, DDS

    Rutgers Cancer Institute of New Jersey

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Assistant Professor. Chief of the Division of Head and Neck Surgical Oncology

Study Record Dates

First Submitted

June 2, 2021

First Posted

June 9, 2021

Study Start

July 19, 2021

Primary Completion

May 8, 2025

Study Completion

May 8, 2025

Last Updated

November 3, 2023

Record last verified: 2023-11

Data Sharing

IPD Sharing
Will not share

Locations