NCT04919512

Brief Summary

The purpose of this study is to evaluate the anti-tumor effects of TAR-200 in combination with intravenous (IV) cetrelimab and IV cetrelimab alone.

Trial Health

67
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Strong global presence with extensive site network
Enrollment
163

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jul 2022

Typical duration for phase_2

Geographic Reach
10 countries

109 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 8, 2021

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 9, 2021

Completed
1.1 years until next milestone

Study Start

First participant enrolled

July 7, 2022

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 4, 2025

Completed
1 year until next milestone

Results Posted

Study results publicly available

February 17, 2026

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

March 31, 2026

Completed
Last Updated

March 25, 2026

Status Verified

March 1, 2026

Enrollment Period

2.6 years

First QC Date

June 8, 2021

Results QC Date

January 29, 2026

Last Update Submit

March 12, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Pathologic Complete Response (pCR) Rate

    pCR was defined as percentage of participants who achieved complete pathologic response. Complete pathologic response is defined as ypT0N0 (no evidence of disease) as assessed by pathologic evaluation on radical cystectomy (RC) specimen. pCR was determined by central pathologic review.

    At Week 12

Secondary Outcomes (3)

  • Number of Participants With Treatment Emergent Adverse Event According to Common Terminology Criteria for Adverse Event (CTCAE) Version 5 Grades

    Cycle Day 1 up to Week 124

  • Number of Participants With Worst Post-baseline Laboratory Values Based on Common Terminology Criteria for Adverse Events (CTCAE)

    Cycle Day 1 up to Week 124

  • Recurrence-Free Survival (RFS)

    Cycle Day 1 up to Week 124

Study Arms (2)

Cohort 1: TAR-200 + Cetrelimab

EXPERIMENTAL

Participants will receive TAR-200 in combination with cetrelimab.

Drug: TAR-200Biological: Cetrelimab

Cohort 2: Cetrelimab

EXPERIMENTAL

Participants will receive cetrelimab.

Biological: Cetrelimab

Interventions

TAR-200 will be administered.

Also known as: JNJ-17000139
Cohort 1: TAR-200 + Cetrelimab
CetrelimabBIOLOGICAL

Cetrelimab will be administered.

Also known as: JNJ-63723283
Cohort 1: TAR-200 + CetrelimabCohort 2: Cetrelimab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically proven, cT2-T4a N0, M0 infiltrating urothelial carcinoma of the bladder. Initial diagnosis must have been within 120 days of randomization date. Participants with variant histologic subtypes are allowed if tumor(s) demonstrate urothelial predominance. However, the presence of small cell or neuroendocrine variants will make a participant ineligible
  • Participants with no residual tumor, or intravesical tumor size of less than or equal to (\<=)3 centimeter (cm) following transurethral resection of bladder tumor (TURBT) are eligible; debulking TURBT for any residual disease is encouraged but not mandated. Participants with persistent tumors greater than (\>)3 cm at screening must undergo a second debulking, re-staging TURBT. Participants will be ineligible if any individual tumor is \>3 cm after debulking TURBT
  • Deemed eligible for and willing to undergo RC by the operating urologist
  • Eastern Cooperative Oncology Group (ECOG) performance status Grade 0 or 1
  • Thyroid function tests within normal range or stable on hormone supplementation per investigator assessment. Investigators may consult an endocrinologist for participant eligibility assessment in the case of equivocal or marginal tests results
  • All adverse events associated with any prior surgery must have resolved to common terminology criteria for adverse events (CTCAE) version 5.0 Grade less than (\<) 2 prior to randomization

You may not qualify if:

  • Must not have received prior systemic chemotherapy, targeted small molecule therapy, or radiation therapy within 2 weeks prior to starting study treatment
  • Participants must not have evidence of cT4b, or N1-3, or M1 disease based on central radiology staging (chest, abdomen, and pelvis must be performed using computed tomography \[CT\] or magnetic resonance imaging \[MRI\]) within 42 days prior to randomization
  • Presence of any bladder or urethral anatomic feature that, in the opinion of the Investigator, may prevent the safe placement, indwelling use, or removal of TAR-200
  • Prior systemic chemotherapy for urothelial cell carcinoma of the bladder at any time
  • Currently participating or has participated in a study of an investigational agent and received study therapy or investigational device within 4 weeks prior to enrollment
  • Participants with evidence of bladder perforation during diagnostic cystoscopy. Participant is eligible if perforation has resolved prior to dosing

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (109)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Urological Associates of Southern Arizona, P.C.

Tucson, Arizona, 85741, United States

Location

UAMS Winthrop P. Rockefeller Cancer Institute

Little Rock, Arkansas, 72205, United States

Location

Arkansas Urology

Little Rock, Arkansas, 72211, United States

Location

City of Hope

Duarte, California, 91010, United States

Location

Genesis Research

San Diego, California, 92123, United States

Location

Colorodo Urology- St. Anthony Hospital

Golden, Colorado, 80401, United States

Location

University of Florida Health Jacksonville

Jacksonville, Florida, 32209, United States

Location

Mayo Clinic

Jacksonville, Florida, 32224, United States

Location

Baptist Hospital of Miami

Miami, Florida, 33176, United States

Location

Winship Cancer Institute Emory University

Atlanta, Georgia, 30322, United States

Location

DuPage Medical Group

Lisle, Illinois, 60532, United States

Location

Urology of Indiana

Indianapolis, Indiana, 46260, United States

Location

First Urology

Jeffersonville, Indiana, 47130, United States

Location

University of Louisville - James Graham Brown Cancer Center

Louisville, Kentucky, 40202, United States

Location

University Of Maryland Medical Center

Baltimore, Maryland, 21201, United States

Location

Penn Medicine - PerelmanCenter for Advanced Medicine

Baltimore, Maryland, 21218, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Michigan Institute of Urology, PC

Troy, Michigan, 48084, United States

Location

University Of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Mayo Clinic 1

Rochester, Minnesota, 55905, United States

Location

Ellis Fischel Cancer Center

Columbia, Missouri, 65201, United States

Location

Washington University School Of Medicine - Center For Advanced Medicine (CAM)

St Louis, Missouri, 63110-1010, United States

Location

David C. Pratt Cancer Center

St Louis, Missouri, 63141, United States

Location

Robert Wood Johnson University Hospital

New Brunswick, New Jersey, 08901, United States

Location

Mount Sinai Queens Infusion Center

Astoria, New York, 11102, United States

Location

New York University Langone Medical Center

New York, New York, 10017, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

SUNY Upstate Medical University

Syracuse, New York, 13202, United States

Location

Associated Medical Professionals

Syracuse, New York, 13210, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

Wake Forest University Baptist Medical Center (WFUBMC) - Comprehensive Cancer Center

Winston-Salem, North Carolina, 27103, United States

Location

The Ohio State University

Columbus, Ohio, 43210, United States

Location

MidLantic Urology

Bala-Cynwyd, Pennsylvania, 19004, United States

Location

University Of Pittsburgh Medical Center UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

Carolina Urologic Research Center

Myrtle Beach, South Carolina, 29572, United States

Location

Urology Associates

Nashville, Tennessee, 37209, United States

Location

Houston Metro Urology

Houston, Texas, 77027, United States

Location

Urology San Antonio Research

San Antonio, Texas, 78229, United States

Location

Huntsman Cancer Institute

Salt Lake City, Utah, 84112, United States

Location

University of Washington School of Medicine

Seattle, Washington, 98195, United States

Location

AZ Sint Jan Brugge Oostende AV

Bruges, 8000, Belgium

Location

Algemeen Ziekenhuis Sint-Jan

Bruges, 8310, Belgium

Location

Ziekenhuis Oost-Limburg

Genk, 3600, Belgium

Location

Hopital de Jolimont

Haine Saint Paul La Louviere, 7100, Belgium

Location

ZNA Jan Palfijn

Merksem, 2170, Belgium

Location

Centre Interuniversitaire Ambroise Pare - Ambroise Paré

Mons, 7000, Belgium

Location

Clinique Tivoli Ducos

Bordeaux, 33000, France

Location

ICH Hopital A. Morvan

Brest, 29200, France

Location

Hopital Henri Mondor

Créteil, 94000, France

Location

Hôpital Privé Le Bois

Lille, 59000, France

Location

Polyclinique de Limoges - Francois Chenieux

Limoges, 87000, France

Location

Hopital de la Timone

Marseille, 13005, France

Location

CHU Montpellier

Montpellier, 34295, France

Location

CHU Nimes

Nîmes, 30029, France

Location

Hopital Europeen Georges-Pompidou

Paris, 75015, France

Location

Hopital Bichat Claude Bernard

Paris, 75877, France

Location

Hospices Civils de Lyon HCL

Pierre-Bénite, 69495, France

Location

Clinical La Croix Du Sud - Ramsay Santé

Quint-Fonsegrives, 31130, France

Location

HIA se Sainte-Anne - Toulon

Toulon, 83041, France

Location

Clinique Pasteur

Toulouse, 31076, France

Location

Staedtisches Klinikum Braunschweig

Braunschweig, 38118, Germany

Location

Agaplesion Frankfurter Diakonie Kliniken GmbH, Markus Krankenhaus

Frankfurt am Main, 60431, Germany

Location

Universitaetsklinikum Halle Saale

Halle, 06120, Germany

Location

Marien hospital Herne

Herne, 44625, Germany

Location

Vivantes Klinikum Am Urban

Kreuzberg, 10967, Germany

Location

Universitatsklinikum Munster

Münster, 48149, Germany

Location

Rambam Health Care Campus

Haifa, 3109601, Israel

Location

Carmel Medical Center

Haifa, 3436212, Israel

Location

Hadassah Medical Center

Jerusalem, 91120, Israel

Location

Rabin Medical Center - Hasharon Hospital

Petah Tikva, 49372, Israel

Location

The Chaim Sheba Medical Center

Ramat Gan, 52621, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 6423906, Israel

Location

Ospedale San Giuseppe Moscati di Avellino

Avellino, 83100, Italy

Location

Ospedale Civile Ramazzini

Carpi, 41012, Italy

Location

SPDC Villa Scassi

Genova, 16100, Italy

Location

IRCCS Ospedale San Raffaele

Milan, 20132, Italy

Location

Istituto Dei Tumori Di Milano

Milan, 20133, Italy

Location

Istituto Europeo di Oncologia

Milan, 20141, Italy

Location

Istituto Nazionale Tumori Fondazione G. Pascale

Naples, 80131, Italy

Location

Azienda Ospedaliero Universitaria Pisana

Pisa, 56126, Italy

Location

ASL Napoli 2 Nord-SM delle Grazie Hospital

Pozzuoli, 80078, Italy

Location

Istituto Nazionale Tumori Regina Elena

Roma, 00144, Italy

Location

IRCCS Istituto Clinico Humanitas

Rozzano, 20089, Italy

Location

Azienda Ospedaliera Universitaria Citta della Salute e della Scienza di Torino

Torino, 10126, Italy

Location

Ziekenhuisgroep Twente

Almelo, 7600, Netherlands

Location

Radboud Umcn

Nijmegen, 6525 GA, Netherlands

Location

Canisius-Wilhelmina Ziekenhuis

Nijmegen, 6532SZ, Netherlands

Location

Haga ziekenhuis

The Hague, 2545 AA, Netherlands

Location

Inje University Haeundae Paik Hospital

Busan, 612-030, South Korea

Location

Kyungpook National University Chilgok Hospital

Daegu, 41404, South Korea

Location

Keimyung University Dongsan Hospital

Daegu, 42601, South Korea

Location

Samsung Medical Center

Gangnam Gu, 06351, South Korea

Location

National Cancer Center

Goyang-si, 10408, South Korea

Location

Korea University Anam Hospital

Seoul, 02841, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Severance Hospital

Seoul, 03722, South Korea

Location

Gangnam Severance Hospital

Seoul, 06273, South Korea

Location

The Catholic University of Korea Seoul St Mary s Hospital

Seoul, 06591, South Korea

Location

Pusan National University Yangsan Hospital

Yangsan, 50612, South Korea

Location

Hosp Univ A Coruna

A Coruña, 15006, Spain

Location

Fund. Puigvert

Barcelona, 08041, Spain

Location

Hosp. Univ. San Cecilio

Granada, 18016, Spain

Location

Clinica Univ. de Navarra

Madrid, 28027, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hosp Virgen de La Victoria

Málaga, 29010, Spain

Location

Hosp. Univ. Marques de Valdecilla

Santander, 39002, Spain

Location

Barts Health NHS Trust

London, EC1A 7BE, United Kingdom

Location

Lancashire Teaching Hospitals NHS Foundation Trust Royal Preston Hospital

Preston, PR2 9HT, United Kingdom

Location

Related Publications (2)

  • Necchi A, Guerrero-Ramos F, Crispen PL, Herrera-Imbroda B, Garje R, Szabados B, Peyton CC, Pradere B, Ku JH, Shore N, Bogemann M, Preston MA, Xylinas E, Sanchez de Llano C, Gong C, Hasan M, Urtishak K, Battaglia S, Stitou H, Bhanvadia S, Sweiti H, Psutka SP. Gemcitabine Intravesical System Plus Cetrelimab or Cetrelimab Alone as Neoadjuvant Therapy in Muscle-Invasive Bladder Cancer: SunRISe-4 Primary Analysis and Biomarker Results. J Clin Oncol. 2026 Mar;44(7):586-597. doi: 10.1200/JCO-25-02382. Epub 2025 Dec 3.

  • Necchi A, Guerrero-Ramos F, Crispen PL, Herrera-Imbroda B, Garje R, Powles T, Peyton CC, Pradere B, Ku JH, Shore N, Bogemann M, Preston MA, Xylinas E, Sanchez de Llano C, Hasan M, Stitou H, Bhanvadia S, Sweiti H, Psutka SP. TAR-200 plus cetrelimab versus cetrelimab monotherapy as neoadjuvant therapy in patients with muscle-invasive bladder cancer who are ineligible for or decline neoadjuvant cisplatin-based chemotherapy (SunRISe-4): interim analysis of a randomised, open-label phase 2 trial. Lancet Oncol. 2025 Oct;26(10):1312-1322. doi: 10.1016/S1470-2045(25)00358-4. Epub 2025 Aug 27.

MeSH Terms

Conditions

Urinary Bladder Neoplasms

Condition Hierarchy (Ancestors)

Urologic NeoplasmsUrogenital NeoplasmsNeoplasms by SiteNeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesUrinary Bladder DiseasesUrologic DiseasesMale Urogenital Diseases

Results Point of Contact

Title
Medical Director Onc
Organization
Janssen Research & Development, LLC

Study Officials

  • Janssen Research & Development, LLC Clinical Trial

    Janssen Research & Development, LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

June 8, 2021

First Posted

June 9, 2021

Study Start

July 7, 2022

Primary Completion

February 4, 2025

Study Completion

March 31, 2026

Last Updated

March 25, 2026

Results First Posted

February 17, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

The data sharing policy of the Janssen Pharmaceutical Companies of Johnson \& Johnson is available at www.janssen.com/clinical-trials/transparency. As noted on this site, requests for access to the study data can be submitted through Yale Open Data Access (YODA) Project site at yoda.yale.edu

More information

Locations