NCT04886804

Brief Summary

The study has 2 parts. The first part is open to adults with different types of advanced cancer (solid tumours with changes in the HER2 gene) for whom previous treatment was not successful. The second part is open to people with non-small cell lung cancer with a specific mutation in the HER2 gene. The purpose of the first study part is to find the highest dose of a medicine called zongertinib the participants can tolerate. Once this dose is found, it will be used in the second study part to test whether zongertinib can make tumours shrink. In this study, zongertinib is given to people for the first time. Participants take zongertinib as tablets once a day or twice a day. The participants are in the study for as long as they benefit from and can tolerate treatment. Study doctors regularly check the participants' health and monitor the tumours. The doctors also take note of any unwanted effects that could have been caused by zongertinib.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
608

participants targeted

Target at P75+ for phase_1

Timeline
29mo left

Started Jul 2021

Longer than P75 for phase_1

Geographic Reach
17 countries

84 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress67%
Jul 2021Aug 2028

First Submitted

Initial submission to the registry

May 4, 2021

Completed
10 days until next milestone

First Posted

Study publicly available on registry

May 14, 2021

Completed
2 months until next milestone

Study Start

First participant enrolled

July 2, 2021

Completed
5.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 30, 2026

Expected
1.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 30, 2028

Last Updated

March 13, 2026

Status Verified

March 1, 2026

Enrollment Period

5.5 years

First QC Date

May 4, 2021

Last Update Submit

March 12, 2026

Conditions

Outcome Measures

Primary Outcomes (5)

  • Phase Ia: Maximum Tolerated Dose (MTD)

    Maximum tolerated dose is defined as the highest dose with less than 25% risk of the true Dose Limiting Toxicity (DLT) rate being equal to or above 33% during the MTD evaluation period in any studied regimen.

    At the end of Cycle 1 (each cycle is 21 days).

  • Phase Ia: Number of patients with Dose Limiting Toxicities (DLTs) in the MTD evaluation period

    At the end of Cycle 1 (each cycle is 21 days).

  • Phase Ib - Cohorts 1, 2 and 5 : Objective response (OR) as assessed by central independent review

    OR is defined as best overall response of complete response (CR) or partial response (PR), where best overall response is determined according to Response Evaluation Criteria In Solid Tumors (RECIST) version 1.1, from the first treatment administration until the earliest of disease progression, death or last evaluable tumor assessment before start of subsequent anticancer therapy, loss to follow-up or withdrawal of consent.

    From the start of the trial treatment until end of month 12, up to 12 months.

  • Phase Ib - Cohorts 3, 6, 7, 8, and 9: Objective response according to RECIST 1.1 by investigator assessment

    From the start of the trial treatment until end of month 12, up to 12 months.

  • Phase Ib: Cohort 4: Objective response according to Response Assessment in Neuro-Oncology for Brain Metastases (RANO-BM) by central independent review

    From the start of the trial treatment until end of month 12, up to 12 months.

Secondary Outcomes (30)

  • Phase Ia: Number of patients experiencing DLTs during the entire treatment period

    From the start of the trial treatment until end of month 8, up to 8 months.

  • Phase Ia: Maximum measured concentration of zongertinib in plasma (Cmax)

    On day 1 and on day 15 of Cycle 1 (each cycle is 21 days).

  • Phase Ia: Area under the concentration-time curve of zongertinib in plasma (AUC0-t2)

    On day 1 and on day 15 of Cycle 1 (each cycle is 21 days).

  • Phase Ib - Cohorts 1, 2 and 5: Duration of objective response (DoR) according to RECIST 1.1

    From the start of the trial treatment until end of month 12, up to 12 months.

  • Phase Ib - Cohorts 1, 2 and 5: Disease control (DC)

    From the start of the trial treatment until end of month 12, up to 12 months.

  • +25 more secondary outcomes

Study Arms (10)

Phase Ia - Dose escalation part

EXPERIMENTAL

Consecutive cohorts of patients treated with escalating doses of BI 1810631 monotherapy.

Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 1

EXPERIMENTAL
Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 2

EXPERIMENTAL
Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 3

EXPERIMENTAL
Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 4

EXPERIMENTAL
Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 5

EXPERIMENTAL
Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 6

EXPERIMENTAL

Cohort only in the United States of America (USA)

Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 7

EXPERIMENTAL

Cohort only in Japan

Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 8

EXPERIMENTAL

Cohort only in the United States of America (USA)

Drug: zongertinib

Phase Ib - Dose expansion part: Cohort 9

EXPERIMENTAL

Cohort only in China

Drug: zongertinib

Interventions

zongertinib

Also known as: BI 1810631, Hernexeos®
Phase Ia - Dose escalation partPhase Ib - Dose expansion part: Cohort 1Phase Ib - Dose expansion part: Cohort 2Phase Ib - Dose expansion part: Cohort 3Phase Ib - Dose expansion part: Cohort 4Phase Ib - Dose expansion part: Cohort 5Phase Ib - Dose expansion part: Cohort 6Phase Ib - Dose expansion part: Cohort 7Phase Ib - Dose expansion part: Cohort 8Phase Ib - Dose expansion part: Cohort 9

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed diagnosis of an advanced, unresectable and/or metastatic non-haematologic malignancy. Patient must show presence of at least one measurable lesion according to Response Evaluation Criteria In Solid Tumors (RECIST) 1.1.
  • Eastern Cooperative Oncology Group (ECOG) score of 0, 1 or 2 (ECOG=2 only for Cohorts 6, 7 and 9) .
  • Availability and patient willingness to provide a sample of tumour for confirmation of the patient´s Human epidermal growth factor receptor 2 (HER2) status. This sample can be archival material obtained at any time prior to study enrollment.
  • Patient willing and able to comply with the protocol requirements for tumour biopsies (biopsies from brain metastases are not allowed).
  • Adequate organ function defined as all of the following:
  • Absolute neutrophil count (ANC) ≥ 1.5 x 10\^9/L (≥ 1.5 x 10\^3/μL) (≥ 1500/mm\^3); haemoglobin ≥ 9.0 g/dL (≥ 90 g/L) (≥ 5.6 mmol/L); platelets ≥ 100 x 10\^9/L (100 x 10\^3/μL) (100 x 10\^3/mm3) without the use of hematopoietic growth factors within 4 weeks of start of trial medication.
  • Total bilirubin ≤ 1.5 times the upper limit of normal (ULN), except for patients with Gilbert's syndrome: total bilirubin ≤ 3 x ULN or direct bilirubin ≤ 1.5 x ULN.
  • Estimated Glomerular Filtration Rate (eGFR) ≥ 50 mL/min - calculated using Chronic Kidney Disease Epidemiology (CKD-EPI) formula (≥ 30 mL/min/1.73m² for cohorts 6, 8, and 9).
  • Aspartate transaminase (AST) and alanine transaminase (ALT) ≤ 3 x ULN if no demonstrable liver metastases, or otherwise ≤ 5 x ULN if transaminase elevation is attributable to liver metastases.
  • Alkaline Phosphatase \< 5 x ULN.
  • Recovered from any previous therapy-related toxicity to ≤ Common Terminology Criteria for Adverse Events (CTCAE) Grade 1 at start of treatment (except for alopecia, stable sensory neuropathy and hypothyroidism (patients on thyroid replacement therapy) which must be ≤ CTCAE Grade 2)
  • Life expectancy of at least 12 weeks at the start of treatment in the opinion of the investigator.
  • At least 18 years of age at the time of consent or over the legal age of consent in countries where that is greater than 18 years.
  • Signed and dated written informed consent in accordance with International Council on Harmonisation-Good Clinical Practice (ICH-GCP) and local legislation prior to admission to the trial.
  • Male or female patients. Women of childbearing potential (WOCBP) and men who are able to father a child must be ready and able to use highly effective methods of birth control per International Council on Harmonisation (ICH) M3 (R2) that result in a low failure rate of less than 1% per year when used consistently and correctly.
  • +25 more criteria

You may not qualify if:

  • Major surgery (major according to the investigator's assessment) performed within 4 weeks prior to first trial treatment or planned within 6 months after screening
  • Previous or concomitant malignancies other than the one treated in this trial within the last 2 years, except:
  • effectively treated non-melanoma skin cancers
  • effectively treated carcinoma in situ of the cervix
  • effectively treated ductal carcinoma in situ
  • other effectively treated malignancy that is considered cured by local treatment.
  • Treatment with a systemic anti-cancer therapy or investigational drug within 21 days or 5 half-lives (whichever is shorter) of the first treatment with the study medication
  • Patients who must or wish to continue the intake of restricted medication or any drug considered likely to interfere with the safe conduct of the trial
  • Previous treatment with zongertinib.
  • Radiotherapy within 2 weeks prior to first study treatment, except palliative radiotherapy to regions other than the chest, which is allowed up to 1 week prior to first study treatment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (85)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

Precision NextGen Oncology

Beverly Hills, California, 90212, United States

Location

City of Hope-Duarte-56419

Duarte, California, 91010, United States

Location

City of Hope - Seacliff

Huntington Beach, California, 92648, United States

Location

City of Hope-Irvine-69674

Irvine, California, 92618, United States

Location

Valkyrie Clinical Trials

Los Angeles, California, 90067, United States

Location

University of California Irvine

Orange, California, 92868, United States

Location

University of California Davis

Sacramento, California, 95817, United States

Location

Georgetown University

Washington D.C., District of Columbia, 20007, United States

Location

Holy Cross Hospital-Fort Lauderdale-57892

Fort Lauderdale, Florida, 33308, United States

Location

Winship Cancer Institute

Atlanta, Georgia, 30322, United States

Location

Hawaii Cancer Care - Honolulu

Honolulu, Hawaii, 96813, United States

Location

Laura & Isaac Perlmutter Cancer Center at NYU Langone Health

New York, New York, 10016, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Sarah Cannon Research Institute-Nashville-48456

Nashville, Tennessee, 37203, United States

Location

Mary Crowley Cancer Research Center

Dallas, Texas, 75230, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

Virginia Cancer Specialists, PC

Fairfax, Virginia, 22031, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Macquarie University

Macquarie Park, New South Wales, 2109, Australia

Location

Ordensklinikum Linz GmbH

Linz, 4020, Austria

Location

Brussels - HOSP Jules Bordet

Anderlecht/Brussels-Capital, 1070, Belgium

Location

Beijing Cancer Hospital

Beijing, 100036, China

Location

Jilin Province Cancer Hospital

Changchun, 130012, China

Location

The First Hospital of Jilin University

Changchun, 130021, China

Location

Fujian Cancer Hospital

Fuzhou, 350014, China

Location

Guangdong Provincial People's Hospital

Guangzhou, 510080, China

Location

The First Affiliated Hospital, Zhejiang University

Hangzhou, 310003, China

Location

Zhejiang Cancer Hospital

Hangzhou, 310022, China

Location

Harbin Medical University Cancer Hospital

Harbin, 150081, China

Location

The Affiliated Cancer Hospital, Guangxi Medical University

Nanning, 530021, China

Location

Shanghai Chest Hospital

Shanghai, 200030, China

Location

Wuhan Union Hospital

Wuhan, 430022, China

Location

Tongji Hospital Affiliated Tongji Medical College Huazhong University of S & T

Wuhan, 430030, China

Location

First Affiliated Hospital of Xiamen University

Xiamen, 361003, China

Location

Henan Cancer Hospital

Zhengzhou, 450008, China

Location

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, 450052, China

Location

Hôpital Louis Pradel

Bron, 69677, France

Location

CTR Leon Berard

Lyon, 69373, France

Location

HOP Timone

Marseille, 13385, France

Location

INS Curie

Paris, 75005, France

Location

HOP Pontchaillou

Rennes, 35000, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Universitätsklinikum Augsburg

Augsburg, 86156, Germany

Location

Universitätsklinikum Köln (AöR)

Cologne, 50937, Germany

Location

Technische Universität Dresden

Dresden, 01307, Germany

Location

Justus-Liebig Universität Gießen

Giessen, 35392, Germany

Location

Pius-Hospital, Oldenburg

Oldenburg, 26121, Germany

Location

Prince of Wales Hospital-Hong Kong-20715

Hong Kong, 999077, Hong Kong

Location

Queen Mary Hospital

Hong Kong, Hong Kong

Location

Rambam Medical Center

Haifa, 3109601, Israel

Location

Meir Medical Center

Kfar Saba, 44281, Israel

Location

Sourasky Medical Center

Tel Aviv, 6423906, Israel

Location

The Chaim Sheba Medical Center Tel HaShomer

Tel Litwinsky, 52621, Israel

Location

Istituto Di Candiolo

Candiolo (TO), 10060, Italy

Location

Istituto Nazionale IRCCS Tumori Fondazione Pascale

Naples, 80131, Italy

Location

Azienda Ospedaliera Unversitaria di Parma

Parma, 43100, Italy

Location

National Cancer Center Hospital East

Chiba, Kashiwa, 277-8577, Japan

Location

Shikoku Cancer Center

Ehime, Matsuyama, 791-0280, Japan

Location

Hiroshima University Hospital

Hiroshima, Hiroshima, 734-8551, Japan

Location

Osaka International Cancer Institute

Osaka, Osaka, 541-8567, Japan

Location

Kindai University Hospital

Osaka, Sakai, 590-0197, Japan

Location

Hamamatsu University Hospital

Shizuoka, Hamamatsu, 431-3192, Japan

Location

National Cancer Center Hospital

Tokyo, Chuo-ku, 104-0045, Japan

Location

Nederlands Kanker Instituut

Amsterdam, 1066 CX, Netherlands

Location

Leids Universitair Medisch Centrum (LUMC)

Leiden, 2333 ZA, Netherlands

Location

Hospital CUF Porto

Porto, 4100-180, Portugal

Location

National University Hospital-Singapore-22806

Singapore, 119228, Singapore

Location

National Cancer Centre Singapore

Singapore, 169610, Singapore

Location

Chungbuk National University Hospital

Chungju, 28644, South Korea

Location

Seoul National University Bundang Hospital

Seongnam, 13620, South Korea

Location

Severance Hospital

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Hospital Universitari Vall D Hebron

Barcelona, 08035, Spain

Location

Hospital Duran i Reynals

L'Hospitalet de Llobregat, 08907, Spain

Location

Hospital General Universitario Gregorio Marañón

Madrid, 28007, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital Universitario Virgen de la Victoria

Málaga, 29010, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, 46010, Spain

Location

Karolinska Universitetssjukhuset Solna

Stockholm, 171 76, Sweden

Location

The Royal Marsden Hospital, Chelsea

London, SW3 6JJ, United Kingdom

Location

Hammersmith Hospital

London, W12 0HS, United Kingdom

Location

The Royal Marsden Hospital, Sutton

Sutton, SM2 5PT, United Kingdom

Location

Related Publications (3)

  • Heymach JV, Ruiter G, Ahn MJ, Girard N, Smit EF, Planchard D, Wu YL, Cho BC, Yamamoto N, Sabari JK, Zhao Y, Tu HY, Yoh K, Nadal E, Sadrolhefazi B, Rohrbacher M, von Wangenheim U, Eigenbrod-Giese S, Zugazagoitia J; Beamion LUNG-1 Investigators. Zongertinib in Previously Treated HER2-Mutant Non-Small-Cell Lung Cancer. N Engl J Med. 2025 Jun 19;392(23):2321-2333. doi: 10.1056/NEJMoa2503704. Epub 2025 Apr 28.

  • Heymach JV, Opdam F, Barve M, Tu HY, Wu YL, Berz D, Schroter L, Botilde Y, Sadrolhefazi B, Serra J, Yoh K, Yamamoto N. HER2-Selective Tyrosine Kinase Inhibitor, Zongertinib (BI 1810631), in Patients With Advanced/Metastatic Solid Tumors With HER2 Alterations: A Phase Ia Dose-Escalation Study. J Clin Oncol. 2025 Apr 10;43(11):1337-1347. doi: 10.1200/JCO-24-01727. Epub 2025 Mar 3.

  • Heymach J, Opdam F, Barve M, Gibson N, Sadrolhefazi B, Serra J, Yamamoto N. A Phase I, Open-Label, Dose Confirmation, Escalation, and Expansion Trial of BI 1810631 as Monotherapy in Patients With Advanced or Metastatic Solid Tumors With HER2 Aberrations. Clin Lung Cancer. 2023 Mar;24(2):e65-e68. doi: 10.1016/j.cllc.2022.10.008. Epub 2022 Nov 11.

Related Links

MeSH Terms

Conditions

Neoplasm MetastasisCarcinoma, Non-Small-Cell Lung

Condition Hierarchy (Ancestors)

Neoplastic ProcessesNeoplasmsPathologic ProcessesPathological Conditions, Signs and SymptomsCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteLung DiseasesRespiratory Tract Diseases

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 4, 2021

First Posted

May 14, 2021

Study Start

July 2, 2021

Primary Completion (Estimated)

December 30, 2026

Study Completion (Estimated)

August 30, 2028

Last Updated

March 13, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will not share

Clinical studies sponsored by Boehringer Ingelheim, phases I to IV, interventional and non-interventional, are in scope for sharing of the raw clinical study data and clinical study documents. Exceptions might apply, e.g. studies in products where Boehringer Ingelheim is not the license holder; studies regarding pharmaceutical formulations and associated analytical methods, and studies pertinent to pharmacokinetics using human biomaterials; studies conducted in a single center or targeting rare diseases (in case of low number of patients and therefore limitations with anonymization). For more details refer to: https://www.clinicalstudies.boehringer-ingelheim.com/msw/datasharing

Locations