NCT04769479

Brief Summary

This is a single centre, open-label, 5-period study in healthy male and non-pregnant and non-lactating healthy female subjects.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
14

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Mar 2021

Shorter than P25 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 19, 2021

Completed
5 days until next milestone

First Posted

Study publicly available on registry

February 24, 2021

Completed
1 month until next milestone

Study Start

First participant enrolled

March 28, 2021

Completed
4 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 4, 2021

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

September 3, 2021

Completed
Last Updated

September 19, 2024

Status Verified

March 1, 2022

Enrollment Period

4 months

First QC Date

February 19, 2021

Last Update Submit

September 10, 2024

Conditions

Outcome Measures

Primary Outcomes (3)

  • Pharmacokinetic Assessments: Cmax

    Maximum Concentration (Cmax)

    72 hours

  • Pharmacokinetic Assessments: AUC

    Area under the plasma concentration-time curve (AUC)

    72 hours

  • Pharmacokinetic Assessments: Tmax

    Time to maximum concentration (Tmax)

    72 hours

Study Arms (1)

acoramidis

EXPERIMENTAL
Drug: acoramidis

Interventions

acoramidis

Also known as: AG10
acoramidis

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Healthy males or non-pregnant, non-lactating healthy females
  • Body mass index (BMI) of 18.0 to 32.0kg/m² and a body weight\>50kg as measured at screening
  • Must be willing and able to communicate and participate in the whole study
  • Must provide written informed consent
  • Must agree to adhere to the contraception requirements

You may not qualify if:

  • Subjects who have received any IMP formulation in a clinical research study within the 90 days prior to Period 1, Day 1
  • History of any drug or alcohol abuse in the past 2 years
  • Subjects with pregnant or lactating partners
  • Clinically significant abnormal clinical chemistry, haematology or urinalysis as judged by the investigator. Subjects with Gilbert's Syndrome are allowed.
  • History of clinically significant cardiovascular, renal, hepatic, dermatological, chronic respiratory or gastrointestinal disease, neurological or psychiatric disorder, as judged by the investigator
  • Presence or history of clinically significant allergy requiring treatment, as judged by the investigator. Hay fever is allowed unless it is active
  • Subjects who are taking, or have taken, any prescribed or over-the-counter drug or herbal remedies (other than up to 4g of paracetamol per day or HRT/hormonal contraception) in the 14 days before first IMP administration.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Quotient Sciences

Ruddington, Nottingham, NG11 6JS, United Kingdom

Location

MeSH Terms

Conditions

Amyloidosis

Interventions

attruby

Condition Hierarchy (Ancestors)

Proteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic Diseases

Study Officials

  • Philip Evans, MBChB, MRCS

    Quotient Sciences

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 19, 2021

First Posted

February 24, 2021

Study Start

March 28, 2021

Primary Completion

August 4, 2021

Study Completion

September 3, 2021

Last Updated

September 19, 2024

Record last verified: 2022-03

Data Sharing

IPD Sharing
Will not share

Locations