NCT04565665

Brief Summary

This is a phase I trial followed by a phase II randomized trial. The purpose of phase I study is the feasibility of treating patients with acute respiratory distress syndrome (ARDS) related to COVID-19 infection (COVID-19) with cord blood-derived mesenchymal stem cells (MSC). The purpose of the phase II trial is to compare the effect of MSC with standard of care in these patients. MSCs are a type of stem cells that can be taken from umbilical cord blood and grown into many different cell types that can be used to treat cancer and other diseases. The MSCs being used for infusion in this trial are collected from healthy, unrelated donors and are stored and grown in a laboratory. Giving MSC infusions may help control the symptoms of COVID-19 related ARDS.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P75+ for phase_1

Timeline
6mo left

Started Jul 2020

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress92%
Jul 2020Oct 2026

Study Start

First participant enrolled

July 29, 2020

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

September 22, 2020

Completed
3 days until next milestone

First Posted

Study publicly available on registry

September 25, 2020

Completed
6.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 30, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 30, 2026

Last Updated

April 14, 2026

Status Verified

April 1, 2026

Enrollment Period

6.3 years

First QC Date

September 22, 2020

Last Update Submit

April 9, 2026

Conditions

Outcome Measures

Primary Outcomes (4)

  • Incidence of composite serious adverse events (Phase I)

    Serious adverse events with be comprised of grade 3 or 4 graft versus host disease or death and will be estimated and reported overall and by group, along with 95% confidence intervals.

    Within 30 days of the first mesenchymal stem cell (MSC) infusion

  • Patients alive without grade 3, 4 infusional toxicity (Phase II)

    At day 30 post MSC infusion

  • Patients alive with grade 3 or 4 infusional toxicity (Phase II)

    At day 30 post MSC infusion

  • Patients not alive (Phase II)

    At day 30 post MSC infusion

Secondary Outcomes (12)

  • Proportion of successfully extubated patients who present intubated on ventilator support (Phase I)

    Up to day 30 post MSC infusion

  • Rate of successful progression to intubation in patients who require supplemental oxygen but who are otherwise able to breathe without assistance (Phase I)

    Up to day 30 post MSC infusion

  • Overall survival rate (Phase I)

    At day 30 post MSC infusion

  • Survival rate in patients who present intubated on ventilator support (Phase I)

    At day 30 post MSC infusion

  • Survival rate in patients who require supplemental oxygen but who are otherwise able to breathe without assistance (Phase I)

    At day 30 post MSC infusion

  • +7 more secondary outcomes

Study Arms (3)

Phase II Arm I (mesenchymal stem cells)

EXPERIMENTAL

Patients receive MSCs as in the Pilot study.

Biological: Mesenchymal Stem Cell

Phase II Arm II (standard of care)

ACTIVE COMPARATOR

Patients receive standard of care.

Other: Best Practice

Pilot study (mesenchymal stem cells)

EXPERIMENTAL

Patients receive MSCs IV over 1-2 hours on day 1. Patients may receive a second infusion of MSCs within 7 days after the first infusion per physician discretion.

Biological: Mesenchymal Stem Cell

Interventions

Receive standard of care

Also known as: standard of care, standard therapy
Phase II Arm II (standard of care)

Given IV

Also known as: Mesenchymal Progenitor Cell, MPC
Phase II Arm I (mesenchymal stem cells)Pilot study (mesenchymal stem cells)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age greater than or equal 18 years.
  • Participants with chest x-ray findings concerning for pneumonia from any cause, with clinical signs suggestive of at least moderate illness such as respiratory rate \>20 breaths per minute or with oxygen saturation less than 93% on room air\*\*
  • Participants with COVID-19 associated pneumonia must meet baseline categorization of Moderate, Severe or Critical COVID-19 per FDA Guidance for Industry COVID-19: Developing Drugs and Biologics Products for Treatment or Prevention, February 2021.
  • Negative pregnancy test in a woman with childbearing potential defined as not post-menopausal for 12 months or no previous surgical sterilization.
  • Participant or legally authorized representative consent. Participants with diminished mental capacity may be allowed on to enroll on the study.
  • Because of the nature of COVID-19, participants enrolled on this study with COVID-19 associated pneumonia may have been previously enrolled in other IND trials for their cancer diagnosis or for COVID-19. These enrollments will not exclude them from enrollment to this study.

You may not qualify if:

  • Moribund participants not expected to survive up to 48 hours
  • Participants with severe chronic liver disease (Childs-Pugh score \> 10)
  • Pregnant and/or lactating women
  • Participants on extracorporeal membrane oxygenation

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

M D Anderson Cancer Center

Houston, Texas, 77030, United States

RECRUITING

Related Links

MeSH Terms

Conditions

COVID-19Hematologic Neoplasms

Interventions

Practice Guidelines as TopicStandard of Care

Condition Hierarchy (Ancestors)

Pneumonia, ViralPneumoniaRespiratory Tract InfectionsInfectionsVirus DiseasesCoronavirus InfectionsCoronaviridae InfectionsNidovirales InfectionsRNA Virus InfectionsLung DiseasesRespiratory Tract DiseasesNeoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Guidelines as TopicQuality Assurance, Health CareQuality of Health CareHealth Services AdministrationHealth Care Quality, Access, and EvaluationQuality Indicators, Health Care

Study Officials

  • Amanda Olson

    M.D. Anderson Cancer Center

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 22, 2020

First Posted

September 25, 2020

Study Start

July 29, 2020

Primary Completion (Estimated)

October 30, 2026

Study Completion (Estimated)

October 30, 2026

Last Updated

April 14, 2026

Record last verified: 2026-04

Locations