NCT04501120

Brief Summary

The purpose of this study is to assess the safety, pharmacokinetic profile of Lisaftoclax (APG-2575) single agent and in combination with HHT/AZA in patients with relapsed/refractory AML and related myeloid malignancies.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
682

participants targeted

Target at P75+ for phase_1

Timeline
41mo left

Started Sep 2020

Longer than P75 for phase_1

Geographic Reach
1 country

12 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress63%
Sep 2020Sep 2029

First Submitted

Initial submission to the registry

August 3, 2020

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 6, 2020

Completed
2 months until next milestone

Study Start

First participant enrolled

September 28, 2020

Completed
7.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2028

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2029

Last Updated

April 29, 2026

Status Verified

April 1, 2026

Enrollment Period

7.9 years

First QC Date

August 3, 2020

Last Update Submit

April 27, 2026

Conditions

Keywords

Acute Myeloid Leukaemia (AML)Bcl-2 InhibitorMyeloid MalignancyLisaftoclax (APG-2575)

Outcome Measures

Primary Outcomes (2)

  • Dose Limiting Toxicities (DLT)

    DLT will be graded according to NCI CTCAE Version 5.0. DLT will be defined as clinically significant drug-related adverse events during cycle one.

    28 days

  • Maximum Tolerated Dose (MTD)/Recommended Phase 2 Dose(RP2D)

    MTD/RP2D will be determined based on DLTs observed during cycle one.

    28 days

Secondary Outcomes (6)

  • Maximum plasma concentration (Cmax)

    28 days

  • Area under the plasma concentration versus time curve (AUC)

    28 days

  • Objective Response Rate (ORR)

    Up to 6 cycles (each cycle is 28 days).

  • progression free survival (PFS)

    Up to 2 years.

  • duration of response (DOR)

    Up to 2 years.

  • +1 more secondary outcomes

Study Arms (8)

Lisaftoclax (APG-2575) single agent

EXPERIMENTAL

Lisaftoclax (APG-2575) orally once daily starting from 200mg and will be increased in subsequent cohorts to 400mg, 600mg, 800mg, to determine the MTD/RP2D.

Drug: Lisaftoclax (APG-2575)

Lisaftoclax (APG-2575)+reduced-dose HHT

EXPERIMENTAL

Lisaftoclax (APG-2575) MTD/RP2D-1 and MTD/RP2D combines with reduced-dose HHT in R/R AML, MPAL, BPDCN, CMML.

Drug: Lisaftoclax (APG-2575)Drug: Reduced-dose HHT

Lisaftoclax (APG-2575)+ standard-dose HHT

EXPERIMENTAL

Lisaftoclax (APG-2575) MTD/RP2D-1 and MTD/RP2D combines with standard-dose HHT in R/R AML, MPAL, BPDCN, CMML.

Drug: Lisaftoclax (APG-2575)Drug: standard-dose HHT

Lisaftoclax (APG-2575)+ AZA

EXPERIMENTAL

Lisaftoclax (APG-2575) MTD/RP2D-1 and MTD/RP2D combines with AZA in R/R AML, MPAL, BPDCN, CMML.

Drug: Lisaftoclax (APG-2575)Drug: Azacitidine

Lisaftoclax (APG-2575)+ AZA(HR-MDS.)

EXPERIMENTAL

Lisaftoclax (APG-2575) MTD/RP2D-1 and MTD/RP2D combines with AZA in HR-MDS.

Drug: AzacitidineDrug: Lisaftoclax (APG-2575)

Lisaftoclax (APG-2575)+ AZA(Naïve AML.)

EXPERIMENTAL

Lisaftoclax (APG-2575) MTD/RP2D-1 and MTD/RP2D combines with AZA in treatment naïve AML.

Drug: Lisaftoclax (APG-2575)Drug: Azacitidine

Lisaftoclax (APG-2575)+AZA+Olverembatinib

EXPERIMENTAL

Lisaftoclax (APG-2575) combines with AZA and Olverembatinib in R/R AML.

Drug: AzacitidineDrug: Lisaftoclax (APG-2575)Drug: olverembatinib

Lisaftoclax (APG-2575)+HHT+Olverembatinib

EXPERIMENTAL

Lisaftoclax (APG-2575) combines with HHT and Olverembatinib in R/R AML.

Drug: standard-dose HHTDrug: Lisaftoclax (APG-2575)Drug: olverembatinib

Interventions

1mg IV QD on Days 1-14 (28-day cycle).

Lisaftoclax (APG-2575)+reduced-dose HHT

2mg/m\^2 IV QD on Days 1-7 (28-day cycle).

Lisaftoclax (APG-2575)+ standard-dose HHTLisaftoclax (APG-2575)+HHT+Olverembatinib

75 mg/m\^2 SC or Iv gtt QD on Days 1- 7 (28-day cycle).

Lisaftoclax (APG-2575)+ AZALisaftoclax (APG-2575)+ AZA(HR-MDS.)Lisaftoclax (APG-2575)+ AZA(Naïve AML.)Lisaftoclax (APG-2575)+AZA+Olverembatinib

Lisaftoclax (APG-2575) orally once daily, every 28 days as a cycle.

Lisaftoclax (APG-2575) single agentLisaftoclax (APG-2575)+ AZALisaftoclax (APG-2575)+ AZA(Naïve AML.)Lisaftoclax (APG-2575)+ standard-dose HHTLisaftoclax (APG-2575)+reduced-dose HHT

orally, with meals, QOD, every 28 days as a cycle.

Lisaftoclax (APG-2575)+AZA+OlverembatinibLisaftoclax (APG-2575)+HHT+Olverembatinib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • In accordance with the World Health Organization (WHO) 2016 diagnostic criteria for relapsed or refractory acute myeloid leukemia (AML), Mixed phenotype acute leukemia(MPAL), Chronic myelomonocytic leukemia (CMML), Higher-risk myelodysplastic syndrome (HR-MDS) , Blastic plasmacytoid dendritic cell neoplasm (BPDCN) and naïve AML ineligible for treatment with a standard chemotherapy due to age or comorbidities.
  • Eastern Cooperative Oncology Group (ECOG) Performance Status (PS): 0 -2 (0 to 3 for participants \>= 60 to 74 years of age who are evaluated as ineligible for treatment with standard chemotherapy).
  • Subjects can accept oral administration of Lisaftoclax (APG-2575).
  • Life expectancy ≥ 3 months.
  • Adequate renal and liver function.
  • Males, female patients of childbearing potential (postmenopausal women who must have been menopausal for at least 12 months to be considered infertile) and their partners voluntarily take contraception which the investigator considers effective during treatment and at least three months after the last dose of study drug.
  • Ability to understand and willingness to sign a written informed consent form (the consent form must be signed by the patient prior to any study-specific procedures).
  • Willingness and ability to comply with study procedures and follow-up examination.

You may not qualify if:

  • Patients diagnosed with acute promyelocytic leukemia or t(9;22)(q34.1;q11.2); BCR-ABL1 positive AML patients.
  • The persistent toxicities caused by previous chemotherapy or radiotherapy has not been restored to lower than grade 2 by CTCAE 5.0 (except for alopecia).
  • Known leukemia infiltration of the central nervous system.
  • Symptomatic active fungal, bacterial and/or viral infections.
  • Prior history of allogeneic hematopoietic stem cell transplantation or adoptive cell immunotherapy, autologous hematopoietic stem cell transplantation within 12 months.
  • Within 14 days before the first dose of study drug, received chemotherapy (hydroxyurea is permitted more than 24 hours before the first dose of study drug), radiotherapy, surgery, immunotherapy, targeted therapy, biological therapy or any investigational treatment.
  • Within 7 days before the first dose of study drug, received a strong and/or moderate CYP3A inducer and/or Inhibitor.
  • At the discretion of the investigator, gastrointestinal diseases that affect the absorption of Lisaftoclax (APG-2575).
  • Any other condition or circumstance, at the discretion of the investigator, that patients would be unsuitable for participation in the study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

Peking University People's Hospital

Beijing, Beijing Municipality, 100044, China

RECRUITING

Chongqing University Cancer Hospital

Chongqing, Chongqing Municipality, China

NOT YET RECRUITING

Sun Yat-sen University Cancer Center

Guangzhou, Guandong, China

RECRUITING

Guangdong Provincial People's Hospital

Guangzhou, Guangdong, 510080, China

RECRUITING

Henan Tumor Hospital

Zhengzhou, Henan, China

RECRUITING

Union Hospital medical college Huazhong University of Science and Technology

Wuhan, Hubei, 430022, China

RECRUITING

Zhongnan Hospital of Hunan university

Wuhan, Hubei, 430071, China

RECRUITING

Xiangya Hospital Central South University

Changsha, Hunan, China

RECRUITING

The First affiliated hospital of Soochow University

Suzhou, Jiangsu, China

RECRUITING

Shanghai The Sixth People' s Hospital

Shanghai, Shanghai Municipality, China

NOT YET RECRUITING

West China Hospital of Sichuan University

Chengdu, Sichuan, 610044, China

RECRUITING

the First Affiliated Hospital, College of Medicine, Zhejiang University

Hangzhou, Zhejiang, 310003, China

RECRUITING

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

LisaftoclaxAzacitidineolverembatinib

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Aza CompoundsOrganic ChemicalsCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsNucleosidesNucleic Acids, Nucleotides, and NucleosidesRibonucleosides

Study Officials

  • Yifan Zhai, M.D., Ph.D.

    Suzhou Yasheng Pharmaceutical Co., Ltd.

    STUDY DIRECTOR
  • Jie Jin, M.D.

    the First Affiliated Hospital, College of Medicine

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 3, 2020

First Posted

August 6, 2020

Study Start

September 28, 2020

Primary Completion (Estimated)

September 1, 2028

Study Completion (Estimated)

September 1, 2029

Last Updated

April 29, 2026

Record last verified: 2026-04

Locations