NCT04428489

Brief Summary

The proposed minimal diagnostic criteria for myelodysplastic syndromes (MDS) and potential pre-MDS conditions has been released by an international consensus group. Based on the criteria, patients with persistent cytopenia could be diagnosed with MDS, CCUS and ICUS. However, the process and outcome of pre-MDS conditions (CCUS, ICUS) is still to be characterized in Chinese population. We design this prospective observational study to explore the disease process and outcome in ICUS and CCUS patients.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
300

participants targeted

Target at P75+ for all trials

Timeline
8mo left

Started Jan 2011

Longer than P75 for all trials

Geographic Reach
1 country

1 active site

Status
enrolling by invitation

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress96%
Jan 2011Dec 2026

Study Start

First participant enrolled

January 1, 2011

Completed
9.4 years until next milestone

First Submitted

Initial submission to the registry

June 9, 2020

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 11, 2020

Completed
6.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2026

Last Updated

December 29, 2025

Status Verified

December 1, 2025

Enrollment Period

16 years

First QC Date

June 9, 2020

Last Update Submit

December 21, 2025

Conditions

Keywords

Idiopathic cytopenia of undetermined significance (ICUS)Clonal cytopenia of unknown significance (CCUS)

Outcome Measures

Primary Outcomes (1)

  • Culumative transformation rate

    Transformation is defined as progression from ICUS to CCUS, ICUS to MDS or CCUS to MDS. All patients are followed-up since entry into this trial and transformation events are recorded. Cumulative transformation rate is defined for all patients and estimated by competing risk methods.

    5 years

Secondary Outcomes (1)

  • Event-free survival

    5 years

Study Arms (2)

Idiopathic cytopenia of undetermined significance (ICUS)

Other: Observation and necessary supportive care

Clonal cytopenia of unknown significance (CCUS)

Other: Observation and necessary supportive care

Interventions

For patients with ICUS and CCUS, necessary supportive care could be given. No addtitional treatment is administrated.

Clonal cytopenia of unknown significance (CCUS)Idiopathic cytopenia of undetermined significance (ICUS)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients diagnosed with ICUS and CCUS based on the proposed minimal diagnostic criteria for myelodysplastic syndromes (MDS) and potential pre-MDS conditions

You may qualify if:

  • Patients with cytopenia of any degree in one or more lineages: erythrocytes, neutrophils, or platelets. And the cytopenia has to be persistent (≥ 4 months) and lacking minimal diagnostic criteria of MDS.

You may not qualify if:

  • Patients with cytopenia which could be explained by any other hematologic or non-hematologic disease.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

The First Affliated Hospital of Soochow University

Suzhou, Jiangsu, 215006, China

Location

MeSH Terms

Conditions

Myelodysplastic Syndromes

Interventions

Observation

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

MethodsInvestigative Techniques

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor

Study Record Dates

First Submitted

June 9, 2020

First Posted

June 11, 2020

Study Start

January 1, 2011

Primary Completion (Estimated)

December 31, 2026

Study Completion (Estimated)

December 31, 2026

Last Updated

December 29, 2025

Record last verified: 2025-12

Locations