NCT04410523

Brief Summary

The purpose of this study is to determine the efficacy and safety of multiple CSJ117 doses (0.5; 1; 2; 4 and 8 mg) inhaled once daily compared with placebo, when added to standard-of-care (SoC) asthma therapy in adult patients with uncontrolled asthma with respect to change from baseline in FEV1 at the end of 12 weeks of treatment.

Trial Health

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Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
335

participants targeted

Target at P75+ for phase_2 asthma

Timeline
Completed

Started Sep 2020

Typical duration for phase_2 asthma

Geographic Reach
15 countries

113 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 6, 2020

Completed
26 days until next milestone

First Posted

Study publicly available on registry

June 1, 2020

Completed
3 months until next milestone

Study Start

First participant enrolled

September 9, 2020

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 12, 2022

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 6, 2022

Completed
11 months until next milestone

Results Posted

Study results publicly available

August 7, 2023

Completed
Last Updated

June 20, 2024

Status Verified

June 1, 2024

Enrollment Period

1.8 years

First QC Date

May 6, 2020

Results QC Date

July 18, 2023

Last Update Submit

June 17, 2024

Conditions

Keywords

CSJ117uncontrolled asthma

Outcome Measures

Primary Outcomes (1)

  • Average Change From Baseline in Pre-dose FEV1 at Week 8 and Week 12

    FEV1 (forced expiratory volume in one second) is the amount of air which can be forcibly exhaled from the lungs in the first second of a forced exhalation, measured through spirometry testing. Pre-dose FEV1 is defined as average of the two FEV1 measurements taken at approximately 45 minutes and 15 minutes prior to dosing. The baseline pre-dose FEV1 value is defined as the average of the values taken approximately 2 hours 45 minutes and 2 hours 15 minutes prior to the first dose of double-blind treatment at Day 1. The least-squares means for change from baseline in pre-dose FEV1 averaged between Week 8 and Week 12 visits for each individual dose group were obtained from a linear mixed effects model for repeated measures (MMRM). A positive average change from baseline in pre-dose FEV1 is considered a favorable outcome.

    Baseline, Weeks 8-12

Secondary Outcomes (11)

  • Average Change From Baseline in FeNO at Week 8 and Week 12

    Baseline, Weeks 8-12

  • Change From Baseline in Morning PEF at Week 12

    Baseline, Week 12

  • Change From Baseline in Evening PEF at Week 12

    Baseline, Week 12

  • Average Change From Baseline in ACQ-5 Score at Week 8 and Week 12

    Baseline, Weeks 8-12

  • Average Change From Baseline in AQLQ+12 Score at Week 8 and Week 12

    Baseline, Weeks 8-12

  • +6 more secondary outcomes

Study Arms (6)

CSJ117 0.5mg

EXPERIMENTAL

CSJ117 0.5 mg inhaled once daily

Drug: CSJ117Drug: Placebo

CSJ117 1mg

EXPERIMENTAL

CSJ117 1 mg inhaled once daily

Drug: CSJ117Drug: Placebo

CSJ117 2mg

EXPERIMENTAL

CSJ117 2 mg inhaled once daily

Drug: CSJ117Drug: Placebo

CSJ117 4mg

EXPERIMENTAL

CSJ117 4 mg inhaled once daily

Drug: CSJ117Drug: Placebo

CSJ117 8mg

EXPERIMENTAL

CSJ117 8 mg inhaled once daily

Drug: CSJ117Drug: Placebo

Placebo

PLACEBO COMPARATOR

Placebo inhaled once daily

Drug: Placebo

Interventions

CSJ117DRUG

CSJ117 inhaled once daily (in the morning) for 12 weeks. Delivered via Concept1 device. CSJ117 = inhaled monoclonal antibody fragment

CSJ117 0.5mgCSJ117 1mgCSJ117 2mgCSJ117 4mgCSJ117 8mg

Run-in period (all arms): Placebo inhaled once daily (in the morning) for 4 weeks. Placebo dosing extended to 8 weeks in case of asthma exacerbation or respiratory tract infection during this period. Treatment period (Placebo arm only): Placebo inhaled once daily (in the morning) for 12 weeks. Delivered via Concept1 device.

CSJ117 0.5mgCSJ117 1mgCSJ117 2mgCSJ117 4mgCSJ117 8mgPlacebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosed asthma
  • Male and female patients aged ≥18 and ≤75 years
  • Patients who have been treated with medium or high dose ICS plus LABA with up to 2 additional controllers
  • Morning pre-BD FEV1 value of ≥ 40% and ≤ 85% of the predicted normal
  • A positive reversibility test
  • ACQ-5 score of ≥ 1.5 at screening and end of run-in visits.

You may not qualify if:

  • Patients who have a cigarette smoking history of greater than 10 pack years or current smokers
  • Pregnant or nursing (lactating) women
  • Women of child-bearing potential, defined as all women physiologically capable of becoming pregnant, unless they are using specified methods of contraception during dosing of study drug and until 12 weeks after last study drug treatment
  • Patients with a history of immunodeficiency disease or hepatitis B, untreated and not cured hepatitis C or HIV.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (113)

Novartis Investigative Site

Bakersfield, California, 93301, United States

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Novartis Investigative Site

Huntington Beach, California, 92647, United States

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Novartis Investigative Site

Los Angeles, California, 90017, United States

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Novartis Investigative Site

Los Angeles, California, 90025, United States

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Novartis Investigative Site

Los Angeles, California, 90048, United States

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Novartis Investigative Site

Mission Viejo, California, 92691, United States

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Novartis Investigative Site

San Jose, California, 95117, United States

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Novartis Investigative Site

Denver, Colorado, 80206, United States

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Novartis Investigative Site

Marietta, Georgia, 30060, United States

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Novartis Investigative Site

Bangor, Maine, 04401, United States

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Novartis Investigative Site

White Marsh, Maryland, 21162, United States

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Novartis Investigative Site

North Dartmouth, Massachusetts, 02747-3322, United States

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Novartis Investigative Site

Columbia, Missouri, 65203, United States

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Novartis Investigative Site

St Louis, Missouri, 63141, United States

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Novartis Investigative Site

Omaha, Nebraska, 68134, United States

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Novartis Investigative Site

Raleigh, North Carolina, 27607, United States

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Novartis Investigative Site

Oklahoma City, Oklahoma, 73120, United States

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Novartis Investigative Site

Pittsburgh, Pennsylvania, 15241, United States

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Novartis Investigative Site

Greenville, South Carolina, 29607, United States

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Novartis Investigative Site

Boerne, Texas, 78006, United States

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Novartis Investigative Site

McKinney, Texas, 75069, United States

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Novartis Investigative Site

CABA, Buenos Aires, C1056ABJ, Argentina

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Novartis Investigative Site

CABA, Buenos Aires, C1122AAK, Argentina

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Novartis Investigative Site

CABA, Buenos Aires, C1414AIF, Argentina

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Novartis Investigative Site

CABA, Buenos Aires, C1425BEN, Argentina

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Novartis Investigative Site

Mar del Plata, Buenos Aires, 7600, Argentina

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Novartis Investigative Site

Ranelagh, Partido de Berazate, Buenos Aires, 1884, Argentina

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Novartis Investigative Site

Concepción del Uruguay, Entre Ríos Province, 3260, Argentina

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Novartis Investigative Site

San Salvador, Entre Ríos Province, E3218CHH, Argentina

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Novartis Investigative Site

Santa Fe, Rosario, S2000DBS, Argentina

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Novartis Investigative Site

Rosario, Santa Fe Province, S2000DBS, Argentina

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Novartis Investigative Site

Rosario, Santa Fe Province, S2000JKR, Argentina

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Novartis Investigative Site

San Miguel de Tucumán, Tucumán Province, 4000, Argentina

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Novartis Investigative Site

San Miguel de Tucumán, Tucumán Province, T4000IFL, Argentina

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Novartis Investigative Site

Buenos Aires, 1900, Argentina

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Novartis Investigative Site

Buenos Aires, C1125ABE, Argentina

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Novartis Investigative Site

Buenos Aires, C1425FVH, Argentina

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Novartis Investigative Site

CABA, C1430CAE, Argentina

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Novartis Investigative Site

Mendoza, 5500, Argentina

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Novartis Investigative Site

Paraná, 3100, Argentina

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Novartis Investigative Site

Erpent, 5100, Belgium

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Novartis Investigative Site

Liège, 4000, Belgium

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Novartis Investigative Site

Rousse, 7002, Bulgaria

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Novartis Investigative Site

Stara Zagora, 6000, Bulgaria

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Novartis Investigative Site

Ajax, Ontario, L1S 2J5, Canada

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Novartis Investigative Site

Burlington, Ontario, L7N 3V2, Canada

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Novartis Investigative Site

Etobicoke, Ontario, M9V 4B4, Canada

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Novartis Investigative Site

Hamilton, Ontario, L8N 3Z5, Canada

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Novartis Investigative Site

Montreal, Quebec, H2V 2K1, Canada

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Novartis Investigative Site

Trois-Rivières, Quebec, G8T 7A1, Canada

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Novartis Investigative Site

Teplice, CZE, 415 01, Czechia

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Novartis Investigative Site

Jindřichův Hradec, 377 01, Czechia

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Novartis Investigative Site

Lovosice, 41002, Czechia

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Novartis Investigative Site

Varnsdorf, 40747, Czechia

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Novartis Investigative Site

Peine, Lower Saxony, 31224, Germany

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Novartis Investigative Site

Bamberg, 96049, Germany

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Novartis Investigative Site

Berlin, 10119, Germany

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Novartis Investigative Site

Berlin, 10717, Germany

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Novartis Investigative Site

Berlin, 10969, Germany

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Novartis Investigative Site

Berlin, 12159, Germany

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Novartis Investigative Site

Berlin, 12203, Germany

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Novartis Investigative Site

Darmstadt, 64283, Germany

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Novartis Investigative Site

Frankfurt, 60596, Germany

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Novartis Investigative Site

Hamburg, 20354, Germany

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Novartis Investigative Site

Hamburg, 22299, Germany

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Novartis Investigative Site

Hanover, 30173, Germany

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Novartis Investigative Site

Leipzig, D-04299, Germany

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Novartis Investigative Site

Leipzig, D-04347, Germany

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Novartis Investigative Site

Mainz, 55128, Germany

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Novartis Investigative Site

Potsdam, 14467, Germany

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Novartis Investigative Site

Witten, 58452, Germany

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Novartis Investigative Site

Guatemala City, GTM, 01010, Guatemala

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Novartis Investigative Site

Guatemala City, GTM, 01011, Guatemala

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Novartis Investigative Site

Guatemala City, 01010, Guatemala

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Novartis Investigative Site

Guatemala City, 01011, Guatemala

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Novartis Investigative Site

Balassagyarmat, 2660, Hungary

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Novartis Investigative Site

Gödöllő, 2100, Hungary

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Novartis Investigative Site

Komárom, 2900, Hungary

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Novartis Investigative Site

Pécs, 7635, Hungary

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Novartis Investigative Site

Szeged, 6722, Hungary

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Novartis Investigative Site

Yokohama, Kanagawa, 223-0059, Japan

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Novartis Investigative Site

Osaka, Osaka, 530 0001, Japan

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Novartis Investigative Site

Chuo Ku, Tokyo, 104-0031, Japan

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Novartis Investigative Site

Chuo-ku, Tokyo, 103-0003, Japan

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Novartis Investigative Site

Chuo-ku, Tokyo, 103-0028, Japan

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Novartis Investigative Site

Kodaira, Tokyo, 187-0024, Japan

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Novartis Investigative Site

Setagaya-Ku, Tokyo, 157-0072, Japan

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Novartis Investigative Site

Setagaya-ku, Tokyo, 158-0097, Japan

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Novartis Investigative Site

Toshima City, Tokyo, 170-0003, Japan

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Novartis Investigative Site

Toshima Ku, Tokyo, 170 0003, Japan

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Novartis Investigative Site

Osaka, 531-0073, Japan

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Novartis Investigative Site

Osaka, 551-0032, Japan

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Novartis Investigative Site

Riga, LV, 1011, Latvia

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Novartis Investigative Site

Riga, LV, 1038, Latvia

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Novartis Investigative Site

Daugavpils, LV-5401, Latvia

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Novartis Investigative Site

Daugavpils, LV-5417, Latvia

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Novartis Investigative Site

Riga, LV 1002, Latvia

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Novartis Investigative Site

Bulacan, 3020, Philippines

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Novartis Investigative Site

Iloilo City, 5000, Philippines

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Novartis Investigative Site

Manila, 1000, Philippines

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Novartis Investigative Site

Manila, 1003, Philippines

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Novartis Investigative Site

Bialystok, 15-044, Poland

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Novartis Investigative Site

Krakow, 30033, Poland

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Novartis Investigative Site

Krakow, 31-011, Poland

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Novartis Investigative Site

Lodz, 90-153, Poland

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Novartis Investigative Site

Poznan, 60-693, Poland

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Novartis Investigative Site

Poznan, 60-823, Poland

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Novartis Investigative Site

Izhevsk, 426061, Russia

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Novartis Investigative Site

Saint Petersburg, 194354, Russia

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Novartis Investigative Site

Saratov, 410012, Russia

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Novartis Investigative Site

Ulyanovsk, 432063, Russia

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Novartis Investigative Site

Levice, 93401, Slovakia

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Novartis Investigative Site

Prešov, 080 01, Slovakia

Location

Related Links

MeSH Terms

Conditions

Asthma

Condition Hierarchy (Ancestors)

Bronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung DiseasesRespiratory HypersensitivityHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 6, 2020

First Posted

June 1, 2020

Study Start

September 9, 2020

Primary Completion

July 12, 2022

Study Completion

September 6, 2022

Last Updated

June 20, 2024

Results First Posted

August 7, 2023

Record last verified: 2024-06

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com.

Locations