NCT04278144

Brief Summary

A first-in-human study using BDC-1001 as a single agent and in combination with nivolumab in HER2 expressing advanced malignancies

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
175

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Feb 2020

Longer than P75 for phase_1

Geographic Reach
4 countries

21 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 12, 2020

Completed
8 days until next milestone

First Posted

Study publicly available on registry

February 20, 2020

Completed
4 days until next milestone

Study Start

First participant enrolled

February 24, 2020

Completed
4.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 10, 2024

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 14, 2025

Completed
Last Updated

September 15, 2025

Status Verified

September 1, 2025

Enrollment Period

4.8 years

First QC Date

February 12, 2020

Last Update Submit

September 9, 2025

Conditions

Keywords

HER2ERBB2ImmunotherapyGastric CancerGastroesophageal junctionBreast CancerStomach CancerColorectal CancerGastrointestinal CancerNon-Small Cell Lung CancerBiliary Tract CancerHead and Neck CancerUrothelial CancerEndometrial CancerTLR7/8 agonist

Outcome Measures

Primary Outcomes (5)

  • Incidence of adverse events (AEs) and serious adverse events (SAEs)

    Escalation period

    2 years

  • Incidence and nature of dose-limiting toxicities (DLTs)

    Escalation period

    up to 21 days

  • Incidence of potential-immune related toxicities

    Escalation period

    2 years

  • Maximum tolerable dose (MTD) or a tolerated dose below MTD

    Escalation period

    2 years

  • Objective response rate (ORR) of confirmed complete or partial responses (CR, PR)

    Expansion period

    2 years

Secondary Outcomes (14)

  • PK (Cmax) of BDC-1001

    2 years

  • PK (Cmin) of BDC-1001

    2 years

  • PK (AUC0-t) of BDC-1001

    2 years

  • PK (AUC0-inf) of BDC-1001

    2 years

  • PK (CL) of BDC-1001

    2 years

  • +9 more secondary outcomes

Study Arms (2)

Single agent BDC-1001

EXPERIMENTAL

Escalating doses followed by expansion targeting HER2-expressing advanced malignancies

Drug: BDC-1001

Combination BDC-1001 plus nivolumab

EXPERIMENTAL

Escalating doses followed by expansion targeting HER2-expressing advanced malignancies

Drug: BDC-1001Drug: Nivolumab

Interventions

Immune stimulating antibody conjugate (ISAC), consisting of an anti-HER2 monoclonal antibody conjugated to a TLR 7/8 dual agonist

Combination BDC-1001 plus nivolumabSingle agent BDC-1001

Programmed death receptor-1 (PD 1)-blocking antibody

Also known as: Opdivo
Combination BDC-1001 plus nivolumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient must have an advanced solid tumor with documented HER2-protein expression or gene amplification for which approved therapies have been exhausted or are not clinically indicated.
  • Measurable disease as determined by RECIST v.1.1.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
  • Tumor tissue (archival or collected prior to the study start) available for exploratory biomarker evaluation.

You may not qualify if:

  • History of severe hypersensitivity to any ingredient of the study drug(s), including trastuzumab or other monoclonal antibody.
  • Previous treatment with a TLR 7, TLR 8 or a TLR 7/8 agonist.
  • Impaired cardiac function or history of clinically significant cardiac disease
  • Human Immunodeficiency virus (HIV) infection, active hepatitis B infection, or hepatitis C infection.
  • Active SARS-CoV-2 infection
  • Untreated central nervous system (CNS), epidural tumor or metastasis, or brain metastasis.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (21)

Stanford University

Palo Alto, California, 94304, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

The University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

START Midwest

Grand Rapids, Michigan, 49546, United States

Location

Memorial Sloan-Kettering Cancer Center

New York, New York, 10065, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Stephenson Cancer Center

Oklahoma City, Oklahoma, 73104, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

South Texas Accelerated Research Therapeutics

San Antonio, Texas, 78229, United States

Location

Virginia Cancer Specialists

Fairfax, Virginia, 22031, United States

Location

Institut Bergonie

Bordeaux, 33076, France

Location

Institut Paoli Calmettes

Marseille, 13009, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Samsung Medical Center

Seoul, Gangnam-gu, 06351, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, 13620, South Korea

Location

Asan Medical Center

Seoul, Songpa-gu, 05505, South Korea

Location

Hospital del Mar

Barcelona, Catalonia, 08003, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, Catalonia, 08035, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, Madrid, 28034, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, Madrid, 28041, Spain

Location

MeSH Terms

Conditions

Stomach NeoplasmsBreast NeoplasmsColorectal NeoplasmsGastrointestinal NeoplasmsCarcinoma, Non-Small-Cell LungBiliary Tract NeoplasmsHead and Neck NeoplasmsEndometrial Neoplasms

Interventions

Nivolumab

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesStomach DiseasesBreast DiseasesSkin DiseasesSkin and Connective Tissue DiseasesIntestinal NeoplasmsColonic DiseasesIntestinal DiseasesRectal DiseasesCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesBiliary Tract DiseasesUterine NeoplasmsGenital Neoplasms, FemaleUrogenital NeoplasmsUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Bolt Clinical Development

    Bolt Biotherapeutics

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Multiple ascending dose and dose-expansion of BDC-1001 administered as a single agent or in combination with nivolumab.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 12, 2020

First Posted

February 20, 2020

Study Start

February 24, 2020

Primary Completion

December 10, 2024

Study Completion

February 14, 2025

Last Updated

September 15, 2025

Record last verified: 2025-09

Data Sharing

IPD Sharing
Will not share

Locations