NCT04238624

Brief Summary

This study is being done to see if adding the study drug, cemiplimab, to the standard therapy with dabrafenib and trametinib is an effective treatment against anaplastic thyroid cancer.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
16

participants targeted

Target at below P25 for phase_2

Timeline
1mo left

Started Jan 2020

Longer than P75 for phase_2

Geographic Reach
1 country

7 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress98%
Jan 2020Jun 2026

Study Start

First participant enrolled

January 20, 2020

Completed
1 day until next milestone

First Submitted

Initial submission to the registry

January 21, 2020

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 23, 2020

Completed
6.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 20, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 20, 2026

Last Updated

July 2, 2025

Status Verified

July 1, 2025

Enrollment Period

6.4 years

First QC Date

January 21, 2020

Last Update Submit

July 1, 2025

Conditions

Keywords

Anaplastic Thyroid CancerThyroid CancerCemiplimabBRAF-Mutant Anaplastic Thyroid CancerBRAF Mutation-Related TumorsBRAF Gene Mutation19-464Memorial Sloan Kettering Cancer Center

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate per RECIST 1.1 Criteria

    Response and progression will be evaluated by using criteria proposed in RECIST 1.1.

    2 years

Study Arms (1)

BRAF-mutant ATC

EXPERIMENTAL

Participants will have a diagnosis of BRAF-V600E mutant Anaplastic Thyroid Cancer

Drug: DabrafenibDrug: Trametinib

Interventions

Participants will receive dabrafenib 150 mg orally twice a day

BRAF-mutant ATC

Participants will receive trametinib 2 mg orally once a day

BRAF-mutant ATC

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Pathological (histologically or cytologically) proven diagnosis of BRAF-V600E mutant ATC (a diagnosis that is noted to be consistent with ATC is acceptable)
  • Either Metastatic disease or locoregional disease that is considered not resectable for cure
  • Ideally a surgeon should determine that the disease is not resectable for cure, but this can also be done by any investigator
  • Patients must have measurable disease according to RECIST 1.1 criteria, defined as at least 1 lesion that can be accurately measured in at least 1 dimension (longest diameter to be recorded for nonnodal lesions and short axis for nodal lesions) as \>/= 20 mm with conventional techniques or as \>/= 10 mm with spiral CT scan, MRI, or calipers by clinical exam
  • Age \>/= 18 years
  • Eastern Cooperative Oncology Group (ECOG) performance status \</= (or Karnofsky performance score \>/= 60)
  • Able to swallow and retain orally administered medication
  • Patient must have normal organ and marrow function as defined below:
  • Absolute neutrophil count \>/=1.5 x 10\^9/L
  • Hemoglobin \>/=8 g/dL
  • Platelets \>/=100 x 10\^9/L
  • Serum bilirubin \</=1.5x institutional ULN (unless the patient has GIlbert's Disease, in which case total bilirubin \</=3x institutional ULN)
  • AST and ALT \</=2.5x institutional ULN (\</=5x institutional ULN if there is liver metastasis)
  • Serum creatinine \</=1.5mg/dL or calculated creatinined clearance (Cockcroft-Gault formula) \>/=50 mL/min or 24-h urine creatinine clearance \>/=50 mL/min
  • Left ventricular ejection fraction greater than or equal to instutional lower limit of normal (LLN) by echocardiogram or multigated acquisition (MUGA)
  • +3 more criteria

You may not qualify if:

  • Previous documentation or current evidence of treatment with dabrafenib and trametinib.
  • ° Exception: (1) Patients who started dabrafenib and tranetinib for ATC at an institution outside of MSK are eligible or (2) with the consent of the PI (Sherman). However, this exception is limited to 8 subjects.
  • Active brain metastases, unless an exception is granted by the Principal Investigator.
  • Current interstitial lung disease or pneumonitis
  • Prior history of idelalisib therapy. Exceptions allowed with the consent of the principal investigator (Dr. Sherman)
  • History of retinal vein occlusion (RVO) or central serous retinopathy (CSR):
  • ° History of RVO or CSR or predisposing factors to RVO or CSR (e.g. uncontrolled glaucoma or ocular hypertension)
  • History or current evidence of cardiovascular risk, including any of the following:
  • Left ventricular ejection fraction (LVEF) \<LLN
  • A QT interval corrected for heart rate using the Bazett's formula of QTcB\>/=480msec
  • Current evidence of clinically significant uncontrolled arrhythmias (exception: patients with controlled atrial fibrillation for \>30 days before enrollment are eligible)
  • History of acute coronary syndromes (including myocardial infarction and unstable angina), coronary angioplasty, or stenting within 6 months before treatment
  • Known hepatitis B virus (HBV) or hepatitis C virus (HCV) infection (with the exception of chronic or cleared HBV and HCV infection, which will be allowed)
  • HIV-positive patients on combination antiretroviral therapy are ineligible because of the potential for pharmacokinetic interactions with trametinib. In addition, these patients are at increased risk of lethal infections when treated with marrow-suppressive therapy
  • Uncontrolled intercurrent illness that would limit compliance with study requirement.
  • +7 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (7)

Memorial Sloan Kettering Basking Ridge (Limited Protocol Activities)

Basking Ridge, New Jersey, 07920, United States

Location

Memorial Sloan Kettering Monmouth (Limited Protocol Activities)

Middletown, New Jersey, 07748, United States

Location

Memorial Sloan Kettering Bergen (Limited Protocol Activities)

Montvale, New Jersey, 07645, United States

Location

Memorial Sloan Kettering Cancer Center @ Commack (Limited Protocol Activities)

Commack, New York, 11725, United States

Location

Memorial Sloan Kettering Westchester (Limited Protocol Activities)

Harrison, New York, 10604, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Memorial Sloan Kettering Nassau (Limited Protocol Activities)

Uniondale, New York, 11553, United States

Location

Related Links

MeSH Terms

Conditions

Thyroid Carcinoma, AnaplasticThyroid Neoplasms

Interventions

dabrafenibtrametinib

Condition Hierarchy (Ancestors)

CarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsEndocrine Gland NeoplasmsNeoplasms by SiteHead and Neck NeoplasmsEndocrine System DiseasesThyroid Diseases

Study Officials

  • Eric Sherman, MD

    Memorial Sloan Kettering Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 21, 2020

First Posted

January 23, 2020

Study Start

January 20, 2020

Primary Completion (Estimated)

June 20, 2026

Study Completion (Estimated)

June 20, 2026

Last Updated

July 2, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

Memorial Sloan Kettering Cancer Center supports the international committee of medical journal editors (ICMJE) and the ethical obligation of responsible sharing of data from clinical trials. The protocol summary, a statistical summary, and informed consent form will be made available on clinicaltrials.gov when required as a condition of Federal awards, other agreements supporting the research and/or as otherwise required. Requests for deidentified individual participant data can be made beginning 12 months after publication and for up to 36 months post publication. Deidentified individual participant data reported in the manuscript will be shared under the terms of a Data Use Agreement and may only be used for approved proposals. Requests may be made to: crdatashare@mskcc.org.

Locations