NCT04179864

Brief Summary

This is a global, multi-center, open-label, randomized phase 1b/2, active-controlled safety and efficacy study of oral administration of tazemetostat in combination with enzalutamide or abiraterone/prednisone (phase 1b) versus enzalutamide or abiraterone/prednisone alone in asymptomatic or mildly symptomatic subjects with progressive, metastatic castration-resistant prostate cancer (mCRPC) who have progressed on either abiraterone acetate, enzalutamide, or apalutamide or who are second generation anti-androgen treatment naive, and who have not received chemotherapy for mCRPC. This study is designed to determine the recommended phase 2 doses (RP2D) of tazemetostat in combination with either enzalutamide or abiraterone/prednisone, based on safety, tolerability, pharmacokinetic, pharmacodynamic, and efficacy profiles.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
102

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Nov 2019

Longer than P75 for phase_1

Geographic Reach
3 countries

24 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 14, 2019

Completed
4 days until next milestone

Study Start

First participant enrolled

November 18, 2019

Completed
9 days until next milestone

First Posted

Study publicly available on registry

November 27, 2019

Completed
4.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 4, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 4, 2024

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

March 10, 2026

Completed
Last Updated

March 10, 2026

Status Verified

February 1, 2026

Enrollment Period

5 years

First QC Date

November 14, 2019

Results QC Date

November 3, 2025

Last Update Submit

February 17, 2026

Conditions

Keywords

metastatic castration resistant prostate cancertazemetostatEPZ-6438E7438enzalutamideabirateronePrednisoneZytigaXtandi

Outcome Measures

Primary Outcomes (3)

  • Phase 1b: Number of Participants With Treatment-Emergent Non-Serious Adverse Events and Treatment-Emergent Serious Adverse Events (TESAEs)

    An AE was any untoward medical occurrence in a participant or clinical investigation participant administered a medicinal product and which did not necessarily had a causal relationship with this study drug. An SAE was an AE which occurred during any study phase and at any dose of study drug, that fulfilled 1 or more of following: resulted in death, was life-threatening, required hospitalization or prolongation of existing hospitalization, resulted in disability or incapacity, was a congenital abnormality or birth defect, or was an important medical event that might jeopardize the participant or might require medical intervention to prevent one of the outcomes listed above. TEAEs were AEs that started or worsened in severity on or after the date of the first dose of study drug through 30 after the end of study drug, or prior to initiation of another investigational agent or cytotoxic chemotherapy. The treatment-emergent non-serious AEs are presented with a frequency threshold of 5%.

    From first dose of study drug (Day 1) up to either 30 days after last dose of study drug or until the initiation of subsequent anticancer therapy or end of treatment visit. Assessed up to 149 weeks

  • Phase 1b: Recommended Phase 2 Dose (RP2D) of Tazemetostat

    RP2D was based on pharmacokinetics (PK) parameters, pharmacodynamics (PD) parameters as well as efficacy and the overall tolerability of each combination (tazemetost with enzalutamide or tazemetostat with abiraterone/prednisone).

    From Day 1 up to Day 28 of Cycle 1 (each cycle was 28 days)

  • Phase 2: Radiographic Progression-Free Survival (rPFS)

    rPFS was defined as the time from date of randomization (phase 2)/date of first dose of study drug (phase 1b) to the first objective evidence of radiographic progression using response evaluation criteria in solid tumors version 1.1 (RECIST 1.1) (soft tissue) and prostate cancer clinical trials working group 3 (PCWG3) (bone), or death from any cause, whichever occurred first. The radiographic PD for soft tissue lesion was determined based on computed tomography (CT) or magnetic resonance imaging (MRI) per RECIST 1.1 criteria and no confirmatory scan was required for soft tissue PD; for bone lesion was determined by 2 or more new bone lesions on bone scan per PCWG3 criteria (i.e., the appearance of 2 or more new bone lesions on bone scan) and the 2 scans (i.e., the confirmatory scan is required for bone disease progression) should be at least 6 weeks apart from each other.

    Assessments performed at screening (within 4 weeks of randomization) and every 8 weeks for first 6 months and then every 12 weeks thereafter, until death, PD, unacceptable toxicity, consent withdrawal, or termination of study. Approximately 200 weeks

Secondary Outcomes (20)

  • Phase 1b and 2: Percentage of Participants With Confirmed Prostate-Specific Antigen >=50% (PSA50) Response

    From Cycle 1 Day 1 (Baseline) up to either 30 days after last dose of study drug or until initiation of subsequent anticancer therapy or end of treatment visit. Assessed up to 149 weeks and 191 weeks for Phase 1b and Phase 2 respectively

  • Phase 1b and 2: Objective Response Rate (ORR)

    Tumor assessments performed at screening (within 4 weeks of randomization) and every 8 weeks for first 6 months and then every 12 weeks thereafter, until death, PD, unacceptable toxicity, consent withdrawal, or termination of study.Approximately 259 weeks

  • Phase 1b and 2: Best Overall Response (BOR)

    Tumor assessments performed at screening (within 4 weeks of randomization) and every 8 weeks for first 6 months and then every 12 weeks thereafter, until death, PD, unacceptable toxicity, consent withdrawal, or termination of study.Approximately 259 weeks

  • Phase 1b and 2: Disease Control Rate (DCR) at 6 Months

    Baseline and at 6 months (24 weeks)

  • Phase 1b and 2: Time to First Skeletal-Related Event (SRE) Per Prostate Cancer Clinical Trials Working Group 3 Criteria

    From first dose of study drug (Phase 1b) and randomization (Phase 2) (Day 1) up to approximately 259 weeks

  • +15 more secondary outcomes

Study Arms (4)

Phase 1b: Tazemetostat in Combination with Abiraterone/Prednisone

EXPERIMENTAL

In Phase 1b, abiraterone/prednisone will be administered in combination with tazemetostat in cycle 1 (28 days) to establish the recommended dose of tazemetostat in this combination; participants may continue treatment in additional 28-day cycles, as tolerated, until progression or unacceptable toxicity

Drug: TazemetostatDrug: Abiraterone/prednisone

Phase 1b: Tazemetostat in Combination with Enzalutamide

EXPERIMENTAL

In Phase 1b, enzalutamide will be administered in combination with tazemetostat in cycle 1 (28 days) to establish the recommended dose of tazemetostat in this combination; participants may continue treatment in additional 28-day cycles, as tolerated, until progression or unacceptable toxicity

Drug: TazemetostatDrug: Enzalutamide

Phase 2: Tazemetostat in Combination with Enzalutamide

EXPERIMENTAL

Participants will receive the newly established recommended phase 2 dose, orally twice daily when given in combination with enzalutamide) as determined in phase 1b part of the study) or enzalutamide alone. All participants will receive treatment in 28-day cycles.

Drug: TazemetostatDrug: Enzalutamide

Phase 2: Enzalutamide only

ACTIVE COMPARATOR

In Phase 2, Enzalutamide will be administered on cycle 1 day 1

Drug: Enzalutamide

Interventions

1,000 mg (two 500 mg tablets or four 250 mg tablets) orally once daily in combination with prednisone 5 mg administered orally twice daily.

Also known as: Zytiga
Phase 1b: Tazemetostat in Combination with Abiraterone/Prednisone

Tazemetostat (EPZ-6438) is a selective small-molecule inhibitor of the histone-lysine methyltransferase EZH2 gene

Also known as: EPZ-6438, E7438, IPN60200
Phase 1b: Tazemetostat in Combination with Abiraterone/PrednisonePhase 1b: Tazemetostat in Combination with EnzalutamidePhase 2: Tazemetostat in Combination with Enzalutamide

enzalutamide 160 mg (four 40 mg capsules) orally once daily

Also known as: Xtandi
Phase 1b: Tazemetostat in Combination with EnzalutamidePhase 2: Enzalutamide onlyPhase 2: Tazemetostat in Combination with Enzalutamide

Eligibility Criteria

Age18 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age at the time of consent ≥ 18 years.
  • Eastern Cooperative Oncology Group (ECOG) performance status 0 to 1 (Appendix
  • Life expectancy of \> 3 months.
  • Histologically or cytologically confirmed adenocarcinoma of the prostate. Small cell or neuroendocrine tumors of the prostate are also permitted.
  • Progressive disease in the setting of medical or surgical castration (ie, castration- resistant prostate cancer \[CRPC\]) by PCWG3 criteria for study entry.
  • Evidence of disease progression by rising PSA or
  • Soft tissue progression per RECIST 1.1 or
  • Evidence of disease progression by observation of 2 new bone lesions since the initiation of last systemic therapy.
  • Metastatic prostate cancer disease, documented by the following imaging
  • Bone lesions on bone scan (per PCWG3) or by soft tissue disease (per RECIST 1.1) by CT/MRI imaging Must have undergone bilateral orchiectomy or be willing to continue GnRH analogue or antagonist.
  • Prior treatment with a second-generation androgen inhibitor as follows:
  • For phase 1b, EITHER Previously untreated with or progressed on a second generation androgen inhibitor (abiraterone, enzalutamide, or apalutamide) OR progressed on a second generation inhibitor (inhibitor (abiraterone, enzalutamide, or apalutamide)
  • For phase 2 randomized component (i.e, enzalutamide- containing treatment arms) of the study, previously progressed on abiraterone.

You may not qualify if:

  • Known symptomatic brain metastases
  • Treatment with any of the following for prostate cancer within the indicated timeframe prior to day 1 of starting study treatment:
  • First generation: AR antagonists (eg, bicalutamide, nilutamide, flutamide) within 4 weeks.
  • alpha-reductase inhibitors, ketoconazole, estrogens (including diethylstilbesterol), or progesterones within 2 weeks.
  • Prior radionuclide therapy within 4 weeks.
  • Another interventional product or standard agent in a clinical study within 28 days prior to the first planned dose of Tazemetostat
  • For phase 2 subjects to be randomized to one of the enzalutamide treatment arms only, prior treatment with the second-generation androgen antagonist including enzalutamide, apalutamide, darolutamide, and proxalutamide, etc.
  • Severe concurrent disease, infection, or comorbidity that, in the judgment of the Investigator, would make the subject inappropriate for enrollment
  • Has had prior exposure to tazemetostat or other inhibitor(s) of enhancer of zeste homologue-2.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (24)

Genesis Healthcare Partners

San Diego, California, 92123, United States

Location

The Urology Center Of Colorado

Denver, Colorado, 80211, United States

Location

Hematology Oncology Associates of the Treasure Coast

Port Saint Lucie, Florida, 34952, United States

Location

XCancer - Northwest Oncology and Hematology

Rolling Meadows, Illinois, 60008, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02115, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Comprehensive Cancer Centers of Nevada - Central Valley

Las Vegas, Nevada, 89169, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Associated Medical Professionals of NY, PLLC - Urology

Syracuse, New York, 13210, United States

Location

Montefiore Einstein Center for Cancer Care

The Bronx, New York, 10461, United States

Location

University of Pittsburgh Medical Center - Hillman Cancer Center

Pittsburgh, Pennsylvania, 15232, United States

Location

SCRI - Tennessee Oncology Chattanooga

Chattanooga, Tennessee, 37404, United States

Location

Urology Associates P.C.

Hendersonville, Tennessee, 37075, United States

Location

XCancer - Tennesee Cancer Specialists

Knoxville, Tennessee, 37909, United States

Location

SCRI - Tennessee Oncology Nashville

Nashville, Tennessee, 37203, United States

Location

Urology San Antonio

San Antonio, Texas, 78229, United States

Location

Academisch Ziekenhuis Groeninge Campus Kennedylaan

Kortrijk, West Vlaanderen, Belgium

Location

Hospital Universitario de Jerez de la Frontera

Jerez de la Frontera, Cadiz, Spain

Location

Hospital de la Santa Creu i. Sant Pau

Barcelona, Spain

Location

Hospital del Mar Parc de Salut Mar

Barcelona, Spain

Location

Hospital Clinico San Carlos

Madrid, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, Spain

Location

Hospital Universitario La Paz

Madrid, Spain

Location

Clinica Universidad de Navarra

Pamplona, Spain

Location

MeSH Terms

Conditions

Prostatic Neoplasms

Interventions

tazemetostatabirateronePrednisoneAbiraterone Acetateenzalutamide

Condition Hierarchy (Ancestors)

Genital Neoplasms, MaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

PregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsAndrostenesAndrostanes

Limitations and Caveats

The study was terminated early as Sponsor decided to discontinue the development of tazemetostat in mCRPC and the primary endpoint was not met for this study. There were no safety concerns.

Results Point of Contact

Title
Medical Director
Organization
Ipsen

Study Officials

  • Ipsen Medical Director

    Ipsen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 14, 2019

First Posted

November 27, 2019

Study Start

November 18, 2019

Primary Completion

November 4, 2024

Study Completion

November 4, 2024

Last Updated

March 10, 2026

Results First Posted

March 10, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to patient level data and related study documents including the clinical study report, study protocol with any amendments, annotated case report form, statistical analysis plan, and dataset specifications. Patient level data will be anonymized and study documents will be redacted to protect the privacy of study participants.

Time Frame
Where applicable, data from eligible studies are available 6 months after the studied medicine and indication have been approved in the US and/or EU.
Access Criteria
Further details on Ipsen's sharing criteria and process for sharing are available here (https://www.ipsen.com/science/clinical-trials/clinical-data-transparency/).
More information

Locations