NCT04172246

Brief Summary

This is a Phase 1/2 study of zanubrutinib in Japanese participants with mature B-cell malignancies. This study intends to assess the use of zanubrutinib as an investigational agent to develop new treatment options for Japanese participants with B-cell malignancies. No formal hypothesis testing will be performed given the small sample size.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
55

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Jan 2020

Longer than P75 for phase_1

Geographic Reach
1 country

15 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 14, 2019

Completed
7 days until next milestone

First Posted

Study publicly available on registry

November 21, 2019

Completed
2 months until next milestone

Study Start

First participant enrolled

January 29, 2020

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 10, 2023

Completed
2.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2025

Completed
Last Updated

November 21, 2025

Status Verified

July 1, 2025

Enrollment Period

3.3 years

First QC Date

November 14, 2019

Last Update Submit

November 20, 2025

Conditions

Keywords

relapsed/refractory chronic lymphocytic leukemiarelapsed/refractory small lymphocytic lymphomatreatment-naïve chronic lymphocytic leukemiatreatment-naïve /small lymphocytic lymphomarelapsed/refractory mantle cell lymphomarelapsed/refractory marginal zone lymphomarelapsed/refractory follicular lymphomarelapsed/refractory Waldenström macroglobulinemiatreatment-naïve Waldenström macroglobulinemia

Outcome Measures

Primary Outcomes (6)

  • Part 1: Number of Participants Experiencing Treatment-Emergent Adverse Events (TEAEs)

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever is earlier

  • Part 1: Number of Participants Experiencing Treatment-Emergent Serious Adverse Events (SAEs)

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever is earlier

  • Part 1: Number of Participants Experiencing Adverse Events (AEs) Leading to Discontinuation of Treatment

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever is earlier

  • Part 1: Maximum Plasma Concentration (Cmax) of zanubrutinib

    Up to 29 days

  • Part 1: Area under plasma concentration-time curve Concentration (AUC) of zanubrutinib

    Up to 29 days

  • Part 2: Overall response rate as assessed by Independent Review Committee (IRC)

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever occurs first

Secondary Outcomes (20)

  • Part 1: Bruton tyrosine kinase (BTK) occupancy in peripheral blood mononuclear cells

    Predose up to 24 hours postdose

  • Part 1: Overall response rate (ORR) as assessed by the investigator

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever is earlier

  • Part 1: Progression-free survival (PFS) as assessed by the investigator

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever is earlier

  • Part 1: Duration of response as assessed by the investigator

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever is earlier

  • Part 1: Time to response as assessed by the investigator

    Until approximately 6 months after the last dose of zanubrutinib for the last participant who discontinues zanubrutinib or zanubrutinib becomes commercially available for the participant's disease, whichever is earlier

  • +15 more secondary outcomes

Study Arms (1)

Zanubrutinib

EXPERIMENTAL
Drug: Zanubrutinib

Interventions

Zanubrutinib at 160 mg orally twice daily

Also known as: BGB-3111
Zanubrutinib

Eligibility Criteria

Age20 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants with Confirmed diagnosis of mature B-cell neoplasms including chronic lymphocytic leukemia/ small lymphocytic lymphoma, mantle cell lymphoma, follicular lymphoma, marginal zone lymphoma and Waldenström's macroglobulinemia
  • Relapsed/refractory disease defined as disease that relapsed after, or been refractory to, at least 1 prior therapy
  • Meeting at least one of criteria for requiring treatment
  • Measurable disease by computed tomography (CT)/ magnetic resonance imaging (MRI) for mantle cell lymphoma (MCL), marginal zone lymphoma (MZL) and follicular lymphoma (FL) participants and by serum immunoglobulin (Ig) M level \> 0.5 g/dL for WM participants
  • Eastern Cooperative Oncology Group performance status of 0, 1, or 2
  • Life expectancy of \> 4 months

You may not qualify if:

  • Known central nervous system involvement by lymphoma/leukemia
  • Known plasma cell neoplasm, prolymphocytic leukemia, history of or currently suspected Richter's syndrome
  • Prior allogeneic stem cell transplant
  • Systemic chemotherapy or radiation therapy within 2 weeks prior to first dose of zanubrutinib
  • Active fungal, bacterial, and/or viral infection requiring systemic therapy
  • Prior therapy with B-cell receptor inhibitor (eg, Bruton tyrosine kinase, phosphoinositide 3 kinase delta, and/or spleen tyrosine kinase inhibitor) or B-cell lymphoma 2 inhibitor (eg, venetoclax/ABT-199)
  • Pregnant, lactating, or nursing women
  • Autoimmune anemia and/or thrombocytopenia that is poorly responsive to corticosteroids or other standard therapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

Nagoya University Hospital

Nagoya, Aichi-ken, 466-8560, Japan

Location

Toyohashi Municipal Hospital

Toyohashishi, Aichi-ken, 441-8570, Japan

Location

Chiba Cancer Center

Chiba, Chiba, 260-8717, Japan

Location

Matsuyama Red Cross Hospital

Matsuyama, Ehime, 790 8524, Japan

Location

Kurume University Hospital

KurumeShi, Fukuoka, 830-0011, Japan

Location

National Hospital Organization Hokkaido Cancer Center

Sapporo, Hokkaido, 003-0804, Japan

Location

Aiiku Hospital

Sapporo, Hokkaido, 064-0804, Japan

Location

Kobe City Medical Center General Hospital

KobeShi, Hyōgo, 650-0047, Japan

Location

Kanagawa Cancer Center

Yokohama, Kanagawa, 241-8515, Japan

Location

National Cancer Center Hospital

ChuoKu, Tokyo, 104-0045, Japan

Location

Aomori Prefectural Central Hospital

Aomori, 030-8553, Japan

Location

Gifu Municipal Hospital

Gifu, 500-8513, Japan

Location

The Japanese Red Cross Nagasaki Genbaku Hospital

Nagasaki, 852-8511, Japan

Location

National Hospital Organization Okayama Medical Center

Okayama, 701-1192, Japan

Location

Yokohama Municipal Citizens Hospital

Yokohama, 221-0855, Japan

Location

MeSH Terms

Conditions

Leukemia, Lymphocytic, Chronic, B-CellLymphoma, Mantle-CellLymphoma, B-Cell, Marginal ZoneLymphoma, FollicularWaldenstrom Macroglobulinemia

Interventions

zanubrutinib

Condition Hierarchy (Ancestors)

Leukemia, B-CellLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsLymphoma, Non-HodgkinLymphomaLymphoma, B-CellNeoplasms, Plasma CellHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHemorrhagic Disorders

Study Officials

  • Study Director

    BeiGene

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 14, 2019

First Posted

November 21, 2019

Study Start

January 29, 2020

Primary Completion

May 10, 2023

Study Completion

June 30, 2025

Last Updated

November 21, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

BeiGene shares data on completed studies responsibly and provides qualified scientific and medical researchers access to data and supporting documentation for clinical trials in dossiers for medicines and indications after submission and approval in the United States, China, and Europe. Clinical trials supporting subsequent local approvals, new indications, or combination products are eligible for sharing once corresponding regulatory approvals are achieved. BeiGene shares data only when permitted by applicable data privacy and security laws and regulations, when it is feasible to do so without compromising the privacy of study participants, and other considerations. Qualified researchers with appropriate competencies who are engaged in novel scientific research may submit a request for participant-level data with a research proposal for BeiGene review. Research teams must include a biostatistician and sign a Data Sharing Agreement prior to receiving access to clinical trial data.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
See plan description
Access Criteria
See plan description
More information

Locations