NCT04106219

Brief Summary

The reason for this study is to see if the study drug LY3295668 erbumine is safe in participants with relapsed/refractory neuroblastoma.

Trial Health

82
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
71

participants targeted

Target at P75+ for phase_1

Timeline
2mo left

Started Jun 2020

Longer than P75 for phase_1

Geographic Reach
9 countries

17 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress98%
Jun 2020Aug 2026

First Submitted

Initial submission to the registry

September 25, 2019

Completed
1 day until next milestone

First Posted

Study publicly available on registry

September 26, 2019

Completed
9 months until next milestone

Study Start

First participant enrolled

June 11, 2020

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 13, 2022

Completed
4.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2026

Expected
Last Updated

April 21, 2026

Status Verified

April 1, 2026

Enrollment Period

1.8 years

First QC Date

September 25, 2019

Last Update Submit

April 16, 2026

Conditions

Keywords

aurora kinase Akinaseaurora Aaurora kinase inhibitoraurora kinase A inhibitorkinase inhibitorAURKAAurApediatric neuroblastomachildren

Outcome Measures

Primary Outcomes (3)

  • Number of Participants with Dose Limiting Toxicities (DLTs)

    Number of Participants with DLTs

    Baseline through Cycle 2 (28 Day Cycle)

  • Overall Response Rate (ORR): Percentage of Participants Who Achieve Complete Response (CR) or Partial Response (PR)

    ORR

    Baseline through Measured Progressive Disease (Estimated up to 5 Years)

  • Duration of Response (DoR)

    DoR

    Date of CR or PR to Date of Disease Progression or Death Due to Any Cause (Estimated up to 5 Years)

Secondary Outcomes (5)

  • Pharmacokinetics (PK): Area Under the Concentration Time Curve (AUC) of LY3295668

    Cycle 1 Day 1 through Cycle 1 Day 15 (28 Day Cycles)

  • PK: AUC of LY3295668 in Combination with Topotecan and Cyclophosphamide

    Cycle 1 Day 1 through Cycle 1 Day 15 (28 Day Cycles)

  • Best Overall Response (BOR): Percentage of Participants with CR, PR, Stable Disease (SD), or Progressive Disease (PD)

    Baseline to Date of Objective Disease Progression (Estimated up to 5 Years)

  • Progression-Free Survival (PFS)

    Baseline to Objective Progression or Death Due to Any Cause (Estimated up to 5 Years)

  • Overall Survival (OS)

    Baseline to Date of Death from Any Cause (Estimated up to 6 Years)

Study Arms (4)

LY3295668 Erbumine Escalation

EXPERIMENTAL

LY3295668 Erbumine given orally.

Drug: LY3295668 Erbumine

LY3295668 Erbumine + Topotecan + Cyclophosphamide Escalation

EXPERIMENTAL

LY3295668 Erbumine given orally and topotecan and cyclophosphamide given intravenously (IV).

Drug: LY3295668 ErbumineDrug: TopotecanDrug: Cyclophosphamide

LY3295668 Erbumine Expansion

EXPERIMENTAL

LY3295668 Erbumine given orally.

Drug: LY3295668 Erbumine

LY3295668 Erbumine + Topotecan + Cyclophosphamide Expansion

EXPERIMENTAL

LY3295668 Erbumine given orally and topotecan and cyclophosphamide given IV.

Drug: LY3295668 ErbumineDrug: TopotecanDrug: Cyclophosphamide

Interventions

Administered orally.

LY3295668 Erbumine + Topotecan + Cyclophosphamide EscalationLY3295668 Erbumine + Topotecan + Cyclophosphamide ExpansionLY3295668 Erbumine EscalationLY3295668 Erbumine Expansion

Administered IV.

LY3295668 Erbumine + Topotecan + Cyclophosphamide EscalationLY3295668 Erbumine + Topotecan + Cyclophosphamide Expansion

Administered IV.

LY3295668 Erbumine + Topotecan + Cyclophosphamide EscalationLY3295668 Erbumine + Topotecan + Cyclophosphamide Expansion

Eligibility Criteria

Age2 Years - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Participants must have relapsed/refractory neuroblastoma and have active disease in at least one site: bone, bone marrow or soft tissue. Participants must be able to submit an archival sample of tissue.
  • Participants must be able to swallow capsules.

You may not qualify if:

  • Participants must not have had an allogeneic hematopoietic stem cell, bone marrow, or solid organ transplant.
  • Participants must not have untreated tumor that has spread to the brain or spinal cord.
  • Participants must not have a serious active disease other than neuroblastoma.
  • Participants must not have a condition affecting absorption.
  • Participants must not have had prior aurora kinase inhibitor exposure.
  • Participants must not have a known allergy to the study treatment.
  • Participants must not have symptomatic human immunodeficiency virus (HIV) infection or symptomatic activated/reactivated hepatitis A, B, or C.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (17)

UCSF Medical Center at Mission Bay

San Francisco, California, 94158, United States

Location

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

Location

University of Chicago - Comer Children's Hospital

Chicago, Illinois, 60637, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02115, United States

Location

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

Texas Childrens Hospital

Houston, Texas, 77030, United States

Location

Perth Children's Hospital

Perth, Western Australia, 6009, Australia

Location

UZ Gent

Ghent, Oost-Vlaanderen, 9000, Belgium

Location

Centre Leon Berard

Lyon, Auvergne-Rhône-Alpes, 69373 CEDEX 08, France

Location

Institut Curie

Paris, 75248, France

Location

Universitätsklinikum Köln

Cologne, 50924, Germany

Location

Istituto Nazionale dei Tumori

Milan, Lombardy, 20133, Italy

Location

National Cancer Center Hospital

Chuo-ku, Tokyo, 104-0045, Japan

Location

Hospital Universitari Vall d'Hebron

Barcelona, Barcelona [Barcelona], 8035, Spain

Location

Hospital Infantil Universitario Niño Jesús

Madrid, 28009, Spain

Location

Alder Hey Children's Hospital

Liverpool, L14 5AB, United Kingdom

Location

Related Links

MeSH Terms

Conditions

NeuroblastomaEpilepsy

Interventions

LY3295668 erbumineTopotecanCyclophosphamide

Condition Hierarchy (Ancestors)

Neuroectodermal Tumors, Primitive, PeripheralNeuroectodermal Tumors, PrimitiveNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

CamptothecinAlkaloidsHeterocyclic CompoundsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus Compounds

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 25, 2019

First Posted

September 26, 2019

Study Start

June 11, 2020

Primary Completion

April 13, 2022

Study Completion (Estimated)

August 1, 2026

Last Updated

April 21, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will not share

Locations