NCT04092452

Brief Summary

This is a study with 3 kinase inhibitors (PF 06650833, PF 06700841 and PF 06826647) in participants with moderate to severe HS. The study will have a maximum duration of approximately 26 weeks. This includes an up to 6-week Screening Period, a 16 week Dosing Period and a 4 week Follow up Period.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
194

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2019

Geographic Reach
3 countries

77 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 15, 2019

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 17, 2019

Completed
3 months until next milestone

Study Start

First participant enrolled

December 2, 2019

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 10, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 10, 2022

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

June 15, 2023

Completed
Last Updated

June 15, 2023

Status Verified

May 1, 2023

Enrollment Period

2.1 years

First QC Date

September 15, 2019

Results QC Date

December 24, 2022

Last Update Submit

May 19, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Achieving Hidradenitis Suppurativa Clinical Response (HiSCR) at Week 16- Minimum Risk (MR) [Full Analysis Set (FAS), Non-responder Imputation (NRI)].

    HiSCR response was defined as at least a 50% reduction in total abscess and inflammatory nodule (AN) count relative to baseline, and no increase in abscess count, and no increase in draining fistula count. Confidence interval (CI) was calculated using Blyth-Still-Casella method.

    At week 16

Secondary Outcomes (24)

  • Percentage of Participants Achieving HiSCR Response at Weeks 1, 2, 4, 6, 8, and 12 - MR (FAS, NRI).

    At weeks 1, 2, 4, 6, 8, and 12

  • Percentage of Participants Achieving a Total Abscess and Inflammatory Nodule (AN) Count of 0 or 1; 0, 1 or 2 at Week 16 - MR (FAS, NRI).

    At week 16

  • Least Squares (LS) Mean of Percent Change From Baseline in AN Count at Weeks 1, 2, 4, 6, 8, 12 and 16 - Analysis of Covariance (ANCOVA) [FAS, Multiply Imputed (MI)].

    At weeks 1, 2, 4, 6, 8, 12 and 16

  • Least Squares Mean of Absolute Score in International Hidradenitis Suppurativa Severity Score System (IHS4) at Weeks 1, 2, 4, 6, 8, 12 and 16 - ANCOVA (FAS, MI).

    At weeks 1, 2, 4, 6, 8, 12 and 16

  • Least Squares Mean of Percent Change From Baseline in International Hidradenitis Suppurativa Severity Score System (IHS4) at Weeks 1, 2, 4, 6, 8, 12 and 16 - ANCOVA (FAS, MI).

    At weeks 1, 2, 4, 6, 8, 12 and 16

  • +19 more secondary outcomes

Study Arms (4)

Cohort 1

EXPERIMENTAL

PF-06650833

Drug: PF-06650833

Cohort 2

EXPERIMENTAL

PF-6700841

Drug: PF-06700841

Cohort 3

EXPERIMENTAL

PF-06826647

Drug: PF-06826647

Cohort placebo

PLACEBO COMPARATOR

placebo

Drug: Placebo

Interventions

400 mg QD

Cohort 1

45 mg QD

Cohort 2

400 mg QD

Cohort 3

placebo

Cohort placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • male or female participants, between 18-75, with a diagnosis of moderate to severe Hidradenitis Suppurativa

You may not qualify if:

  • History of human immunodeficiency virus (HIV) or positive HIV serology at screening,
  • Infected with hepatitis B or hepatitis C viruses.
  • Have evidence of active or latent or inadequately treated infection with Mycobacterium tuberculosis (TB)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (77)

The University Of Alabama At Birmingham

Birmingham, Alabama, 35233, United States

Location

The University of Alabama at Birmingham Hospital Outreach Lab

Birmingham, Alabama, 35249, United States

Location

The University of Alabama at Birmingham Investigation Drug Services Pharmacy

Birmingham, Alabama, 35249, United States

Location

The University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Mayo Clinic

Scottsdale, Arizona, 85259, United States

Location

Center for Dermatology Clinical Research, Inc.

Fremont, California, 94538, United States

Location

Pacific Clinical Trials

Long Beach, California, 90806, United States

Location

Keck School of Medicine of University of Southern California

Los Angeles, California, 90033, United States

Location

UCSF Dermatology Clinic

San Francisco, California, 94115, United States

Location

University of California San Francisco

San Francisco, California, 94115, United States

Location

UCSF Psoriasis and Skin Treatment Center

San Francisco, California, 94118, United States

Location

Clinical Science Institute

Santa Monica, California, 90404, United States

Location

New England Research Associates, LLC

Bridgeport, Connecticut, 06606, United States

Location

Dermatology Physicians of Connecticut

Shelton, Connecticut, 06484, United States

Location

Total Dermatology Care Center

Jacksonville, Florida, 32204, United States

Location

Jacksonville Center for Clinical Research

Jacksonville, Florida, 32216, United States

Location

Olympian Clinical Research Largo Office

Largo, Florida, 33770, United States

Location

University of Miami Hospital

Miami, Florida, 33125, United States

Location

Tory Sullivan MD PA

North Miami Beach, Florida, 33162, United States

Location

Renstar Medical Research

Ocala, Florida, 34470, United States

Location

MidState Skin Institute

Ocala, Florida, 34471, United States

Location

Renstar Medical Research

Ocala, Florida, 34471, United States

Location

Park Avenue Dermatology

Orange Park, Florida, 32073, United States

Location

Leavitt Medical Associates of Florida d/b/a Ameriderm Research

Ormond Beach, Florida, 32174, United States

Location

Riverchase Dermatology and Cosmetic Surgery

Pembroke Pines, Florida, 33028, United States

Location

ForCare Clinical Research

Tampa, Florida, 33613, United States

Location

Alliance Clinical Research of Tampa

Tampa, Florida, 33615, United States

Location

MedaPhase Inc.

Newnan, Georgia, 30263, United States

Location

Advanced Medical Research PC

Sandy Springs, Georgia, 30328, United States

Location

Georgia Skin Cancer and Aesthetic Dermatology

Watkinsville, Georgia, 30677, United States

Location

NorthShore University HealthSystem Dermatology Clinic

Skokie, Illinois, 60077, United States

Location

Ds Research

Clarksville, Indiana, 47129, United States

Location

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, 46250, United States

Location

DS Research

Louisville, Kentucky, 40241, United States

Location

Boston Medical Center

Boston, Massachusetts, 02118, United States

Location

Boston University General Clinical Research Unit

Boston, Massachusetts, 02118, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Wayne State University / Integrative Biosciences Center

Detroit, Michigan, 48202, United States

Location

Revival Research Institute, LLC

Troy, Michigan, 48084, United States

Location

Clinical Research Unit

Minneapolis, Minnesota, 55455, United States

Location

Lillihei Clinical Research Unit

Minneapolis, Minnesota, 55455, United States

Location

University of Minnesota Department of Dermatology

Minneapolis, Minnesota, 55455, United States

Location

MediSearch Clinical Trials

Saint Joseph, Missouri, 64506, United States

Location

Saint Louis University - Department of Dermatology

St Louis, Missouri, 63110, United States

Location

Skin Specialists PC

Omaha, Nebraska, 68144, United States

Location

J Woodson Clinical Studies Group

Henderson, Nevada, 89052, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Vital Prospects Clinical Research Institute

Tulsa, Oklahoma, 74136, United States

Location

Penn State Health Milton S. Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Penn State Health Radiology - University Physician Center

Hershey, Pennsylvania, 17033, United States

Location

Paddington Testing Company, Inc

Philadelphia, Pennsylvania, 19103, United States

Location

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, 19107, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

Dermatology and Skin Cancer Consultants

Humboldt, Tennessee, 38343, United States

Location

Clinical Research Solutions

Jackson, Tennessee, 38305, United States

Location

Dermatology and Skin Cancer Consultants

Jackson, Tennessee, 38305, United States

Location

Arlington Research Center

Arlington, Texas, 76011, United States

Location

Austin Institute for Clinical Research, Inc.

Pflugerville, Texas, 78660, United States

Location

University of Utah MidValley Dermatology

Murray, Utah, 84107, United States

Location

Virginia Commonwealth University Medical Center

Richmond, Virginia, 23298, United States

Location

Bellevue Dermatology Clinical Research Center

Bellevue, Washington, 98004, United States

Location

Bellevue Dermatology Clinic

Bellevue, Washington, 98004, United States

Location

Dermatology Associates of Seattle

Seattle, Washington, 98101, United States

Location

Woden Dermatology

Phillip, Australian Capital Territory, 2606, Australia

Location

Premier Specialists Pty Ltd

Kogarah, New South Wales, 2217, Australia

Location

Holdsworth House Medical Practice

Sydney, New South Wales, 2010, Australia

Location

Veracity Clinical Research

Woolloongabba, Queensland, 4102, Australia

Location

Skin Health Institute Inc.

Carlton, Victoria, 3053, Australia

Location

Sinclair Dermatology

East Melbourne, Victoria, 3002, Australia

Location

SimcoDerm Medical and Surgical Dermatology Center

Barrie, Ontario, L4M 7G1, Canada

Location

Manna Research (London)

London, Ontario, N6A 2C2, Canada

Location

DermEffects

London, Ontario, N6H 5L5, Canada

Location

SKiN Centre for Dermatology

Peterborough, Ontario, K9J 5K2, Canada

Location

The Centre for Dermatology

Richmond Hill, Ontario, L4B 1A5, Canada

Location

Diex Recherche Sherbrooke Inc.

Sherbrooke, Quebec, J1L 0H8, Canada

Location

Centre de Recherche Saint-Louis

Québec, G1W4R4, Canada

Location

Alpha Recherche Clinique

Québec, G2J 0C4, Canada

Location

Related Publications (1)

  • Kimball AB, Peeva E, Forman S, Moiin A, Khattri S, Porter ML, Mangold AR, Ghosh P, Banfield C, Oemar B. Brepocitinib, Zimlovisertib, and Ropsacitinib in Hidradenitis Suppurativa. NEJM Evid. 2024 Mar;3(3):EVIDoa2300155. doi: 10.1056/EVIDoa2300155. Epub 2024 Feb 9.

Related Links

MeSH Terms

Conditions

Hidradenitis Suppurativa

Interventions

1-(((2S,3S,4S)-3-ethyl-4-fluoro-5-oxopyrrolidin-2-yl)methoxy)-7-methoxyisoquinoline-6-carboxamidePF-06700841ropsacitinib

Condition Hierarchy (Ancestors)

Skin Diseases, BacterialBacterial InfectionsBacterial Infections and MycosesInfectionsSkin Diseases, InfectiousSuppurationSkin DiseasesSkin and Connective Tissue DiseasesHidradenitisSweat Gland Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: The treatment period is a parallel design
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 15, 2019

First Posted

September 17, 2019

Study Start

December 2, 2019

Primary Completion

January 10, 2022

Study Completion

January 10, 2022

Last Updated

June 15, 2023

Results First Posted

June 15, 2023

Record last verified: 2023-05

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations