NCT04089449

Brief Summary

This is a Phase 1 dose-escalation study of PRT811, a protein arginine N-methyltransferase (PRMT) 5 inhibitor, in subjects with advanced cancers and high-grade gliomas who have exhausted available treatment options. The purpose of this study is to define a safe dose and schedule to be used in subsequent development of PRT811.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
86

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Nov 2019

Typical duration for phase_1

Geographic Reach
1 country

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 11, 2019

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 13, 2019

Completed
2 months until next milestone

Study Start

First participant enrolled

November 6, 2019

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 28, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 28, 2023

Completed
Last Updated

April 5, 2023

Status Verified

April 1, 2023

Enrollment Period

3.4 years

First QC Date

September 11, 2019

Last Update Submit

April 3, 2023

Conditions

Keywords

PRMT5PRMT5 Inhibitor

Outcome Measures

Primary Outcomes (3)

  • To describe dose limiting toxicities (DLT) of PRT811

    Dose limiting toxicities will be evaluated through the first cycle

    Baseline through Day 21

  • To determine the maximally tolerated dose (MTD)

    The MTD will be established for further investigation in participants with solid tumors and gliomas

    Baseline through approximately 2 years

  • To determine the recommended phase 2 dose (RP2D) and schedule of PRT811

    The RP2D will be established for further investigation in participants with solid tumors and gliomas

    Baseline through approximately 2 years

Secondary Outcomes (3)

  • To describe the adverse event profile and tolerability of PRT811

    Baseline through approximately 2 years

  • To describe the pharmacokinetic profile of PRT811

    Cycle 1 (each cycle is 21 days) on Days 1, 8 and 14. For subsequent cycles, Day 1 of each cycle through the end of study treatment, an average of 6 months

  • To describe any anti-tumor activity of PRT811

    Baseline through approximately 2 years

Study Arms (1)

PRT811

EXPERIMENTAL

PRT811 will be administered orally

Drug: PRT811

Interventions

PRT811DRUG

PRT811 will be administered orally

PRT811

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Malignancies that are refractory to or intolerant of established therapies known to provide clinical benefit for the malignancy in question, or in the opinion of the Investigator, not be a candidate for such therapies
  • Subjects must have recovered from the effects of any prior investigational system therapies
  • For subjects with recurrent high-grade glioma or GBM, must have biopsy proven evidence (WHO Grade III or IV) and received external bean fractionated radiotherapy and at least 2 cycles of adjuvant temozolomide chemotherapy. Mutant Glioma must comply with biomarker defined enrollment criterias.
  • For biomarker-selected solid tumors: must meet enrollment criteria
  • Eastern Cooperative Oncology Group (ECOG) Performance Score of 0 or 1
  • Adequate organ function (bone marrow, hepatic, renal, cardiovascular)
  • Female subjects of childbearing potential must have a negative pregnancy test within 7 days of the start of treatment and must agree to use an effective method of contraception during the trial

You may not qualify if:

  • Untreated concurrent malignancies or malignancies that have been in complete remission for less than one year
  • Treatment with strong inhibitors of CYP3A4 for which there are no therapeutic substitutions
  • Inflammatory disorders of the gastrointestinal tract, or subjects with GI malabsorption
  • HIV positive; known active hepatitis B or C
  • Known hypersensitivity to any of the components of PRT811

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

Sarah Cannon Research Institute at HealthONE

Denver, Colorado, 80218, United States

Location

Yale- New Haven Hospital- Yale Cancer Center

New Haven, Connecticut, 06510, United States

Location

Christiana Care Health Services, Christiana Hospital

Newark, Delaware, 19718, United States

Location

Florida Cancer Specialists

Lake Mary, Florida, 32746, United States

Location

Georgia Cancer Center at Augusta University

Augusta, Georgia, 30912, United States

Location

Northwestern Memorial Hospital

Chicago, Illinois, 60611, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

Washington University School of Medicine - Siteman Cancer Center

St Louis, Missouri, 63110, United States

Location

The Ohio State University and Wexner Medical Center

Columbus, Ohio, 43210, United States

Location

Thomas Jefferson University, Sidney Kimmel Cancer Center

Philadelphia, Pennsylvania, 19107, United States

Location

Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

Related Publications (1)

  • Barry A, Samuel SF, Hosni I, Moursi A, Feugere L, Sennett CJ, Deepak S, Achawal S, Rajaraman C, Iles A, Wollenberg Valero KC, Scott IS, Green V, Stead LF, Greenman J, Wade MA, Beltran-Alvarez P. Investigating the effects of arginine methylation inhibitors on microdissected brain tumour biopsies maintained in a miniaturised perfusion system. Lab Chip. 2023 May 30;23(11):2664-2682. doi: 10.1039/d3lc00204g.

MeSH Terms

Conditions

Glioma

Condition Hierarchy (Ancestors)

Neoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 11, 2019

First Posted

September 13, 2019

Study Start

November 6, 2019

Primary Completion

March 28, 2023

Study Completion

March 28, 2023

Last Updated

April 5, 2023

Record last verified: 2023-04

Locations