NCT04061811

Brief Summary

Objectives: The aim of this study is to determine whether growth differentiation factor-15 (GDF15) and circulating neprilysin (cNEP) improve the diagnosis of congestive heart failure (HF) in patients on dialysis. Background: Dialysis patients are at increased risk of HF. However, diagnostic utility of NT-proBNP as a biomarker is decreased in patients on dialysis. GDF15 and cNEP are biomarkers of distinct mechanisms that may contribute to HF pathophysiology in such cohorts. Methods: We compare circulating concentrations of NT-proBNP, GDF15, and cNEP along with NEP activity in patients on chronic dialysis without and with HF, as diagnosed by clinical parameters and post-dialysis echocardiography. We use correlation, linear and logistic regression as well as receiver operating characteristic (ROC) analyses.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
153

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Aug 2018

Shorter than P25 for all trials

Geographic Reach
2 countries

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2018

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 28, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 28, 2019

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

August 16, 2019

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 20, 2019

Completed
Last Updated

August 20, 2019

Status Verified

August 1, 2019

Enrollment Period

7 months

First QC Date

August 16, 2019

Last Update Submit

August 19, 2019

Conditions

Keywords

congestive heart failure (HF)biomarkerchronic kidney disease (CKD)hemodialysis (HD)peritoneal dialysis (PD)neprilysin (NEP)growth differentiation factor-15 (GDF15)

Outcome Measures

Primary Outcomes (1)

  • HF diagnosis

    Diagnosis of HF

    Baseline (at study entry (diagnostic biomarker study))

Study Arms (2)

HF (heart failure)

Patients with end stage renal disease requiring dialysis with reduced or preserved ejection fraction.

Diagnostic Test: Diagnostic biomarker study

Control

Patients with end stage renal disease requiring dialysis without HF.

Diagnostic Test: Diagnostic biomarker study

Interventions

Comparing circulating concentrations of NT-proBNP, GDF15, and neprilysin (NEP) along with NEP activity in patients with and without HF, as diagnosed by clinical parameters and post-dialysis echocardiography.

ControlHF (heart failure)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

End stage renal disease (ESRD) patients on chronic dialysis.

You may qualify if:

  • ESRD on either chronic hemodialysis (HD) or peritoneal dialysis (PD) for ≥3 months

You may not qualify if:

  • previous switch of the type of renal replacement therapy from HD to PD or vice versa
  • age \<18 years
  • pregnancy
  • plasma exchange or apheresis in the past 6 months
  • unipolar pacemaker
  • history of whole extremity amputation

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Inserm Umr S-942

Paris, France

Location

Hannover Medical School

Hanover, 30175, Germany

Location

Biospecimen

Retention: SAMPLES WITHOUT DNA

Plasma, serum, peritoneal dialysate.

MeSH Terms

Conditions

Heart FailureKidney Failure, ChronicRenal Insufficiency, Chronic

Condition Hierarchy (Ancestors)

Heart DiseasesCardiovascular DiseasesRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Michael S Balzer, MD

    Hannover Medical School

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
OTHER
Time Perspective
CROSS SECTIONAL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Postdoctoral fellow

Study Record Dates

First Submitted

August 16, 2019

First Posted

August 20, 2019

Study Start

August 1, 2018

Primary Completion

February 28, 2019

Study Completion

February 28, 2019

Last Updated

August 20, 2019

Record last verified: 2019-08

Data Sharing

IPD Sharing
Will not share

Locations