NCT03959488

Brief Summary

The purpose of this study is to evaluate the safety and tolerability of MEDI8897 compared to palivizumab when administered to preterm infants entering their first RSV season and children with chronic lung disease (CLD) and congenital heart disease (CHD) entering their first and second RSV season.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
925

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jul 2019

Typical duration for phase_2

Geographic Reach
25 countries

126 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 21, 2019

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 22, 2019

Completed
2 months until next milestone

Study Start

First participant enrolled

July 30, 2019

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 3, 2021

Completed
1.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 20, 2023

Completed
8 months until next milestone

Results Posted

Study results publicly available

September 21, 2023

Completed
Last Updated

September 21, 2023

Status Verified

September 1, 2023

Enrollment Period

1.8 years

First QC Date

May 21, 2019

Results QC Date

August 16, 2023

Last Update Submit

September 20, 2023

Conditions

Keywords

Respiratory Syncytial Virus InfectionsPreterm InfantsLower Respiratory Infection

Outcome Measures

Primary Outcomes (1)

  • Safety and Tolerability of MEDI8897 as Assessed by the Occurrence of All Treatment Emergent Adverse Events (TEAEs) and Treatment Emergent Serious Adverse Events (TESAEs) and Adverse Events of Special Interest (AESIs) and New Onset Chronic Disease (NOCD)

    Safety and tolerability of MEDI8897 will be assessed by the occurrence of all treatment-emergent adverse events (TEAEs), treatment-emergent serious adverse events (TESAEs) , adverse events of special interest (AESIs), and new onset chronic diseases (NOCDs)

    360 days post first dose

Secondary Outcomes (3)

  • Serum Concentrations of MEDI8897 and Palivizumab

    Day 15, Day 31, Day 151 post first dose in Season 1 and Season 2

  • Incidence of Anti-drug Antibody (ADA) to MEDI8897 and Palivizumab in Serum

    360 days post first dose

  • Incidence of Medically Attended Lower Respiratory Track Infection (LRTI) and Hospitalization Due to Reverse Transcriptase Chain Reaction (RT-PCR) Confirmed Respiratory Syncytial Virus (RSV) Through 150 Days Post First Dose

    150 days post first dose

Study Arms (2)

MEDI8897

EXPERIMENTAL

anti-RSV monoclonal antibody with an extended half-life

Drug: MEDI8897

Palivizumab

ACTIVE COMPARATOR

anti-RSV monoclonal antibody

Drug: Palivizumab

Interventions

Anti-RSV monoclonal antibody with an extended half-life

MEDI8897

Approved anti-RSV monoclonal antibody

Palivizumab

Eligibility Criteria

Age0 Years - 1 Year
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • For the preterm cohort (excluding subjects with CLD or hemodynamically significant CHD): preterm infants in their first year of life and born ≤ 35 weeks 0 days GA eligible to receive palivizumab in accordance with national or local guidelines, including those with:
  • Uncomplicated small atrial or ventricular septal defects or patent ductus arteriosus, or
  • Aortic stenosis, pulmonic stenosis, or coarctation of the aorta alone
  • For the CLD/CHD cohort:
  • Subjects with CLD - infants in their first year of life and a diagnosis of CLD of prematurity requiring medical intervention/management (ie, supplemental oxygen, bronchodilators, or diuretics) within the 6 months prior to randomization
  • Subjects with CHD - infants in their first year of life and documented, hemodynamically significant CHD (must be unoperated or partially corrected CHD) Note: Infants with hemodynamically significant acyanotic cardiac lesions must have pulmonary hypertension (≥ 40 mmHg measured pressure in the pulmonary artery) or the need for daily medication to manage CHD
  • Infants who are entering their first RSV season at the time of screening
  • Written informed consent and any locally required authorization (eg, Health Insurance Portability and Accountability Act in the USA, EU Data Privacy Directive in the EU) obtained from the subject's parent(s)/legal representative(s) prior to performing any protocol-related procedures, including screening evaluations
  • Subject's parent(s)/legal representative(s) able to understand and comply with the requirements of the protocol including follow-up and illness visits as judged by the investigator
  • Subject is available to complete the follow-up period, which will be 1 year after Season 1/ Dose 1 for subjects without CLD/CHD, or 1 year after Season 2/Dose 1 (or last replacement dose as applicable for CHD) for subjects with CLD/CHD

You may not qualify if:

  • Any fever (≥ 100.4°F \[≥ 38.0°C\], regardless of route) or acute illness within 7 days prior to randomization
  • Any history of LRTI or active LRTI prior to, or at the time of, randomization
  • Known history of RSV infection or active RSV infection prior to, or at the time of, randomization
  • Hospitalization at the time of randomization, unless discharge is expected within the 7 days after randomization
  • Requirement for mechanical ventilation, extracorporeal membrane oxygenation, CPAP, or other mechanical respiratory or cardiac support at the time of randomization
  • Anticipated cardiac surgery within 2 weeks after randomization
  • Anticipated survival of \< 6 months after randomization
  • Receipt of any investigational drug
  • Known renal impairment
  • Known hepatic dysfunction including known or suspected active or chronic hepatitis infection
  • Clinically significant congenital anomaly of the respiratory tract
  • Chronic seizure, or evolving or unstable neurologic disorder
  • Prior history of a suspected or actual acute life-threatening event
  • Known immunodeficiency, including human immunodeficiency virus (HIV)
  • Mother with HIV infection (unless the child has been proven to be not infected)
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (128)

Research Site

Anaheim, California, 92804, United States

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Long Beach, California, 90806, United States

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Los Angeles, California, 90027, United States

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National City, California, 91950, United States

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Paramount, California, 90723, United States

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West Covina, California, 91790, United States

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Aurora, Colorado, 80045, United States

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Colorado Springs, Colorado, 80922, United States

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Washington D.C., District of Columbia, 20016, United States

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Atlanta, Georgia, 30322, United States

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Chicago, Illinois, 60611, United States

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Indianapolis, Indiana, 46202, United States

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South Bend, Indiana, 46617, United States

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West Des Moines, Iowa, 50266, United States

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Louisville, Kentucky, 40202, United States

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Jackson, Mississippi, 39216, United States

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Columbia, Missouri, 65201, United States

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Mineola, New York, 11501, United States

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Syracuse, New York, 13210, United States

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Durham, North Carolina, 27710, United States

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Greenville, North Carolina, 27834, United States

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Cincinnati, Ohio, 45229, United States

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Columbus, Ohio, 43205, United States

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Greenville, South Carolina, 29607, United States

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Corpus Christi, Texas, 78411, United States

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Layton, Utah, 84041, United States

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St. George, Utah, 84790, United States

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Charlottesville, Virginia, 22902, United States

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Seattle, Washington, 98105, United States

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Morgantown, West Virginia, 26506, United States

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Graz, 8036, Austria

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Brussels, 1200, Belgium

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Ghent, 9000, Belgium

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Montana, 3400, Bulgaria

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Pazardzhik, 4400, Bulgaria

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Pleven, 5800, Bulgaria

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Plovdiv, 4000, Bulgaria

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Plovdiv, 4003, Bulgaria

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Rousse, 7002, Bulgaria

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Sliven, 8800, Bulgaria

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Sofia, 1309, Bulgaria

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Sofia, 1407, Bulgaria

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Veliko Tarnovo, 5000, Bulgaria

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Edmonton, Alberta, T6G 1C9, Canada

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Vancouver, British Columbia, V6H 3V4, Canada

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Prague, 14710, Czechia

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Tallinn, 13419, Estonia

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Tartu, 51014, Estonia

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Tampere, 33100, Finland

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Amiens, 80054, France

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Bordeaux, 33000, France

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Brest, 29609, France

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Bron, 69677, France

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Caen, 1403, France

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Créteil, 94010, France

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Grenoble, 38043, France

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Marseille, 13015, France

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Pau, 64046, France

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Frankenthal, 67227, Germany

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Leipzig, 04103, Germany

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Mannheim, 68161, Germany

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Baja, 6500, Hungary

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Budapest, 1096, Hungary

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Debrecen, 4032, Hungary

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Kecskemét, 6000, Hungary

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Miskolc, 3526, Hungary

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Pisa, 56126, Italy

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Verona, 37126, Italy

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Fukui-shi, 918-8503, Japan

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Fukuoka, 813-0017, Japan

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Kitakyusyu-shi, 806-8501, Japan

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Maebashi, 371-0811, Japan

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Saitama Shi, 336 8522, Japan

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Setagaya-ku, 157-8535, Japan

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Jēkabpils, LV-5201, Latvia

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Riga, 1004, Latvia

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Riga, LV1002, Latvia

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Kaunas, 48259, Lithuania

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Kaunas, 50161, Lithuania

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Cuernavaca, 62290, Mexico

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México, 06720, Mexico

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Christchurch, 8011, New Zealand

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Bydgoszcz, 85 168, Poland

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Gdansk, 80-214, Poland

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Krakow, 30-348, Poland

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Krakow, 31-624, Poland

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Wroclaw, 51-169, Poland

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Kazan', 420012, Russia

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Novosibirsk, 630089, Russia

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Perm, 614066, Russia

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Saint Petersburg, 191025, Russia

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Saint Petersburg, 193312, Russia

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Saint Petersburg, 197341, Russia

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Yaroslavl, 150003, Russia

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Cape Town, 7505, South Africa

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Cape Town, 7800, South Africa

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Johannesburg, 2112, South Africa

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Johannesburg, 2193, South Africa

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Pretoria, 0087, South Africa

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Pretoria, 0101, South Africa

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Soweto, 2013, South Africa

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Ansan-si, 15355, South Korea

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Seoul, 06351, South Korea

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Suwon, 16499, South Korea

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Alicante, 03010, Spain

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Boadilla del Monte, 28660, Spain

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Elche, 03203, Spain

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Leganés, 28911, Spain

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Lleida, 25198, Spain

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Madrid, 28046, Spain

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Málaga, 29004, Spain

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Pozuelo de Alarcón, 28223, Spain

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Sant Cugat del Vallès, 08190, Spain

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Tarragona, 43007, Spain

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Stockholm, 118 83, Sweden

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Adana, 01330, Turkey (Türkiye)

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Izmir, 35100, Turkey (Türkiye)

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Kocaeli, 41380, Turkey (Türkiye)

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Chernivtsі, 58001, Ukraine

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Dnipro, 49006, Ukraine

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Ivano-Frankivsk, 76014, Ukraine

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Kharkiv Region, 61093, Ukraine

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Odesa, 65031, Ukraine

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Sumy, 40022, Ukraine

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Vinnytsia, 21000, Ukraine

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Leicester, LE3 9QP, United Kingdom

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London, W2 1NY, United Kingdom

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Nottingham, NG7 2UH, United Kingdom

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Related Publications (1)

  • Domachowske J, Madhi SA, Simoes EAF, Atanasova V, Cabanas F, Furuno K, Garcia-Garcia ML, Grantina I, Nguyen KA, Brooks D, Chang Y, Leach A, Takas T, Yuan Y, Griffin MP, Mankad VS, Villafana T; MEDLEY Study Group. Safety of Nirsevimab for RSV in Infants with Heart or Lung Disease or Prematurity. N Engl J Med. 2022 Mar 3;386(9):892-894. doi: 10.1056/NEJMc2112186. No abstract available.

Related Links

MeSH Terms

Conditions

Respiratory Syncytial Virus Infections

Interventions

Palivizumab

Condition Hierarchy (Ancestors)

Pneumovirus InfectionsParamyxoviridae InfectionsMononegavirales InfectionsRNA Virus InfectionsVirus DiseasesInfections

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 21, 2019

First Posted

May 22, 2019

Study Start

July 30, 2019

Primary Completion

May 3, 2021

Study Completion

January 20, 2023

Last Updated

September 21, 2023

Results First Posted

September 21, 2023

Record last verified: 2023-09

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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