NCT03953079

Brief Summary

Phase 2b, multicenter, visual examiner-masked, randomized active-controlled, parallel-arm design study to evaluate the safety and duration of repeated IVT injections of 3 dose levels of GB-102 compared with aflibercept.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
56

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Sep 2019

Geographic Reach
1 country

33 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 13, 2019

Completed
3 days until next milestone

First Posted

Study publicly available on registry

May 16, 2019

Completed
4 months until next milestone

Study Start

First participant enrolled

September 26, 2019

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 15, 2020

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 3, 2021

Completed
7 months until next milestone

Results Posted

Study results publicly available

January 11, 2022

Completed
Last Updated

January 19, 2022

Status Verified

January 1, 2022

Enrollment Period

1.2 years

First QC Date

May 13, 2019

Results QC Date

December 14, 2021

Last Update Submit

January 10, 2022

Conditions

Keywords

Age-related macular degeneration (AMD)Choroidal neovascularization

Outcome Measures

Primary Outcomes (1)

  • Time to First Rescue Treatment

    Kaplan-Meier estimate of the median time to first rescue treatment.

    Baseline through 12 months

Secondary Outcomes (8)

  • Time to Fulfillment of at Least One Rescue Criterion

    6 months through 12 months

  • Number of Times That at Least One Rescue Criterion is Met

    Baseline through 12 months

  • Number of Treatments, Including Both Rescue and Scheduled Study Treatments, During the Study

    Baseline through 12 months

  • Change From Baseline in Best-corrected Visual Acuity (BCVA) (ETDRS Letter Score) at All Visits

    Baseline through 12 months

  • Categorical Change From Baseline in BCVA (ETDRS Letter Score) at All Visits

    Baseline through 12 months

  • +3 more secondary outcomes

Study Arms (3)

GB-102 1 mg/1 mg

EXPERIMENTAL

Participants will receive intravitreal (IVT) GB-102 1 mg in the study eye at Baseline and Month 6 and sham at Months 2, 4, 8 and 10.

Drug: Drug: GB-102

GB-102 2 mg/1 mg

EXPERIMENTAL

Participants will receive intravitreal (IVT) GB-102 2 mg in the study eye at Baseline, intravitreal (IVT) GB-102 1 mg at Month 6 and sham at Months 2, 4, 8 and 10.

Drug: Drug: GB-102

Aflibercept 2 mg

ACTIVE COMPARATOR

Participants will receive intravitreal (IVT) aflibercept 2 mg in the study eye at Baseline, Months 2, 4, 6, 8 and 10.

Drug: Aflibercept

Interventions

Intravitreal injection of GB-102

Also known as: Sunitinib malate
GB-102 1 mg/1 mgGB-102 2 mg/1 mg

Intravitreal injection of aflibercept (2 mg dose)

Also known as: Eylea
Aflibercept 2 mg

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males or females ≥ 50 years of age
  • Presence of a choroidal neovascularization (CNV) lesion secondary to AMD treated with at least 3 prior intravitreal (IVT) injections of an anti-vascular endothelial growth factor (VEGF) agent (aflibercept, bevacizumab, or ranibizumab).
  • Demonstrated response to prior anti-VEGF treatment since diagnosis
  • Best-corrected visual acuity (BCVA) of 35 letters or better

You may not qualify if:

  • History, within 6 months prior to screening, of any of the following: myocardial infarction, any cardiac event requiring hospitalization, treatment for acute congestive heart failure, transient ischemic attack, or stroke
  • Uncontrolled hypertension, diabetes mellitus or intraocular pressure (IOP)
  • Chronic renal disease
  • Abnormal liver function
  • Women who are pregnant or lactating

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (33)

Retinal Consultants AZ

Gilbert, Arizona, 85296, United States

Location

Retinal Research Institute

Phoenix, Arizona, 85017, United States

Location

California Retina Research Consultants

Bakersfield, California, 93309, United States

Location

Retinal Diagnostic Center of Northern California

Campbell, California, 95008, United States

Location

The Retina Partners

Encino, California, 91436, United States

Location

Retina Consultants of Orange County

Fullerton, California, 92835, United States

Location

Northern California Retina Vitreous Associates Medical Group, Inc.

Mountain View, California, 94040, United States

Location

West Coast Retina Medical Group, Inc.

San Francisco, California, 94109, United States

Location

California Retina Consultants - CRC

Santa Barbara, California, 93103, United States

Location

Bay Area Retina Associates

Walnut Creek, California, 94598, United States

Location

Specialty Retina Center

Coral Springs, Florida, 32503, United States

Location

Florida Retina Institute

Orlando, Florida, 32806-1101, United States

Location

Retina Specialty Institute

Pensacola, Florida, 32503, United States

Location

Eye Associates of Pinellas

Pinellas Park, Florida, 33782, United States

Location

Southeast Retina Center

Augusta, Georgia, 30909, United States

Location

Retina Consultants of Hawaii

‘Aiea, Hawaii, 96701, United States

Location

University Retina and Macula

Lemont, Illinois, 60439, United States

Location

Wolfe Eye Clinic - West Des Moines

Des Moines, Iowa, 50266, United States

Location

Eye Associates of Northeast Louisiana

West Monroe, Louisiana, 71291, United States

Location

Cumberland Valley Retina Consultants

Hagerstown, Maryland, 21740, United States

Location

Mid Atlantic Retina Specialists

Hagerstown, Maryland, 21740, United States

Location

Sierra Eye Associates

Reno, Nevada, 89502, United States

Location

Ophthalmic Consultants of Long Island

Oceanside, New York, 11572, United States

Location

Sterling Research

Cincinnati, Ohio, 45219, United States

Location

Black Hills Regional Eye Institute

Rapid City, South Dakota, 57701, United States

Location

Retina Research Institute of Texas

Abilene, Texas, 79606, United States

Location

Austin Retina Associates

Austin, Texas, 78705, United States

Location

Retina Research Center, PLLC

Austin, Texas, 78705, United States

Location

Retina Specialists

Plano, Texas, 75093, United States

Location

Retina Consultants of Houston

The Woodlands, Texas, 77384, United States

Location

Strategic Clinical Research Group LLC

Willow Park, Texas, 76087, United States

Location

Piedmont Eye Center

Lynchburg, Virginia, 24502, United States

Location

Retina Center NW PLLC

Silverdale, Washington, 98383, United States

Location

MeSH Terms

Conditions

Macular DegenerationChoroidal Neovascularization

Interventions

Sunitinibaflibercept

Condition Hierarchy (Ancestors)

Retinal DegenerationRetinal DiseasesEye DiseasesChoroid DiseasesUveal DiseasesNeovascularization, PathologicMetaplasiaPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-Ring

Limitations and Caveats

Small sample size hinders the ability to compare groups statistically.

Results Point of Contact

Title
Executive Director, Biostatistics
Organization
Graybug Vision

Study Officials

  • Chief Medical Officer

    Graybug Vision, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Masking Details
Visual examiner-masked
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Parallel-arm design
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 13, 2019

First Posted

May 16, 2019

Study Start

September 26, 2019

Primary Completion

December 15, 2020

Study Completion

June 3, 2021

Last Updated

January 19, 2022

Results First Posted

January 11, 2022

Record last verified: 2022-01

Locations