NCT03787758

Brief Summary

This study is a phase 1, double-blind, placebo-controlled, multiple ascending dose study to determine the safety, tolerability, and pharmacokinetics of SAGE-718 oral solution in healthy adults (Part A) with an open-label cohort of patients with Huntington's disease (Part B)

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
6

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Feb 2019

Shorter than P25 for phase_1

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 17, 2018

Completed
9 days until next milestone

First Posted

Study publicly available on registry

December 26, 2018

Completed
2 months until next milestone

Study Start

First participant enrolled

February 28, 2019

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 7, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 7, 2019

Completed
Last Updated

September 17, 2025

Status Verified

January 1, 2022

Enrollment Period

7 months

First QC Date

December 17, 2018

Last Update Submit

September 11, 2025

Conditions

Outcome Measures

Primary Outcomes (5)

  • Number of Participants with the Incidence of Adverse Events and Serious Adverse Events.

    21 Days

  • Percentage of participants with change from baseline in vital signs.

    21 Days

  • Change from baseline in electrocardiograms (ECGs) including PR interval, QT interval, QTc interval, QTcF, and rhythm abnormalities

    21 Days

  • Percentage of participants with change from baseline in clinical laboratory parameters.

    21 Days

  • Change from baseline in Columbia-Suicide Severity Rating Scale (C-SSRS).

    21 Days

Secondary Outcomes (3)

  • PK profile of SAGE-718 following administration of multiple doses of SAGE-718 Oral Solution as assessed by area under the curve [AUC].

    17 Days

  • PK profile of SAGE-718 following administration of multiple doses of SAGE-718 Oral Solution as assessed by maximum observed concentration [Cmax].

    17 Days

  • PK profile of SAGE-718 following administration of multiple doses of SAGE-718 Oral Solution as assessed by time of occurrence of Cmax [tmax].

    17 Days

Study Arms (1)

SAGE-718

EXPERIMENTAL
Drug: SAGE-718

Interventions

SAGE-718

SAGE-718

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject is positive for mutant HTT (documented CAG repeats ≥ 40 units).
  • Subject has a body weight ≥50 kg and body mass index ≥18.0 and ≤30.0 kg/m2 at screening.

You may not qualify if:

  • Subject has any clinically significant abnormal finding on the physical exam at screening or admission.
  • Subject has a history or presence of a neurologic disease or condition (other than Huntington's disease), including but not limited to severe chorea, epilepsy, closed head trauma with clinically significant sequelae, or a prior seizure.
  • Subject has a family history of epilepsy.
  • Subject has a positive screening test for alcohol or drugs of abuse (including marijuana) at screening or admission.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Sage Investigational Site

Long Beach, California, 90806, United States

Location

Sage Investigational Site

Marlton, New Jersey, 08053, United States

Location

Related Publications (1)

  • Koenig A, Lewis M, Wald J, Li S, Varoglu M, Dai J, Sankoh A, Paumier K, Doherty J, Quirk M. Dalzanemdor (SAGE-718), a novel, investigational N-methyl-D-aspartate receptor positive allosteric modulator: Safety, tolerability, and clinical pharmacology in randomized dose-finding studies in healthy participants and an open-label study in participants with Huntington's disease. Clin Transl Sci. 2024 Jul;17(7):e13852. doi: 10.1111/cts.13852.

MeSH Terms

Conditions

Huntington Disease

Condition Hierarchy (Ancestors)

Basal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesDementiaChoreaDyskinesiasMovement DisordersHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCognition DisordersNeurocognitive DisordersMental Disorders

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 17, 2018

First Posted

December 26, 2018

Study Start

February 28, 2019

Primary Completion

October 7, 2019

Study Completion

October 7, 2019

Last Updated

September 17, 2025

Record last verified: 2022-01

Data Sharing

IPD Sharing
Will not share

Data sharing will be consistent with the results submission policy of ClinicalTrials.gov.

Locations