NCT00514774

Brief Summary

The purpose of this study is to evaluate the safety of the drug ursodiol (ursodeoxycholic acid, UDCA) in people with Huntington's disease (HD) and to explore how the compound is processed by the body.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
21

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Aug 2007

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2007

Completed
7 days until next milestone

First Submitted

Initial submission to the registry

August 8, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 10, 2007

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2009

Completed
Last Updated

February 5, 2009

Status Verified

February 1, 2009

Enrollment Period

1.8 years

First QC Date

August 8, 2007

Last Update Submit

February 4, 2009

Conditions

Keywords

Huntington choreachoreahereditarytauroursodeoxycholic acidursodeoxycholic acidTUDCAUDCA

Outcome Measures

Primary Outcomes (3)

  • Safety measures (complete blood count, chemistry profile, electrocardiogram, urinalysis)

    35 days

  • Tolerability measures (adverse event severity)

    35 days

  • Pharmacokinetic measures (Serum and CSF levels of bile acids)

    28 days

Study Arms (3)

A

EXPERIMENTAL
Drug: ursodiol

B

EXPERIMENTAL
Drug: ursodiol

C

PLACEBO COMPARATOR
Drug: placebo

Interventions

ursodiol 300 mg twice daily for study days 0 through 28 ursodiol 600mg twice daily on study days 0 through 28

Also known as: Ursodeoxycholic acid, UDCA
AB

placebo 600mg twice daily for study days 0 through 28

C

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • All subjects will be age 18 or older
  • All subjects will have manifest Huntington disease determined by clinical exam plus either documented prior DNA testing for the HD gene or a documented family history of the disease

You may not qualify if:

  • Subjects taking oral contraceptives, cholestyramine, colestipol, or aluminum-based antacids will be excluded
  • Subjects with known allergy or other contraindication to the study drug will be excluded
  • Subjects with bleeding diathesis, or on coumadin or mandatory aspirin will be excluded
  • Subjects with unstable medical or psychiatric illness will be excluded
  • Subjects with clinically significant lab / EKG abnormalities at screening will be excluded
  • Subjects who are currently pregnant or breastfeeding will be excluded

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

Related Publications (2)

  • Keene CD, Rodrigues CM, Eich T, Chhabra MS, Steer CJ, Low WC. Tauroursodeoxycholic acid, a bile acid, is neuroprotective in a transgenic animal model of Huntington's disease. Proc Natl Acad Sci U S A. 2002 Aug 6;99(16):10671-6. doi: 10.1073/pnas.162362299. Epub 2002 Jul 29.

    PMID: 12149470BACKGROUND
  • Keene CD, Rodrigues CM, Eich T, Linehan-Stieers C, Abt A, Kren BT, Steer CJ, Low WC. A bile acid protects against motor and cognitive deficits and reduces striatal degeneration in the 3-nitropropionic acid model of Huntington's disease. Exp Neurol. 2001 Oct;171(2):351-60. doi: 10.1006/exnr.2001.7755.

    PMID: 11573988BACKGROUND

Related Links

MeSH Terms

Conditions

Huntington DiseaseChorea

Interventions

Ursodeoxycholic Acid

Condition Hierarchy (Ancestors)

Basal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesDementiaDyskinesiasMovement DisordersHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCognition DisordersNeurocognitive DisordersMental DisordersNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Deoxycholic AcidCholic AcidsBile Acids and SaltsSteroidsFused-Ring CompoundsPolycyclic CompoundsCholanes

Study Officials

  • Penelope Hogarth, M.D.

    Oregon Health and Science University

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER

Study Record Dates

First Submitted

August 8, 2007

First Posted

August 10, 2007

Study Start

August 1, 2007

Primary Completion

June 1, 2009

Study Completion

June 1, 2009

Last Updated

February 5, 2009

Record last verified: 2009-02

Locations