NCT03768505

Brief Summary

This is the study of the PI3Kδ inhibitor Zandelisib (ME-401) in subjects with relapsed/refractory follicular lymphoma or marginal zone lymphoma after failure of at least 2 prior lines of systemic therapy

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
169

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jun 2019

Typical duration for phase_2

Geographic Reach
13 countries

112 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 4, 2018

Completed
3 days until next milestone

First Posted

Study publicly available on registry

December 7, 2018

Completed
7 months until next milestone

Study Start

First participant enrolled

June 25, 2019

Completed
3.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 24, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 24, 2023

Completed
10 months until next milestone

Results Posted

Study results publicly available

February 1, 2024

Completed
Last Updated

December 31, 2024

Status Verified

December 1, 2022

Enrollment Period

3.7 years

First QC Date

December 4, 2018

Results QC Date

December 5, 2023

Last Update Submit

December 29, 2024

Conditions

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate (ORR) of ME-401 in Relapsed or Refractory FL or MZL

    ORR is measured as the proportion of subjects achieving the best response rating of CR or PR prior to first PD

    3 years 9 months

Secondary Outcomes (6)

  • Duration of Response (DOR)

    3 years 9 months

  • Complete Response (CR) Rate

    3 years 9 months

  • Progression-free Survival (PFS)

    3 years 9 months

  • Overall Survival

    2 years

  • Overall Incidence of Treatment Emergent Adverse Events (TEAEs)

    3 years 9 months

  • +1 more secondary outcomes

Study Arms (1)

Zandelisib (ME-401) open label

EXPERIMENTAL

Subjects with relapsed/refractory FL or MZL will be administered 60 mg of ME-401 orally, once a day on an intermittent schedule (IS).

Drug: Zandelisib (ME-401)

Interventions

Zandelisib (ME-401) 60 mg

Zandelisib (ME-401) open label

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed diagnosis as defined in the World Health Organization (WHO) classification scheme
  • Follicular Lymphoma (FL) limited to Grade 1,2 or 3a or
  • Marginal Zone Lymphoma (MZL) including nodal, extranodal and splenic MZL
  • Subjects that have had progression of disease or had no response to therapy after at least 2 prior systemic therapies for FL or MZL
  • Age ≥ 18
  • At least one bi-dimensionally measurable nodal lesion \> 1.5 cm in its longest diameter by computed tomography (CT) scan as defined by the Lugano Classification
  • Adequate hematologic, renal and hepatic parameters at screening unless abnormal values are due to FL per Investigator assessment
  • QT-interval corrected according to Fridericia's formula (QTcF) ≤ 450 milliseconds (msec);
  • Left ventricular ejection fraction (LVEF) ≥ 45%

You may not qualify if:

  • Histologically confirmed FL Grade 3b transformation from FL to an aggressive lymphoma
  • Known lymphomatous involvement of the central nervous system
  • Uncontrolled clinically significant illness
  • Ongoing or history of drug-induced pneumonitis
  • History of clinically significant cardiovascular abnormalities
  • History of clinically significant GI conditions
  • Known history of, or active HIV infection

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (115)

Oncology Institute of Hope and Innovation

Tucson, Arizona, 85710, United States

Location

Pacific Cancer Medical Center, Inc.

Anaheim, California, 92801, United States

Location

Tower Hematology Oncology

Beverly Hills, California, 90211, United States

Location

The Oncology Institute of Hope and Innovation

Downey, California, 90241, United States

Location

Sharp Memorial Hospital

San Diego, California, 92123, United States

Location

H. Lee Moffit Cancer Center

Tampa, Florida, 33612, United States

Location

Cleveland Clinic-Florida

Weston, Florida, 333331, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Advocate Health & Hospitals Corporation

Niles, Illinois, 61761, United States

Location

Investigative Clinical Research of Indiana LLC

Indianapolis, Indiana, 46260, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

University of Michigan Medical School

Ann Arbor, Michigan, 48109, United States

Location

St. Vincent Frontier Cancer Center

Billings, Montana, 59102, United States

Location

The Oncology Institute of Hope and Innovation

Henderson, Nevada, 89052, United States

Location

Memorial Sloan Kettering

Basking Ridge, New Jersey, 07920, United States

Location

Memorial Sloan Kettering

Middletown, New Jersey, 07748, United States

Location

Memorial Sloan Kettering

Montvale, New Jersey, 07645, United States

Location

San Juan Oncology

Farmington, New Mexico, 87401, United States

Location

Memorial Sloan Kettering

Commack, New York, 11725, United States

Location

Memorial Sloan Kettering

Harrison, New York, 10604, United States

Location

Clinical Research Alliance

Lake Success, New York, 11042, United States

Location

Memorial Sloan Kettering

New York, New York, 10065, United States

Location

Stony Brook University

Stony Brook, New York, 11794, United States

Location

Memorial Sloan Kettering

Uniondale, New York, 11553, United States

Location

Duke Cancer Center

Durham, North Carolina, 27710, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Vanderbilt University

Nashville, Tennessee, 37203, United States

Location

Renovatio Clinical

Houston, Texas, 77056, United States

Location

Swedish Cancer Institute

Edmonds, Washington, 98026, United States

Location

Swedish Cancer Institute

Seattle, Washington, 98104, United States

Location

Medical Oncology Associates PS

Spokane, Washington, 99208, United States

Location

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, 53705, United States

Location

Marshfield Medical Center

Marshfield, Wisconsin, 54449, United States

Location

Peninsula and South Eastern Haematology and Oncology Group

Frankston, Victoria, 3199, Australia

Location

The Perth Blood Institute

West Perth, Western Australia, 6005, Australia

Location

Liverpool Hospital

Sydney, NSW2170, Australia

Location

Kepler Universitatsklinikum GmBH

Linz, 4021, Austria

Location

Medical University of Vienna

Vienna, 1160, Austria

Location

AZ Sint-Jan Brugge-Oostende

Bruges, 8000, Belgium

Location

Institut Jules Bordet

Brussels, 1000, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Antwerp University Hospital

Edegem, 2650, Belgium

Location

C H de la Cote Basque, Service d'Hematologie

Bayonne, 64100, France

Location

CHD Vendee, Onco-hematologie

La Roche-sur-Yon, 85925, France

Location

Centre Hospitalier du Mans

Le Mans, F720000, France

Location

Centre Hospitalier de Mulhouse

Mulhouse, 68100, France

Location

Centre Hospitalier Universitaire (CHU) de Poitiers - Hôpital de la Miletrie

Poitiers, 86021, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Klinikum Mutterhaus Feldstr

Trier, Rhineland-Palatinate, Germany

Location

Hamatologisch-Onkolgische Praxis

Nordheim, Stolberg, 52222, Germany

Location

Universitatsklinikum Halle

Halle, 06120, Germany

Location

Munich Municipal Hospital

Munich, 80804, Germany

Location

Universitatsklinikum Munster

Münster, 48149, Germany

Location

Universitatsklinikum Ulm

Ulm, 89081, Germany

Location

Centro di Riferimento Oncologico di Aviano (CRO) IRCCS

Aviano, 33081, Italy

Location

Policlinico Sant'Orsola Malpighi

Bologna, 40138, Italy

Location

IRCCS AOU Policlinico San Martino

Genova, 16132, Italy

Location

Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori I.R.S.T.

Meldola, 47014, Italy

Location

UOC Oncoematologia

Napoli, 80131, Italy

Location

Ospedale Santa Maria delle Croci

Ravenna, 48121, Italy

Location

Infermi Hospital Rimini

Rimini, 47923, Italy

Location

Universita Cattolica del Sacro Cuore

Roma, 00168, Italy

Location

IRCCS Regina Elena National Cancer Institute

Rome, 00144, Italy

Location

Azienda Ospedaliera Santa Maria

Terni, 05100, Italy

Location

Ospedale DellAngelo Di Mestre Umberto I

Venice, 30174, Italy

Location

North Shore Hospital

Auckland, 0622, New Zealand

Location

Southern District Hospital

Dunedin, 9054, New Zealand

Location

Szpital Uniwersytecki nr 2 im.

Bydgoszcz, 85-168, Poland

Location

Pratia MCM Krakow

Krakow, 30-510, Poland

Location

ojewodzkie Wielospecjalistyczne Centrum

Lodz, 93-510, Poland

Location

Primary Specialty Oncology

Warsaw, 02-034, Poland

Location

Instytut Hematologii i Transfuzjologii

Warsaw, 02-776, Poland

Location

Dolnoslaskie Centrum Transplantacji Komorkowych z Krajowym Bankiem Dawcow Szpiku

Wroclaw, 53-439, Poland

Location

Dong-A University Hospital

Busan, 49201, South Korea

Location

Pusan National University Hospital

Busan, 49241, South Korea

Location

Korea University Anam Hospital

Seoul, 02841, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Ewha Womans University Mokdong Hospital

Seoul, 07985, South Korea

Location

The Catholic University of Korea-Seoul St. Marys Hospital

Seoul, 6591, South Korea

Location

Ulsan University Hospital

Ulsan, 44033, South Korea

Location

Hospital Universitario de Canarias

San Cristóbal de La Laguna, Tenerife, 38320, Spain

Location

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Universitari Mutua Terrasa

Barcelona, 08221, Spain

Location

ICO-Hospital Duran i Reynals

Barcelona, 08908, Spain

Location

MD Anderson Cancer Center

Madrid, 28033, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, 28034, Spain

Location

Fundacion Jimenez Diaz

Madrid, 28040, Spain

Location

Hospital Universitario Quiron Salud Madrid

Madrid, 28223, Spain

Location

Complejo Hospitalario de Navarra

Pamplona, 31008, Spain

Location

Hospital Clinico de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario Virgen Macarena

Seville, 41009, Spain

Location

Hospital Virgen del Rocio

Seville, 41013, Spain

Location

Miguel Servet Hospital

Zaragoza, 50009, Spain

Location

Ente Ospedaliero Cantonale (EOC)

Bellinzona, 6500, Switzerland

Location

China Medical University Hospital

Taichung, 40447, Taiwan

Location

National Cheng Kung University Hospital

Tainan, 70403, Taiwan

Location

Chi-Mei Medical Center, Liouying

Tainan, 736, Taiwan

Location

National Taiwan University Hospital NTUH

Taipei, 10002, Taiwan

Location

North Wales Cancer Treatment Centre, Glan Clwyd Hospital

Rhyl, Denbighire, LL185UJ, United Kingdom

Location

Royal Marsden Hospital

London, Sutton, SM25PT, United Kingdom

Location

Nottingham University Hospital

Nottingham, UK, NG51PB, United Kingdom

Location

Belfast Health and Social Care Trust - Belfast City Hospital

Belfast, 28040, United Kingdom

Location

Royal Cornwall Hospital

Cornwell, TR1 3LJ, United Kingdom

Location

e Clatterbridge Cancer Centre

Liverpool, L78XP, United Kingdom

Location

Royal Liverpool University Hospital

Liverpool, L78XP, United Kingdom

Location

Lewisham and Greenwich University Hospital Lewisham

London, SE136LH, United Kingdom

Location

St George's Hospital

London, SW170QT, United Kingdom

Location

Centre for Haematology, Imperial College London

London, W12ONN, United Kingdom

Location

The Christie NHS Foundation Trust

Manchester, M20, United Kingdom

Location

Norfolk and Norwich University Hospital NHS Foundation Trust

Norwich, NR4 7UY, United Kingdom

Location

Oxford University Hospitals

Oxford, 0X46LB, United Kingdom

Location

Royal Hallamshire Hospital

Sheffield, S102JF, United Kingdom

Location

MeSH Terms

Conditions

Lymphoma, FollicularLymphoma, Non-HodgkinLymphoma, B-Cell, Marginal Zone

Interventions

ME-401

Condition Hierarchy (Ancestors)

LymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesLymphoma, B-Cell

Limitations and Caveats

The study was closed prematurely for business reasons.

Results Point of Contact

Title
Richard Ghalie, MD CMO
Organization
MEI Pharma

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Model Details: Treatment with Zandelisib (ME-401) (60 mg) given orally once a day on an intermittent schedule
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 4, 2018

First Posted

December 7, 2018

Study Start

June 25, 2019

Primary Completion

March 24, 2023

Study Completion

March 24, 2023

Last Updated

December 31, 2024

Results First Posted

February 1, 2024

Record last verified: 2022-12

Data Sharing

IPD Sharing
Will not share

Locations