NCT03749447

Brief Summary

This extended access study will assess the long-term safety and tolerability of bardoxolone methyl in qualified patients with chronic kidney disease (CKD) who previously participated in one of the qualifying clinical studies with bardoxolone methyl. Patients will remain in the study until bardoxolone methyl is available through commercial channels or until patient withdrawal, whichever is sooner.

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
270

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Mar 2019

Typical duration for phase_3

Geographic Reach
6 countries

87 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 19, 2018

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 21, 2018

Completed
4 months until next milestone

Study Start

First participant enrolled

March 8, 2019

Completed
4.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 23, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 23, 2023

Completed
7 months until next milestone

Results Posted

Study results publicly available

March 19, 2024

Completed
Last Updated

June 3, 2025

Status Verified

May 1, 2025

Enrollment Period

4.5 years

First QC Date

November 19, 2018

Results QC Date

February 20, 2024

Last Update Submit

May 22, 2025

Conditions

Keywords

Bardoxolone methylCDDO-MERTA 402Alport SyndromeAutosomal Dominant Polycystic KidneyADPKD

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Treatment-emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)

    An AE is any untoward medical occurrence in a participant administered a pharmaceutical product that does not necessarily have a causal relationship with this treatment. An SAE is any untoward medical occurrence that at any dose results in death, places the participant at immediate risk of death, requires inpatient hospitalization or prolongation of existing hospitalization, results in persistent or significant disability/incapacity, results in a congenital anomaly/birth defect, or is a medically important event. AEs and SAEs that occurred within 30 days after the last dose were considered treatment-emergent. The study follow-up assessment was collected within 14 to 35 days after the last dose.

    From the first dose of the study drug (baseline) up to the end of the study follow-up (up to 4.2 years)

Study Arms (1)

Bardoxolone methyl

EXPERIMENTAL

Adult participants received bardoxolone methyl capsules, once daily (QD) at a starting dose of 5 milligrams (mg), followed by dose- escalation to 10 mg at Week 2 (Day 14 ± 3), and to 20 mg at Week 4 (Day 28 ± 3). Based on the eligibility UACR \>300 milligrams per gram (mg/g), the dose was increased to 30 mg starting from Week 6 (Day 42 ± 3) until the end of the study. Participants under 18 years of age received bardoxolone methyl capsules at a starting dose of 5 mg every other day during the first week and QD during the second week of the study, followed by dose-escalation to 10 mg at Week 2 and to 20 mg at Week 4. Based on the eligibility UACR \>300 mg/g, the dose was increased to 30 mg starting from Week 6 until the end of the study.

Drug: Bardoxolone methyl

Interventions

Bardoxolone methyl capsules

Also known as: RTA 402
Bardoxolone methyl

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Patients who are participating (or who have participated) in qualifying studies and who have not been required to discontinue study treatment for protocol or safety reasons and who have completed required End-of-Treatment and/or Follow-up visits in a prior clinical study with bardoxolone methyl and who, according to the assessment of the investigator, have a potential positive benefit-risk assessment for participating in the trial.
  • Meets the following eligibility criteria based on assessments from the prior qualifying study (last on-treatment visit) or from a screening visit, if applicable:
  • Not expected to reach end stage kidney disease (ESKD) or nephrotic syndrome within 12 weeks of study enrollment, in the investigator's judgement; subjects with eGFR \<20 ml/min/1.73m2 should be discussed with the medical monitor before enrollment (e.g., such subjects with an average rate of eGFR decline \> 1.0 ml/min/1.73m2 per month in the 3 months prior to eligibility assessment may not be eligible);
  • BNP \< 200 pg/mL at the last on-treatment visit in the prior qualifying study or at a new screening visit, if applicable;
  • No occurrence of a cardiovascular serious adverse event in the prior qualifying study or in the interval between the end of the qualifying study and the screening visit, if applicable.
  • Willing and able to comply with scheduled visits, treatment plan, laboratory tests, and other study procedures.
  • Evidence of a personally signed and dated informed consent document (and assent form if necessary) indicating that the patient (or a legally acceptable representative) has been informed of all pertinent aspects of the study prior to initiation of any protocol-mandated procedures.

You may not qualify if:

  • Participation in other investigational clinical studies involving interventional products being tested or used in a way different from the approved form or when used for an unapproved indication;
  • Patients who have an ongoing SAE from a clinical study that is assessed by the investigator as related to bardoxolone methyl;
  • Unwilling to practice acceptable methods of birth control (both males who have partners of childbearing potential and females of childbearing potential) while screening, taking study drug and 30 days after the last study drug dose;
  • Women who are pregnant or breastfeeding;
  • Patient is, in the opinion of the investigator, unable to comply with the requirements of the study protocol or is unsuitable for the study for any reason;
  • Known hypersensitivity to any component of the study drug.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (87)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Apogee Clinical Research

Huntsville, Alabama, 35805, United States

Location

Arizona Kidney Disease and Hypertension Research Services, PLLC

Glendale, Arizona, 85306, United States

Location

Centricity Research Phoenix Multispecialty

Mesa, Arizona, 85206, United States

Location

California Institute Renal Research

La Mesa, California, 91942, United States

Location

Academic Medical Research Institute

Los Angeles, California, 90022, United States

Location

David Geffen School of Medicine at UCLA

Los Angeles, California, 90095, United States

Location

Apex Research of Riverside

Riverside, California, 92505, United States

Location

Rady Children's Hospital - San Diego

San Diego, California, 92123, United States

Location

University of California San Francisco - Children's Renal Center

San Francisco, California, 94143, United States

Location

University of California, San Francisco

San Francisco, California, 94143, United States

Location

Western Nephrology

Arvada, Colorado, 80002, United States

Location

University of Colorado Anschutz Medical Center

Aurora, Colorado, 80045, United States

Location

Colorado Kidney Care, PC

Denver, Colorado, 80230, United States

Location

South Florida Research Institute

Lauderdale Lakes, Florida, 33313, United States

Location

Innovation Medical Research, Inc.

Palmetto Bay, Florida, 33157, United States

Location

USF Health South Tampa Center

Tampa, Florida, 33606, United States

Location

Florida Premier Research Institute, LLC

Winter Park, Florida, 32789, United States

Location

Emory University School of Medicine

Atlanta, Georgia, 30322, United States

Location

Boise Kidney & Hypertension, PLLC

Caldwell, Idaho, 83605, United States

Location

Boise Kidney & Hypertension, PLLC

Meridian, Idaho, 83642, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Nephrology Research NorthShore University Health System

Evanston, Illinois, 60201, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66224, United States

Location

Renal Associates of Baton Rouge

Baton Rouge, Louisiana, 70808, United States

Location

Northwest Louisiana Nephrology

Shreveport, Louisiana, 71101, United States

Location

The Johns Hopkins University

Baltimore, Maryland, 21287, United States

Location

Tufts Medical Center - Division of Nephrology

Boston, Massachusetts, 02110, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Nephrology Center, PC

Kalamazoo, Michigan, 49007, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Children's Mercy Hospital and Clinics

Kansas City, Missouri, 64108, United States

Location

Clinical Research Consultants, LLC

Kansas City, Missouri, 64111, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

KSOSN

Las Vegas, Nevada, 89128, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Mountain Kidney & Hypertension Associates

Asheville, North Carolina, 28801, United States

Location

North Carolina Nephrology

Cary, North Carolina, 27511, United States

Location

Metrolina Nephrology Associates

Charlotte, North Carolina, 28208, United States

Location

Duke University Medical Center

Durham, North Carolina, 27701, United States

Location

Metrolina Nephrology Associates

Gastonia, North Carolina, 28054, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Remington-Davis Clinical Research

Columbus, Ohio, 43215, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Northeast Clinical Research Center

Bethlehem, Pennsylvania, 18017, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

UPMC Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, 15224, United States

Location

Columbia Nephrology Associates, PA

Columbia, South Carolina, 29203, United States

Location

South Carolina Nephrology & Hypertension Center, Inc

Orangeburg, South Carolina, 29118, United States

Location

Arlington Nephrology

Arlington, Texas, 76015, United States

Location

Research Management, Inc.

Austin, Texas, 78751, United States

Location

Renal Disease Research Institute

Dallas, Texas, 75204, United States

Location

DaVita Med Center

Houston, Texas, 77004, United States

Location

Southwest Houston Research

Houston, Texas, 77099, United States

Location

Clinical Advancement Center

San Antonio, Texas, 78215, United States

Location

University of Vermont Medical Center

Burlington, Vermont, 05401, United States

Location

Nephrology Associates of Northern Virginia, Inc.

Fairfax, Virginia, 22033, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Milwaukee Nephrologists, SC

Wauwatosa, Wisconsin, 53226, United States

Location

John Hunter Hospital

New Lambton, New South Wales, 2305, Australia

Location

Royal Brisbane and Women's Hospital

Herston, Queensland, 4029, Australia

Location

Melbourne Renal Research Group

Reservoir, Victoria, 3073, Australia

Location

The Royal Melbourne Hospital

Parkville, 3050, Australia

Location

Chu Grenoble Alpes

Grenoble, 38043, France

Location

Hopital Necker, Universite Paris Descartes

Paris, 75015, France

Location

Japanese Red Cross Nagoya Daini Hospital

Nagoya, Aichi-ken, 466-8650, Japan

Location

Hokkaido University Hospital

Sapporo, Hokkaido, 060-8648, Japan

Location

Kobe University Hospital

Kobe, Hyōgo, 650-0017, Japan

Location

Toranomon Hospital Kajigaya

Kawasaki, Kanagawa, 213-8587, Japan

Location

St Marianna University Hospital

Kawasaki, Kanagawa, 216-8511, Japan

Location

JCHO Sendai Hospital

Sendai, Miyagi, 981-3281, Japan

Location

Kitano Hospital

Osaka, Osaka, 530-8480, Japan

Location

Osaka University Hospital

Suita, Osaka, 565-8971, Japan

Location

Saga University Hospital

Saga, Saga-ken, 849-8501, Japan

Location

Saitama Children's Medical Center

Saitama-shi, Saitama, 330-8777, Japan

Location

Juntendo University Hospital

Bunkyō-Ku, Tokyo, 113-8431, Japan

Location

Jutendo University Hospital

Bunkyō-Ku, Tokyo, 113-8431, Japan

Location

Tokyo Metropolitan Children's Medical Center

Fuchū, Tokyo, 183-8561, Japan

Location

Toranomon Hospital

Minato-Ku, Tokyo, 105-8470, Japan

Location

Tokyo Women's Medical University Hospital

Shinjuku-Ku, Tokyo, 162-8666, Japan

Location

Niigata University Medical and Dental Hospital

Niigata, 951-8520, Japan

Location

Local Incorporated Administrative Agency Osaka City Hospital Organization Osaka City General Hospital

Osaka, 834-0021, Japan

Location

Puerto Rico Clinical and Translational Research Consortium (PRCTRC)

Rio Piedras, 00935, Puerto Rico

Location

Fundacio Puigvert

Barcelona, Catalonia, 08025, Spain

Location

Hospital Virgen de la Arrixaca

El Palmar, Murcia, 30120, Spain

Location

MeSH Terms

Conditions

Renal Insufficiency, ChronicNephritis, HereditaryPolycystic Kidney, Autosomal Dominant

Interventions

bardoxolone methyl

Condition Hierarchy (Ancestors)

Renal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsUrogenital AbnormalitiesNephritisCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCollagen DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesPolycystic Kidney DiseasesKidney Diseases, CysticAbnormalities, MultipleCiliopathiesGenetic Diseases, Inborn

Limitations and Caveats

Early termination of trial due to discontinuation of all bardoxolone chronic kidney disease programs.

Results Point of Contact

Title
US Biogen Clinical Trial Center
Organization
Biogen

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 19, 2018

First Posted

November 21, 2018

Study Start

March 8, 2019

Primary Completion

August 23, 2023

Study Completion

August 23, 2023

Last Updated

June 3, 2025

Results First Posted

March 19, 2024

Record last verified: 2025-05

Data Sharing

IPD Sharing
Will share

In accordance with Biogen's Clinical Trial Transparency and Data Sharing Policy on https://www.biogentrialtransparency.com/

More information

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