NCT03732534

Brief Summary

This is an open-label, rollover study to collect long-term safety, tolerability, and investigator- and participant-reported pharmacodynamic (PD) data after chronic administration of NBI-98854 in pediatric participants with Tourette Syndrome (TS), as well as to provide open-label access to NBI-98854 for the treatment of TS for pediatric participants who have taken part in a Phase 2 NBI-98854 study.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
6

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Oct 2018

Shorter than P25 for phase_2

Geographic Reach
2 countries

10 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 17, 2018

Completed
19 days until next milestone

First Submitted

Initial submission to the registry

November 5, 2018

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 6, 2018

Completed
3 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 18, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 18, 2019

Completed
3.2 years until next milestone

Results Posted

Study results publicly available

April 19, 2022

Completed
Last Updated

April 19, 2022

Status Verified

March 1, 2022

Enrollment Period

4 months

First QC Date

November 5, 2018

Results QC Date

January 29, 2022

Last Update Submit

March 25, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Treatment-Emergent Adverse Events (TEAEs)

    A TEAE is an adverse event not present prior to the initiation of study drug dosing, or is an already present event that worsens either in intensity or frequency following the initiation of study drug dosing.

    Up to 16 Weeks

Study Arms (1)

NBI-98854

EXPERIMENTAL

NBI-98854 administered once daily for up to 96 weeks

Drug: NBI-98854

Interventions

vesicular monoamine transporter 2 (VMAT2) inhibitor

Also known as: Valbenazine
NBI-98854

Eligibility Criteria

Age6 Years - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Have a clinical diagnosis of Tourette Syndrome (TS)
  • Have participated in the NBI-98854-TS2004 or NBI 98854-TS2005 Phase 2 studies
  • If using maintenance medication(s) for TS and/or TS spectrum diagnoses (e.g. obsessive-compulsive disorder \[OCD\], Attention-Deficit Hyperactivity Disorder \[ADHD\]), be on stable doses
  • Be in good general health
  • Subjects of childbearing potential who do not practice total abstinence must agree to use hormonal or two forms of nonhormonal contraception (dual contraception) consistently during the screening, treatment and follow-up periods of the study

You may not qualify if:

  • Have an active, clinically significant unstable medical condition within 1 month before screening
  • Have a known history of long QT syndrome or cardiac arrhythmia
  • Have a known history of neuroleptic malignant syndrome
  • Have a cancer diagnosis within 3 years prior to screening (some exceptions allowed)
  • Have an allergy, hypersensitivity, or intolerance to VMAT2 inhibitors
  • Have a blood loss ≥250 mL or donated blood within 56 days, or donated plasma within 7 days, before the start of the study
  • Have a known history of substance dependence, substance (drug) or alcohol abuse within 3 months before the start of the study
  • Have a significant risk of suicidal or violent behavior
  • Have received an investigational drug within 30 days before the start of the study or plan to use an investigational drug (other than NBI-98854) during the study
  • Are currently participating in another NBI-98854 clinical study
  • Are pregnant (for females)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

Neurocrine Clinical Site

Anaheim, California, 92805, United States

Location

Neurocrine Clinical Site

San Diego, California, 92108, United States

Location

Neurocrine Clinical Site

Gulf Breeze, Florida, 32561, United States

Location

Neurocrine Clinical Site

Hialeah, Florida, 33013, United States

Location

Neurocrine Clinical Site

Chicago, Illinois, 60634, United States

Location

Neurocrine Clinical Site

Naperville, Illinois, 60563, United States

Location

Neurocrine Clinical Site

Lincoln, Nebraska, 68526, United States

Location

Neurocrine Clinical Site

Dallas, Texas, 75243, United States

Location

Neurocrine Clinical Site

Houston, Texas, 77058, United States

Location

Neurocrine Clinical Site

San Juan, PR, 00926, Puerto Rico

Location

MeSH Terms

Conditions

Tourette Syndrome

Interventions

valbenazine

Condition Hierarchy (Ancestors)

Basal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTic DisordersMovement DisordersHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesNeurodevelopmental DisordersMental Disorders

Results Point of Contact

Title
Neurocrine Medical Information
Organization
Neurocrine Biosciences

Study Officials

  • Clinical Development Lead

    Neurocrine Biosciences

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 5, 2018

First Posted

November 6, 2018

Study Start

October 17, 2018

Primary Completion

February 18, 2019

Study Completion

February 18, 2019

Last Updated

April 19, 2022

Results First Posted

April 19, 2022

Record last verified: 2022-03

Data Sharing

IPD Sharing
Will not share

Locations