NCT03703076

Brief Summary

Post-authorisation non-interventional observational study of patients with Primary Biliary Cholangitis who started Ocaliva® treatment between October 1st, 2016 and December 31, 2017.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
150

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Apr 2018

Shorter than P25 for all trials

Geographic Reach
1 country

2 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 10, 2018

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

October 9, 2018

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 11, 2018

Completed
6 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2019

Completed
Last Updated

October 11, 2018

Status Verified

October 1, 2018

Enrollment Period

12 months

First QC Date

October 9, 2018

Last Update Submit

October 9, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Response to Ocaliva® after 12 months of treatment

    Response to Ocaliva® after 12 months of treatment as monotherapy or in combination, using the published Paris 2 response criteria

    12 month

Secondary Outcomes (1)

  • Response rate using the Paris 2 criteria at the end of the study

    18 month

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

1\. Patients with PBC treated between October 1st, 2016 and December 31, 2017 with Ocaliva® 5 mg or 10 mg according to the terms of Ocaliva® approved SmPC: in combination with ursodeoxycholic acid (UDCA) in adults with an inadequate response to UDCA or as monotherapy in adults unable to tolerate UDCA (over the age of 18 years at the time of treatment introduction).

You may qualify if:

  • Patients with PBC treated with Ocaliva® 5 mg or 10 mg according to the terms of Ocaliva® approved SmPC: in combination with ursodeoxycholic acid (UDCA) in adults with an inadequate response to UDCA or as monotherapy in adults unable to tolerate UDCA (over the age of 18 years at the time of treatment introduction).
  • Patients with PBC with a suboptimal response to UDCA who received at least one dose of Ocaliva®.
  • Patients with or without an overlap syndrome (Nguyen-Khac E, 2004)
  • The patient (or his or her legal representative or designated healthcare proxy) must have read the information sheet and agreed verbally to take part, and must show the sheet to any doctor who is consulted.

You may not qualify if:

  • Diseases triggering a non-hepatic elevation of alkaline phosphatases (ALP) (for example Paget's disease or fractures within the previous three months).
  • Participation in another investigational study on a product, biological material or medical device within the 30 days prior to selection.
  • Inability to comply with the study follow-up procedures.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Chu Grenoble

Grenoble, 38700, France

RECRUITING

Hopital Saint Antoine

Paris, 75571, France

RECRUITING

MeSH Terms

Conditions

Liver Cirrhosis, Biliary

Condition Hierarchy (Ancestors)

Cholestasis, IntrahepaticCholestasisBile Duct DiseasesBiliary Tract DiseasesDigestive System DiseasesLiver DiseasesLiver CirrhosisFibrosisPathologic ProcessesPathological Conditions, Signs and Symptoms

Central Study Contacts

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR INVESTIGATOR
PI Title
CRO Project manager

Study Record Dates

First Submitted

October 9, 2018

First Posted

October 11, 2018

Study Start

April 10, 2018

Primary Completion

April 1, 2019

Study Completion

April 1, 2019

Last Updated

October 11, 2018

Record last verified: 2018-10

Locations