NCT03742973

Brief Summary

This study evaluates the safety and efficacy of baricitinib in participants with primary biliary cholangitis (PBC) who do not respond or are unable to take ursodeoxycholic acid (UDCA).

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Mar 2019

Shorter than P25 for phase_2

Geographic Reach
2 countries

12 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 14, 2018

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 15, 2018

Completed
4 months until next milestone

Study Start

First participant enrolled

March 28, 2019

Completed
6 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 26, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 26, 2019

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

October 14, 2020

Completed
Last Updated

October 14, 2020

Status Verified

October 1, 2019

Enrollment Period

6 months

First QC Date

November 14, 2018

Results QC Date

September 18, 2020

Last Update Submit

September 18, 2020

Conditions

Keywords

Janus kinase inhibitorJAK

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Alkaline Phosphatase (ALP)

    Change from baseline in Alkaline Phosphatase (ALP)

    Baseline, Week 12

Secondary Outcomes (3)

  • Percentage of Participants With Alkaline Phosphatase (ALP) <1.67 x Upper Limit of Normal (ULN) (and at Least 15% Decrease From Baseline) and Total Bilirubin Level Less Than ULN

    Week 12

  • Change From Baseline in Itch Numeric Rating Scale (NRS)

    Baseline, Week 12

  • Change From Baseline in Fatigue NRS

    Baseline, Week 12

Study Arms (4)

Baricitinib Cohort A

EXPERIMENTAL

Participants received 2 milligram (mg) of Baricitinib tablet orally once a day for 12 weeks. Cohort A is not reported due to protection of personal identifiable information based on enrollment futility.

Drug: Baricitinib

Placebo Cohort A

PLACEBO COMPARATOR

Participants received placebo orally once a day for 12 weeks. Cohort A is not reported due to protection of personal identifiable information based on enrollment futility.

Drug: Placebo

Baricitinib Cohort B

EXPERIMENTAL

Participants received 4 mg of Baricitinib orally once a day for 12 weeks. Cohort B was planned, but due to enrollment futility, the strategic decision was made to terminate the study.

Drug: Baricitinib

Placebo Cohort B

PLACEBO COMPARATOR

Placebo administered orally. Cohort B was planned, but due enrollment futility, the strategic decision was made to terminate the study.

Drug: Placebo

Interventions

Administered orally.

Also known as: LY3009104
Baricitinib Cohort ABaricitinib Cohort B

Administered orally.

Placebo Cohort APlacebo Cohort B

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have a diagnosis of PBC (consistent with American Association for the Study of Liver Disease (AASLD) and European Association for Study of the Liver (EASL) Practice Guidelines; as demonstrated by the presence of at least 2 of the following 3 diagnostic factors:
  • History of elevated Alkaline Phosphatase (ALP) levels for at least 6 months
  • Positive antimitochondrial antibodies titer
  • Liver biopsy consistent with PBC
  • Have ALP ≥1.67 x ULN but ≤6 x Upper Limit Normal (ULN).
  • Taking UDCA for at least 52 weeks (stable dose for at least 12 weeks) prior to Week 0, or have previously taken, but are intolerant (in the opinion of the investigator) to UDCA and have not received UDCA for at least 12 weeks prior to Week 0.
  • Nonpregnant, nonbreastfeeding female participants of childbearing potential.

You may not qualify if:

  • History or presence of other concomitant liver diseases including:
  • Hepatitis C virus (HCV) infection
  • Hepatitis B virus (HBV) infection
  • Primary sclerosing cholangitis
  • Alcoholic liver disease
  • Autoimmune liver disease other than PBC, such as overlap hepatitis
  • Nonalcoholic steatohepatitis
  • Gilbert's syndrome
  • Presence of clinical complications of PBC or clinically significant hepatic decompensation, including:
  • Liver transplantation, current placement on a liver transplant list or current Model for End Stage Liver Disease (MELD) score ≥15
  • Portal hypertension with complications, including known gastric or esophageal varices, ascites, history of variceal bleeds or related therapeutic or prophylactic interventions (e.g., beta blockers, insertion of variceal bands or transjugular intrahepatic portosystemic shunt), or hepatic encephalopathy
  • Cirrhosis, including history or presence of one or more of the following:
  • spontaneous bacterial peritonitis
  • hepatocellular carcinoma
  • Hepatorenal syndrome (type I or II)
  • +27 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

Southern California GI and Liver Centers (SCLC)

Coronado, California, 92118, United States

Location

University of California, Davis - Health Systems

Sacramento, California, 95817, United States

Location

University of Colorado School of Medicine

Aurora, Colorado, 80045, United States

Location

Schiff Center for Liver Diseases/University of Miami

Miami, Florida, 33136, United States

Location

The Institute for Digestive Health and Liver Disease at Mercy

Baltimore, Maryland, 21202, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

NYU Langone

New York, New York, 10016, United States

Location

UH Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Klinical Investigations Group, LLC

San Juan, PR, 00909, Puerto Rico

Location

University of Puerto Rico, Medical Sciences Campus

San Juan, PR, 00936, Puerto Rico

Location

Related Links

MeSH Terms

Conditions

Liver Cirrhosis, Biliary

Interventions

baricitinib

Condition Hierarchy (Ancestors)

Cholestasis, IntrahepaticCholestasisBile Duct DiseasesBiliary Tract DiseasesDigestive System DiseasesLiver DiseasesLiver CirrhosisFibrosisPathologic ProcessesPathological Conditions, Signs and Symptoms

Limitations and Caveats

Zero participants reported in cohort A due to protection of personal identifiable information based on enrollment futility and cohort B is not reported due to early study termination based on enrollment futility.

Results Point of Contact

Title
Chief Medical Officer
Organization
Eli Lilly and Company

Study Officials

  • Call 1-877-CTILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 14, 2018

First Posted

November 15, 2018

Study Start

March 28, 2019

Primary Completion

September 26, 2019

Study Completion

September 26, 2019

Last Updated

October 14, 2020

Results First Posted

October 14, 2020

Record last verified: 2019-10

Data Sharing

IPD Sharing
Will share

Anonymized individual patient level data will be provided in a secure access environment upon approval of a research proposal and a signed data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data are available 6 months after the primary publication and approval of the indication studied in the US and European Union (EU), whichever is later. Data will be indefinitely available for requesting.
Access Criteria
A research proposal must be approved by an independent review panel and researchers must sign a data sharing agreement.
More information

Locations