NCT03678493

Brief Summary

This is a randomized, double-blind, placebo-controlled clinical trial of Fecal Microbiota Transplant (FMT) in 2 independent cohorts (60 acute myeloid leukemia patients undergoing intensive chemotherapy and 60 Allo-HCT patients). Participants in each cohort will be randomized in a 2:1 ratio to receive up to 3 treatments of FMT vs. placebo after each exposure to antibacterial antibiotics until 3 months after randomization.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
100

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Sep 2019

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 18, 2018

Completed
1 day until next milestone

First Posted

Study publicly available on registry

September 19, 2018

Completed
12 months until next milestone

Study Start

First participant enrolled

September 9, 2019

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 11, 2022

Completed
1.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 4, 2023

Completed
5 months until next milestone

Results Posted

Study results publicly available

May 16, 2024

Completed
Last Updated

May 16, 2024

Status Verified

April 1, 2024

Enrollment Period

2.4 years

First QC Date

September 18, 2018

Results QC Date

November 3, 2023

Last Update Submit

April 22, 2024

Conditions

Keywords

AMLAllo-HCT

Outcome Measures

Primary Outcomes (1)

  • Efficacy of FMT in AML Patients and Allo-HCT Recipients - Number of Infections

    Number of infections infections until 4 months after the first intervention. Monitored each visit through safety assessment.

    4 Months

Secondary Outcomes (7)

  • FMT Engraftment

    2 Weeks after first FMT treatment

  • FMT Engraftment

    4 Weeks after first FMT treatment

  • Percentage of Participants With Grade II-IV Acute Graft-versus-host Disease (aGVHD II-IV)

    Day 180 post-HCT, up to 7 months

  • Number of BSI of Suspected Gut Origin

    1 week after first FMT treatment

  • Number of Bacterial Infections

    4 Months after first FMT treatment

  • +2 more secondary outcomes

Study Arms (4)

AML Patients undergoing Intensive Chemotherapy

EXPERIMENTAL
Biological: Fecal Microbiota Transplant (FMT)

AML Patients undergoing Intensive Chemotherapy Control

PLACEBO COMPARATOR
Other: Placebo

Patients undergoing Allo-HCT Patients

EXPERIMENTAL
Biological: Fecal Microbiota Transplant (FMT)

Patients undergoing Allo-HCT Patients Control

PLACEBO COMPARATOR
Other: Placebo

Interventions

Oral Capsule

Also known as: FMT
AML Patients undergoing Intensive ChemotherapyPatients undergoing Allo-HCT Patients
PlaceboOTHER

Oral Capsule

AML Patients undergoing Intensive Chemotherapy ControlPatients undergoing Allo-HCT Patients Control

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age≥ 18 years
  • Cohort A: Patients undergoing intensive induction chemotherapy for acute myeloid leukemia (AML; newly diagnosed or relapsed/refractory).
  • \* Any intensive regimen with planned \~4 weeks of inpatient stay
  • Cohort B: Allo-HCT patients
  • \* Any allogeneic transplant regimen with planned GVHD prophylaxis containing generic IV Mycophenolate Mofetil (MMF) and tacrolimus (Tac)
  • Sexually active females of childbearing potential and males with partners of child-bearing potential must agree to use adequate birth control until at least six months post-FMT/placebo
  • Voluntary written consent signed before performance of any study-related procedure not part of normal medical care

You may not qualify if:

  • Planned continuation of antibacterial antibiotics after the first neutrophil recovery (ANC \> 1,000)
  • Patients who are currently receiving or recently received (within 28 days) other investigational agents.
  • Pregnant or breast feeding. The FDA has not classified this agent into a specified pregnancy category. Females of childbearing potential must have a blood test or urine study within 14 days prior to registration to rule out pregnancy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Masonic Cancer Center at University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Related Publications (1)

  • Rashidi A, Ebadi M, Rehman TU, Elhusseini H, Kazadi D, Halaweish H, Khan MH, Hoeschen A, Cao Q, Luo X, Kabage AJ, Lopez S, Holtan SG, Weisdorf DJ, Khoruts A, Staley C. Randomized Double-Blind Phase II Trial of Fecal Microbiota Transplantation Versus Placebo in Allogeneic Hematopoietic Cell Transplantation and AML. J Clin Oncol. 2023 Dec 1;41(34):5306-5319. doi: 10.1200/JCO.22.02366. Epub 2023 May 26.

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

Fecal Microbiota Transplantation

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Biological TherapyTherapeutics

Results Point of Contact

Title
Armin Rashidi, MD, PhD
Organization
University of Minnesota, Masonic Cancer Center

Study Officials

  • Armin Rashidi, MD, PhD

    University of Minnesota, Division of Hematology, Oncology and Transplantation

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 18, 2018

First Posted

September 19, 2018

Study Start

September 9, 2019

Primary Completion

February 11, 2022

Study Completion

December 4, 2023

Last Updated

May 16, 2024

Results First Posted

May 16, 2024

Record last verified: 2024-04

Locations