NCT03665597

Brief Summary

The purpose of this study is to characterize the pharmacokinetic (PK) profile of pembrolizumab (MK-3475) following single subcutaneous (SC) injection of pembrolizumab Dose A versus pembrolizumab Dose C in adults with advanced melanoma. Additionally, the safety and tolerability of pembrolizumab SC injections will be assessed. And, finally, the efficacy of pembrolizumab intravenous (IV) infusion administration will be assessed.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
138

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Nov 2018

Longer than P75 for phase_1

Geographic Reach
4 countries

15 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 23, 2018

Completed
19 days until next milestone

First Posted

Study publicly available on registry

September 11, 2018

Completed
2 months until next milestone

Study Start

First participant enrolled

November 19, 2018

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 4, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 4, 2023

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

February 10, 2025

Completed
Last Updated

February 10, 2025

Status Verified

January 1, 2025

Enrollment Period

5 years

First QC Date

August 23, 2018

Results QC Date

November 21, 2024

Last Update Submit

February 3, 2025

Conditions

Keywords

Programmed Cell Death 1PD1PD-1Programmed Cell Death-Ligand 1PDL1PD-L1

Outcome Measures

Primary Outcomes (8)

  • Area Under the Concentration-Time Curve (AUC) of Pembrolizumab - Cohort A

    AUC was defined as a measure of pembrolizumab exposure that was calculated as the product of plasma drug concentration and time. Blood samples were collected at designated time points and a pharmacokinetic (PK) model based on historical intravenous pembrolizumab PK data were used for the determination of the AUC of pembrolizumab. Geometric least-square mean (GM) and 95% confidence intervals were derived from mixed-effects model performed on natural log-transformed values. Data were reported by treatment received.

    Cycles 1-3: Day 1 Predose and Days 2, 5, 10 and 15; Cycle 4: Day 1 Predose. Samples were also collected after IV infusion on Cycles 1-3: Day 1 ~0.5 hours after infusion and after SC injection on Days 3, 4, 6, and 7. Each cycle was 21 days.

  • Maximum Plasma Concentration (Cmax) of Pembrolizumab - Cohort A

    Cmax was defined as the maximum concentration of pembrolizumab observed in plasma following a single dose. Blood samples were collected at designated time points and a PK model based on historical intravenous pembrolizumab PK data were used for the determination of the AUC of pembrolizumab. GM and 95% confidence intervals were derived from mixed-effects model performed on natural log-transformed values. Data were reported by treatment received.

    Cycles 1-3: Day 1 Predose and Days 2, 5, 10 and 15; Cycle 4: Day 1 Predose. Samples were also collected after IV infusion on Cycles 1-3: Day 1 ~0.5 hours after infusion and after SC injection on Days 3, 4, 6, and 7. Each cycle was 21 days.

  • Bioavailability (F) of Pembrolizumab - Cohort A

    Blood samples were collected at designated time points and a population PK model based on historical intravenous pembrolizumab PK data was used for the determination of the F of pembrolizumab. Per protocol, an integrated population PK analysis was performed and combined data for Cohort A was reported.

    Cycles 1-3: Day 1 Predose and Days 2, 5, 10 and 15; Cycle 4: Day 1 Predose. Samples were also collected after IV infusion on Cycles 1-3: Day 1 ~0.5 hours after infusion and after SC injection on Days 3, 4, 6, and 7. Each cycle was 21 days.

  • Absorption Rate Constant (Ka) of Pembrolizumab - Cohort A

    Blood samples were collected at designated time points and a population PK model based on historical intravenous pembrolizumab PK data was used for the determination of the Ka of pembrolizumab. Per protocol, an integrated population PK analysis was performed and combined data for Cohort A was reported. Participants in Cohort B weren't analyzed, per protocol.

    Cycles 1-3: Day 1 Predose and Days 2, 5, 10 and 15; Cycle 4: Day 1 Predose. Samples were also collected after IV infusion on Cycles 1-3: Day 1 ~0.5 hours after infusion and after SC injection on Days 3, 4, 6, and 7. Each cycle was 21 days.

  • Time of Maximum Plasma Concentration (Tmax) of Pembrolizumab - Cohort A

    Blood samples were collected at designated time points for the determination of the Tmax of pembrolizumab.

    Cycles 1-3: Day 1 Predose and Days 2, 5, 10 and 15; Cycle 4: Day 1 Predose. Samples were also collected after IV infusion on Cycles 1-3: Day 1 ~0.5 hours after infusion and after SC injection on Days 3, 4, 6, and 7. Each cycle was 21 days.

  • Clearance (CL) of Pembrolizumab - Cohort A

    Blood samples were collected at designated time points and a population PK model based on historical intravenous pembrolizumab PK data was used for the determination of the CL of pembrolizumab. Per protocol, an integrated population PK analysis was performed and combined data for Cohort A was reported.

    Cycles 1-3: Day 1 Predose and Days 2, 5, 10 and 15; Cycle 4: Day 1 Predose. Samples were also collected after IV infusion on Cycles 1-3: Day 1 ~0.5 hours after infusion and after SC injection on Days 3, 4, 6, and 7. Each cycle was 21 days.

  • Central Volume of Distribution (Vc) of Pembrolizumab - Cohort A

    Blood samples were collected at designated time points and a population PK model based on historical intravenous pembrolizumab PK data was used for the determination of the Vc of pembrolizumab. Per protocol, an integrated population PK analysis was performed and combined data for Cohort A was reported.

    Cycles 1-3: Day 1 Predose and Days 2, 5, 10 and 15; Cycle 4: Day 1 Predose. Samples were also collected after IV infusion on Cycles 1-3: Day 1 ~0.5 hours after infusion and after SC injection on Days 3, 4, 6, and 7. Each cycle was 21 days.

  • Objective Response Rate (ORR) Per Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1) - Cohort B

    ORR was defined as the percentage of participants in the analysis population who had a Complete Response (CR: Disappearance of all target lesions) or Partial Response (PR: At least a 30% decrease in the sum of diameters of target lesions). Responses were based upon blinded independent central review (BICR) per RECIST 1.1. ORR was reported for participants in Cohort B.

    Up to approximately 54 months

Secondary Outcomes (15)

  • Number of Participants Positive for Pembrolizumab Anti-Drug Antibody (ADA) Formation - Cohort A

    Cycles 1-4 Day 1: Predose. Each cycle is 21 days. (Up to approximately 64 days)

  • Number of Participants Who Experienced One or More Adverse Event (AEs) - Cohort A

    Up to approximately 27 months

  • Number of Participants Who Discontinued Study Treatment Due to an AE - Cohort A

    Up to approximately 23 months

  • Number of Participants With One or More Injection Site Signs and Symptoms After Subcutaneous Pembrolizumab Injection in Cycles 1-3 - Cohort A

    Cycles 1-3 Day 1: Up to 60 minutes postdose. Each cycle is 21 days. (Up to approximately 43 days)

  • Duration of Response (DOR) Per RECIST 1.1 - Cohort B

    Up to approximately 54 months

  • +10 more secondary outcomes

Study Arms (7)

Cohort A Pembrolizumab Treatment Sequence 1

EXPERIMENTAL

Participants receive a single dose of pembrolizumab in each 21-day cycle in the following sequence: Cycle 1 Day 1: pembrolizumab 165 mg/mL subcutaneously (SC); Cycle 2 Day 1: pembrolizumab 200 mg intravenously (IV); Cycle 3 Day 1: pembrolizumab 130 mg/mL SC; Cycle 4 Day 1 and every cycle thereafter, up to a total of 35 cycles (up to approximately 2 years), Day 1: pembrolizumab 200 mg IV.

Biological: Pembrolizumab Dose CBiological: Pembrolizumab Dose ABiological: Pembrolizumab Dose B

Cohort A Pembrolizumab Treatment Sequence 2

EXPERIMENTAL

Participants receive a single dose of pembrolizumab in each 21-day cycle in the following sequence: Cycle 1 Day 1: pembrolizumab 165 mg/mL SC; Cycle 2 Day 1: pembrolizumab 130 mg/mL SC; Cycle 3 Day 1: pembrolizumab 200 mg IV; Cycle 4 Day 1 and every cycle thereafter, up to a total of 35 cycles (up to approximately 2 years), Day 1: pembrolizumab 200 mg IV.

Biological: Pembrolizumab Dose CBiological: Pembrolizumab Dose ABiological: Pembrolizumab Dose B

Cohort A Pembrolizumab Treatment Sequence 3

EXPERIMENTAL

Participants receive a single dose of pembrolizumab in each 21-day cycle in the following sequence: Cycle 1 Day 1: pembrolizumab 130 mg/mL SC; Cycle 2 Day 1: pembrolizumab 165 mg/mL SC; Cycle 3 Day 1: pembrolizumab 200 mg IV; Cycle 4 Day 1 and every cycle thereafter, up to a total of 35 cycles (up to approximately 2 years), Day 1: pembrolizumab 200 mg IV.

Biological: Pembrolizumab Dose CBiological: Pembrolizumab Dose ABiological: Pembrolizumab Dose B

Cohort A Pembrolizumab Treatment Sequence 4

EXPERIMENTAL

Participants receive a single dose of pembrolizumab in each 21-day cycle in the following sequence: Cycle 1 Day 1: pembrolizumab 200 mg SC; Cycle 2 Day 1: pembrolizumab 200 mg IV; Cycle 3 Day 1: pembrolizumab 130 mg/mL SC; Cycle 4 Day 1 and every cycle thereafter, up to a total of 35 cycles (up to approximately 2 years), Day 1: pembrolizumab Dose 200 mg IV.

Biological: Pembrolizumab Dose CBiological: Pembrolizumab Dose ABiological: Pembrolizumab Dose B

Cohort A Pembrolizumab Treatment Sequence 5

EXPERIMENTAL

Participants receive a single dose of pembrolizumab in each 21-day cycle in the following sequence: Cycle 1 Day 1: pembrolizumab 200 mg IV; Cycle 2 Day 1: pembrolizumab 130 mg/mL SC; Cycle 3 Day 1: pembrolizumab 165 mg/mL SC: Cycle 4 Day 1 and every cycle thereafter, up to a total of 35 cycles (up to approximately 2 years), Day 1: pembrolizumab 200 mg IV.

Biological: Pembrolizumab Dose CBiological: Pembrolizumab Dose ABiological: Pembrolizumab Dose B

Cohort A Pembrolizumab Treatment Sequence 6

EXPERIMENTAL

Participants receive a single dose of pembrolizumab in each 21-day cycle in the following sequence: Cycle 1 Day 1: pembrolizumab 200 mg IV; Cycle 2 Day 1: pembrolizumab 165 mg/mL SC; Cycle 3 Day 1: pembrolizumab 130 mg/mL SC; Cycle 4 Day 1 and every cycle thereafter, up to a total of 35 cycles (up to approximately 2 years), Day 1: pembrolizumab 200 mg IV.

Biological: Pembrolizumab Dose CBiological: Pembrolizumab Dose ABiological: Pembrolizumab Dose B

Cohort B Pembrolizumab 400 mg IV

EXPERIMENTAL

Participants receive a single dose of pembrolizumab 400 mg IV on Day 1 of each 42-day cycle (every 6 weeks; Q6W) for up to 18 cycles (up to approximately 2 years).

Biological: Pembrolizumab Dose D

Interventions

165 mg/mL administered to a final dose of 285 mg via subcutaneous injection

Also known as: KEYTRUDA®, MK-3475
Cohort A Pembrolizumab Treatment Sequence 1Cohort A Pembrolizumab Treatment Sequence 2Cohort A Pembrolizumab Treatment Sequence 3Cohort A Pembrolizumab Treatment Sequence 4Cohort A Pembrolizumab Treatment Sequence 5Cohort A Pembrolizumab Treatment Sequence 6

130 mg/mL administered to a final dose of 285 mg via subcutaneous injection

Also known as: KEYTRUDA®, MK-3475
Cohort A Pembrolizumab Treatment Sequence 1Cohort A Pembrolizumab Treatment Sequence 2Cohort A Pembrolizumab Treatment Sequence 3Cohort A Pembrolizumab Treatment Sequence 4Cohort A Pembrolizumab Treatment Sequence 5Cohort A Pembrolizumab Treatment Sequence 6

200 mg administered via intravenous infusion

Also known as: KEYTRUDA®, MK-3475
Cohort A Pembrolizumab Treatment Sequence 1Cohort A Pembrolizumab Treatment Sequence 2Cohort A Pembrolizumab Treatment Sequence 3Cohort A Pembrolizumab Treatment Sequence 4Cohort A Pembrolizumab Treatment Sequence 5Cohort A Pembrolizumab Treatment Sequence 6

400 mg administered via intravenous infusion

Also known as: KEYTRUDA®, MK-3475
Cohort B Pembrolizumab 400 mg IV

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has histologically or cytologically confirmed diagnosis of advanced melanoma.
  • Has unresectable Stage III or Stage IV melanoma, as per American Joint Committee on Cancer (AJCC) staging system not amenable to local therapy.
  • Has been untreated for advanced or metastatic disease except as follows:
  • a. BRAF V600 mutant melanoma may have received standard of care targeted therapy (e.g. BRAF/ mitogen-activated protein kinase kinase enzyme \[MEK\] inhibitor, alone or in combination) and be eligible for this study.
  • b. Prior adjuvant (post-surgery) or neoadjuvant (pre-surgery) melanoma therapy is permitted if it was completed ≥4 weeks before randomization and all related AEs have either returned to baseline or stabilized (resolution of toxic effect\[s\] of the most recent prior therapy to Grade 1 or less \[except alopecia\]).
  • Female participants must agree to use contraception during the treatment period and for ≥120 days after the last dose of study treatment.
  • Has measurable disease per RECIST 1.1 as assessed by BICR. Lesions situated in a previously irradiated area are considered measurable if progression has been demonstrated in such lesions.
  • Has an Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 1.
  • Has adequate organ function.

You may not qualify if:

  • Has received prior therapy with an anti-programmed cell death 1 (PD-1), anti-programmed cell death-ligand 1 (anti-PD-L1), or anti-PD-L2 or with an agent directed to another stimulatory or co-inhibitory T-cell receptor (e.g. OX-40 and CD137) or any other antibody or drug specifically targeting checkpoint pathways other than anti-cytotoxic T-lymphocyte-associated protein 4 (anti-CTLA-4) which is permitted in the adjuvant setting.
  • Has received prior radiotherapy within 2 weeks of start of study treatment. Participants must have recovered from all radiation-related toxicities, not require corticosteroids, and not have had radiation pneumonitis.
  • Has received a live vaccine within 30 days prior to the first dose of study treatment.
  • Is currently participating in or has participated in a study of an investigational agent or has used an investigational device within 4 weeks prior to the first dose of study treatment.
  • Has a diagnosis of immunodeficiency or is receiving chronic systemic steroid therapy (in dosing exceeding 10 mg daily of prednisone equivalent) or any other form of immunosuppressive therapy within 7 days prior the first dose of study treatment.
  • Has a known additional malignancy that is progressing or has required active treatment within the past 2 years. Note: Participants with basal cell carcinoma of the skin, squamous cell carcinoma of the skin, or carcinoma in situ (e.g. breast carcinoma, cervical cancer in situ) that have undergone potentially curative therapy are not excluded.
  • Has known active central nervous system metastases and/or carcinomatous meningitis.
  • Has severe hypersensitivity (≥Grade 3) to pembrolizumab and/or any of its excipients.
  • Has ocular melanoma.
  • Has an active autoimmune disease that has required systemic treatment in past 2 years (i.e., with use of disease modifying agents, corticosteroids or immunosuppressive drugs).
  • Has a history of (non-infectious) pneumonitis that required steroids or has current pneumonitis.
  • Has an active infection requiring systemic therapy.
  • Has a known history of human immunodeficiency virus (HIV) infection.
  • Has a known history of Hepatitis B or known active Hepatitis C virus infection.
  • Is pregnant or breastfeeding or expecting to conceive or father children within the projected duration of the study, starting with the screening visit through 120 days after the last dose of study treatment.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

Orange Health Services ( Site 0004)

Orange, New South Wales, 2800, Australia

Location

Calvary Mater Newcastle ( Site 0006)

Waratah, New South Wales, 2298, Australia

Location

Cairns and Hinterland Hospital and Health Service ( Site 0001)

Cairns, Queensland, 4870, Australia

Location

Royal Adelaide Hospital ( Site 0002)

Adelaide, South Australia, 5000, Australia

Location

Ballarat Health Services ( Site 0003)

Ballarat, 3350, Australia

Location

MNCCI Port Macquarie Base Hospital ( Site 0005)

Port Macquarie, 2444, Australia

Location

MPOC ( Site 0027)

Groenkloof Pretoria, Gauteng, 0181, South Africa

Location

WITS Clinical Research CMJAH Clinical Trial Site ( Site 0030)

Johannesburg, Gauteng, 2193, South Africa

Location

The Medical Oncology Centre of Rosebank ( Site 0026)

Johannesburg, Gauteng, 2196, South Africa

Location

Cape Town Oncology Trials Pty Ltd ( Site 0028)

Kraaifontein, Western Cape, 7570, South Africa

Location

Sandton Oncology Medical Group PTY LTD ( Site 0029)

Johannesburg, 2196, South Africa

Location

Hospital Universitari Vall d Hebron ( Site 0062)

Barcelona, 08035, Spain

Location

Hospital Clinic i Provincial de Barcelona ( Site 0061)

Barcelona, 08036, Spain

Location

Onkologikoa - Instituto Oncologico de San Sebastian ( Site 0063)

Donostia / San Sebastian, 20014, Spain

Location

Karolinska Universitetssjukhuset Solna ( Site 0040)

Solna, 171 64, Sweden

Location

Related Publications (1)

  • Cohen G, Rapoport B, Chan SW, Ruff P, Arance A, Mujika Eizmendi K, Houghton B, Brown MP, Zielinski RM, Munoz Couselo E, Lyle M, Anderson JR, Jain L, de Alwis D, Lala M, Akala O, Chartash E, Jacobs C. Pembrolizumab 400 mg every 6 weeks as first-line therapy for advanced melanoma (KEYNOTE-555): Results from cohort B of an open-label, phase 1 study. PLoS One. 2024 Nov 12;19(11):e0309778. doi: 10.1371/journal.pone.0309778. eCollection 2024.

Related Links

MeSH Terms

Conditions

Melanoma

Interventions

pembrolizumab

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue Diseases

Results Point of Contact

Title
Senior Vice President, Global Clinical Development
Organization
Merck Sharp & Dohme LLC

Study Officials

  • Medical Director

    Merck Sharp & Dohme LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
CROSSOVER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 23, 2018

First Posted

September 11, 2018

Study Start

November 19, 2018

Primary Completion

December 4, 2023

Study Completion

December 4, 2023

Last Updated

February 10, 2025

Results First Posted

February 10, 2025

Record last verified: 2025-01

Data Sharing

IPD Sharing
Will share

http://engagezone.msd.com/doc/ProcedureAccessClinicalTrialData.pdf

More information

Locations