NCT03636269

Brief Summary

This is a multicenter, international study to evaluate the safety and efficacy of intravenous (IV) CR845 at a dose of 0.5 mcg/kg administered after each dialysis session. The study includes a 12-week randomized, double-blind, placebo-controlled Phase and a 52-week Open-label Extension Phase.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
473

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2018

Geographic Reach
11 countries

92 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 17, 2018

Completed
17 days until next milestone

First Submitted

Initial submission to the registry

August 3, 2018

Completed
14 days until next milestone

First Posted

Study publicly available on registry

August 17, 2018

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 30, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 30, 2020

Completed
2.1 years until next milestone

Results Posted

Study results publicly available

April 26, 2022

Completed
Last Updated

April 26, 2022

Status Verified

March 1, 2022

Enrollment Period

1.7 years

First QC Date

August 3, 2018

Results QC Date

September 21, 2021

Last Update Submit

March 29, 2022

Conditions

Keywords

HemodialysisdifelikefalinCR845PruritusChronic ItchItchItchingUremic PruritusDialysisCKDCKD-associated pruritusCKD-aPESRD (end stage renal disease)KALMChronic Kidney DiseaseKidney failure, chronicKidney dysfunctionGeneralized pruritus

Outcome Measures

Primary Outcomes (1)

  • Reduction of Itch Intensity as Assessed by the Percentage of Patients Achieving an Improvement From Baseline ≥3 Points With Respect to the Weekly Mean of the Daily 24-hour Worst Itching Intensity Numerical Rating Scale (NRS) Score at Week 12

    Intensity of itch will be measured using an NRS used to indicate the intensity of the worst itching over the past 24 hours using a 0 to 10 numeric rating scale, where "0" represents "no itching" and "10" represents "worst itching imaginable". LS means estimated percent, odds ratio and P value used a logistic regression model.

    Week 12

Secondary Outcomes (3)

  • Reduction of Itch Intensity as Assessed by the Percentage of Patients Achieving an Improvement From Baseline ≥4 Points With Respect to the Weekly Mean of the Daily 24-hour Worst Itching Intensity NRS Score at Week 12

    Week 12

  • Improvement in Itch-related Quality of Life as Assessed by the Change From Baseline in Total Skindex-10 Scale Score at the End of Week 12

    Baseline, Week 12

  • Improvement in Itch-related Quality of Life as Assessed by the Change From Baseline in 5-D Itch Scale Score at the End of Week 12

    Baseline, Week 12

Study Arms (2)

CR845 0.5mcg/kg

ACTIVE COMPARATOR

IV CR845 0.5 mcg/kg administered after each dialysis session (3 times/week)

Drug: CR845 0.5 mcg/kg

Placebo

PLACEBO COMPARATOR

IV Placebo administered after each dialysis session (3 times/week)

Drug: Placebo

Interventions

IV CR845 0.5 mcg/kg administered three times/week

Also known as: CR845, Difelikefalin
CR845 0.5mcg/kg

IV placebo administered three times/week

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has end-stage renal disease (ESRD) and has been on hemodialysis 3 times per week for at least 3 months prior to the start of screening;
  • Has at least 2 single-pool Kt/V measurements ≥1.2, or at least 2 urea reduction ratio measurements ≥65%, or 1 single pool Kt/V measurement ≥1.2 and 1 urea reduction ratio measurement ≥65% on different dialysis days during the 3 months period prior to screening;
  • Prior to randomization:
  • Has completed Worst Itching Intensity NRS worksheets up to 8 days prior to 1st dose;
  • Has a mean baseline Worst Itching Intensity NRS indicative of moderate to severe uremic pruritus.
  • Has received at least 30 doses of the planned 36 doses of study drug during the Double-blind Phase of this study;

You may not qualify if:

  • A patient will be excluded from the Double-blind Phase of the study if any of the following criteria are met:
  • Known noncompliance with dialysis treatment that in the opinion of the investigator would impede completion or validity of the study;
  • Scheduled to receive a kidney transplant during the study;
  • New or change of treatment received for itch including antihistamines and corticosteroids (oral, IV, or topical) within 14 days prior to screening;
  • Received another investigational drug within 30 days prior to the start of screening or is planning to participate in another clinical study while enrolled in this study;
  • Has pruritus only during the dialysis session (by patient report);
  • Is receiving ongoing ultraviolet B and anticipates receiving such treatment during the study;
  • Participated in a previous clinical study with CR845.
  • A patient will be excluded from the Open-label Extension Phase of the study if any of the additional key following criteria are met at the time of entry into the Open-label Extension Phase:
  • Completed the Double-blind Phase of this study but exhibited adverse events during the course of the Treatment Period that may preclude continued exposure to the study drug;
  • Was noncompliant with protocol procedures during the Double-blind Phase of this study which is indicative of an inability to follow protocol procedures.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (92)

Cara Therapeutics Study Site

Chula Vista, California, 91910, United States

Location

Cara Therapeutics Study Site

Fountain Valley, California, 92708, United States

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Cara Therapeutics Study Site

Northridge, California, 91324, United States

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Cara Therapeutics Study Site

Riverside, California, 92503, United States

Location

Cara Therapeutics Study Site 2

San Dimas, California, 91773, United States

Location

Cara Therapeutics Study Site

San Dimas, California, 91773, United States

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Cara Therapeutics Study Site

Westminster, Colorado, 80031, United States

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Cara Therapeutics Study Site

Hialeah, Florida, 33012, United States

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Cara Therapeutics Study Site

Miami Gardens, Florida, 33169, United States

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Cara Therapeutics Study Site

Orlando, Florida, 32810, United States

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Cara Therapeutics Study Site

Athens, Georgia, 30606, United States

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Cara Therapeutics Study Site

Macon, Georgia, 31201, United States

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Cara Therapeutics Study Site

Baton Rouge, Louisiana, 70808, United States

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Cara Therapeutics Study Site

Brockton, Massachusetts, 02301, United States

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Cara Therapeutics Study Site

Kalamazoo, Michigan, 49007, United States

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Cara Therapeutics Study Site

Roseville, Michigan, 48066, United States

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Cara Therapeutics Study Site

Saint Clair, Michigan, 48081, United States

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Cara Therapeutics Study Site

Tupelo, Mississippi, 38801, United States

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Cara Therapeutics Study Site

St Louis, Missouri, 63136, United States

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Cara Therapeutics Study Site

Clifton, New Jersey, 07011, United States

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Cara Therapeutics Study Site

Somerville, New Jersey, 08876, United States

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Cara Therapeutics Study Site

Albuquerque, New Mexico, 87109, United States

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Cara Therapeutics Study Site

Long Island City, New York, 11106, United States

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Cara Therapeutics Study Site

Austin, Texas, 78758, United States

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Cara Therapeutics Study Site

Dallas, Texas, 75228, United States

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Cara Therapeutics Study Site

McAllen, Texas, 78503, United States

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Cara Therapeutics Study Site

San Antonio, Texas, 78207, United States

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Cara Therapeutics Study Site

St. George, Utah, 84790, United States

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Cara Therapeutics Study Site

Roanoke, Virginia, 24014, United States

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Cara Therapeutics Study Site

Camperdown, New South Wales, Australia

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Cara Therapeutics Study Site

Concord, New South Wales, Australia

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Cara Therapeutics Study Site

Wahroonga, New South Wales, 2076, Australia

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Cara Therapeutics Study Site

Westmead, New South Wales, Australia

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Cara Therapeutics Study Site

Launceston, Tasmania, Australia

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Cara Therapeutics Study Site

Clayton, Victoria, Australia

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Cara Therapeutics Study Site

Heidelberg, Victoria, Australia

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Cara Therapeutics Study Site

St Albans, Victoria, Australia

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Cara Therapeutics Study Site

Adelaide, Australia

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Cara Therapeutics Study Site

Halifax, Nova Scotia, Canada

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Cara Therapeutics Study Site

Oshawa, Ontario, Canada

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Cara Therapeutics Study Site

Scarborough Village, Ontario, Canada

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Cara Therapeutics Study Site

Toronto, Ontario, Canada

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Cara Therapeutics Study Site

Montreal, Quebec, Canada

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Cara Therapeutics Study Site

Frýdek-Místek, Czechia

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Cara Therapeutics Study Site

Prague, Czechia

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Cara Therapeutics Study Site

Düsseldorf, Germany

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Cara Therapeutics Study Site

Heilbronn, Germany

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Cara Therapeutics Study Site

Baja, 6500, Hungary

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Cara Therapeutics Study Site

Debrecen, Hungary

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Cara Therapeutics Study Site 2

Pécs, Hungary

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Cara Therapeutics Study Site

Pécs, Hungary

Location

Cara Therapeutics Study Site

Szeged, 6720, Hungary

Location

Cara Therapeutics Study Site

Székesfehérvár, Hungary

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Cara Therapeutics Study Site

Szigetvár, Hungary

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Cara Therapeutics Study Site

Auckland, New Zealand

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Cara Therapeutics Study Site

Hamilton, New Zealand

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Cara Therapeutics Study Site

New Plymouth, New Zealand

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Cara Therapeutics Study Site

Brodnica, Poland

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Cara Therapeutics Study Site

Brzeg, Poland

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Cara Therapeutics Study Site

Bydgoszcz, Poland

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Cara Therapeutics Study Site

Grójec, Poland

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Cara Therapeutics Study Site

Krakow, Poland

Location

Cara Therapeutics Study Site

Kwidzyn, Poland

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Cara Therapeutics Study Site 2

Lodz, Poland

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Cara Therapeutics Study Site

Lodz, Poland

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Cara Therapeutics Study Site

Nakło nad Notecią, Poland

Location

Cara Therapeutics Study Site

Olkusz, Poland

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Cara Therapeutics Study Site

Olsztyn, Poland

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Cara Therapeutics Study Site

Poznan, Poland

Location

Cara Therapeutics Study Site

Warsaw, Poland

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Cara Therapeutics Study Site

Wroclaw, Poland

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Cara Therapeutics Study Site

Zamość, Poland

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Cara Therapeutics Study Site

Żyrardów, Poland

Location

Cara Therapeutics Study Site

Daegu, 41931, South Korea

Location

Cara Therapeutics Study Site 2

Daegu, South Korea

Location

Cara Therapeutics Study Site

Daejeon, South Korea

Location

Cara Therapeutics Study Site

Goyang-si, South Korea

Location

Cara Therapeutics Study Site

Guri-si, South Korea

Location

Cara Therapeutics Study Site

Seogu, 49201, South Korea

Location

Cara Therapeutics Study Site 2

Seoul, South Korea

Location

Cara Therapeutics Study Site 3

Seoul, South Korea

Location

Cara Therapeutics Study Site

Seoul, South Korea

Location

Cara Therapeutics Study Site

Kaohsiung City, Taiwan

Location

Cara Therapeutics Study Site

New Taipei City, Taiwan

Location

Cara Therapeutics Study Site 2

Taipei, Taiwan

Location

Cara Therapeutics Study Site

Taipei, Taiwan

Location

Cara Therapeutics Study Site

Belfast, United Kingdom

Location

Cara Therapeutics Study Site

Ipswich, United Kingdom

Location

Cara Therapeutics Study Site

London, United Kingdom

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Cara Therapeutics Study Site

Londonderry, United Kingdom

Location

Cara Therapeutics Study Site

Nottingham, United Kingdom

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Cara Therapeutics Study Site

Westcliff-on-Sea, United Kingdom

Location

Related Publications (5)

  • Fishbane SN, Block GA, Evenepoel P, Budden J, Morin I, Menzaghi F, Wen W, Lerma EV. Pruritus Severity and Serum Phosphate in CKD: A Post Hoc Analysis of Difelikefalin Studies. Kidney360. 2024 Sep 1;5(9):1270-1280. doi: 10.34067/KID.0000000000000520. Epub 2024 Jul 22.

  • Weiner DE, Schaufler T, McCafferty K, Kalantar-Zadeh K, Germain M, Ruessmann D, Morin I, Menzaghi F, Wen W, Stander S. Difelikefalin improves itch-related sleep disruption in patients undergoing haemodialysis. Nephrol Dial Transplant. 2024 Jun 28;39(7):1125-1137. doi: 10.1093/ndt/gfad245.

  • Fishbane S, Wen W, Munera C, Lin R, Bagal S, McCafferty K, Menzaghi F, Goncalves J. Safety and Tolerability of Difelikefalin for the Treatment of Moderate to Severe Pruritus in Hemodialysis Patients: Pooled Analysis From the Phase 3 Clinical Trial Program. Kidney Med. 2022 Jun 28;4(8):100513. doi: 10.1016/j.xkme.2022.100513. eCollection 2022 Aug.

  • Topf J, Wooldridge T, McCafferty K, Schomig M, Csiky B, Zwiech R, Wen W, Bhaduri S, Munera C, Lin R, Jebara A, Cirulli J, Menzaghi F. Efficacy of Difelikefalin for the Treatment of Moderate to Severe Pruritus in Hemodialysis Patients: Pooled Analysis of KALM-1 and KALM-2 Phase 3 Studies. Kidney Med. 2022 Jun 28;4(8):100512. doi: 10.1016/j.xkme.2022.100512. eCollection 2022 Aug.

  • Hercz D, Jiang SH, Webster AC. Interventions for itch in people with advanced chronic kidney disease. Cochrane Database Syst Rev. 2020 Dec 7;12(12):CD011393. doi: 10.1002/14651858.CD011393.pub2.

MeSH Terms

Conditions

PruritusRenal Insufficiency, ChronicKidney Failure, Chronic

Interventions

difelikefalin

Condition Hierarchy (Ancestors)

Skin DiseasesSkin and Connective Tissue DiseasesSkin ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic Processes

Results Point of Contact

Title
Frédérique Menzaghi, PhD
Organization
Cara Therapeutics

Study Officials

  • Frédérique Menzaghi, PhD

    Cara Therapeutics

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 3, 2018

First Posted

August 17, 2018

Study Start

July 17, 2018

Primary Completion

March 30, 2020

Study Completion

March 30, 2020

Last Updated

April 26, 2022

Results First Posted

April 26, 2022

Record last verified: 2022-03

Data Sharing

IPD Sharing
Will not share

Locations