NCT03545425

Brief Summary

The overall objective of this study is to determine whether LRRK2 kinase activity and/or mitochondrial DNA (mtDNA) damage could serve as potential biomarkers in PD.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
114

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started May 2018

Geographic Reach
1 country

5 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 16, 2018

Completed
6 days until next milestone

First Submitted

Initial submission to the registry

May 22, 2018

Completed
13 days until next milestone

First Posted

Study publicly available on registry

June 4, 2018

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2020

Completed
Last Updated

September 8, 2021

Status Verified

August 1, 2021

Enrollment Period

2 years

First QC Date

May 22, 2018

Last Update Submit

August 31, 2021

Conditions

Keywords

Parkinson's DiseaseBiomarkerLRRK2

Outcome Measures

Primary Outcomes (3)

  • Phosphorylated LRRK2 and LRRK2-phosphorylated Rabs

    Assess the levels of phosphorylated LRRK2 and LRRK2-phosphorylated Rabs, as measures of LRRK2 kinase activity, in PBMCs and neutrophils from LRRK2 PD, idiopathic PD, non-manifesting LRRK2 mutation carriers and healthy controls.

    7 months

  • mtDNA damage in buffy coat

    Assess the levels of mtDNA damage in buffy coat from LRRK2 PD, idiopathic PD, non-manifesting LRRK2 mutation carriers and healthy controls.

    7 months

  • Correlate LRRK2 kinase activity to mtDNA damage

    Correlate LRRK2 kinase activity to mtDNA damage in blood from LRRK2 PD, idiopathic-PD, non-manifesting LRRK2 mutation carriers and healthy controls.

    7 months

Secondary Outcomes (3)

  • Assess the ability of the network to efficiently conduct a study

    7 months

  • Assess the ability of the network to collect high quality biospecimens

    7 months

  • To gauge the willingness of participants to participate in subsequent Fox BioNet studies

    7 Months

Study Arms (4)

Idiopathic Parkinson's Disease patients

Up to 30 Parkinson's Disease patients will be enrolled.

Procedure: Biofluid samplings

Healthy Controls

Up to 30 Healthy Controls will be enrolled.

Procedure: Biofluid samplings

LRRK2 G2019S - Manifesting

Up to 30 LRRK2 G2019S Manifesting carriers will be enrolled.

Procedure: Biofluid samplings

LRRK2 G2019S - Non-Manifesting

Up to 30 LRRK2 G2019s Non-Manifesting carriers will be enrolled.

Procedure: Biofluid samplings

Interventions

Blood and Urine

Healthy ControlsIdiopathic Parkinson's Disease patientsLRRK2 G2019S - ManifestingLRRK2 G2019S - Non-Manifesting

Eligibility Criteria

Age30 Years+
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

30 LRRK2 G2019S Manifesting carriers, 30 Idiopathic PD subjects, 30 LRRK2 G2019S Non-Manifesting Carriers, 30 Healthy Controls

You may qualify if:

  • LRRK2 Parkinson Disease (PD) Subjects:
  • Patients must have confirmed LRRK2 mutation
  • Patients must meet the MDS criteria for Parkinson's disease
  • Disease duration: any
  • Male or female age 30 years or older at time of PD diagnosis.
  • Idiopathic PD Subjects:
  • Patients must meet the MDS criteria for Parkinson's disease.
  • Disease duration: any
  • Male or female age 30 years or older at time of PD diagnosis.
  • Non-manifesting LRRK2 mutation carriers:
  • Patients must have confirmed LRRK2 mutation
  • Male or female age 30 years or older at Screening.
  • Control (C) Subjects:
  • Male or female age 30 years or older at Screening.

You may not qualify if:

  • LRRK2 Parkinson Disease (PD) Subjects:
  • Inability to provide informed consent
  • Participation in a blinded clinical trial of any kind or an unblinded trial of an investigational product that is not currently approved for use in humans.
  • Treatment for cancer in the last 5 years.
  • Idiopathic PD Subjects:
  • Inability to provide informed consent
  • Participation in a blinded clinical trial of any kind or an unblinded trial of an investigational product that is not currently approved for use in humans.
  • Treatment for cancer in the last 5 years.
  • Non-manifesting LRRK2 mutation carriers:
  • Inability to provide informed consent
  • Participation in a blinded clinical trial of any kind or an unblinded trial of an investigational product that is not currently approved for use in humans.
  • Treatment for cancer in the last 5 years.
  • Control Subjects:
  • Inability to provide informed consent
  • Participation in a blinded clinical trial of any kind or an unblinded trial of an investigational product that is not currently approved for use in humans.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Charles E. Schmidt College of Medicine, Florida Atlantic University

Boca Raton, Florida, 33431, United States

Location

Northwestern University

Chicago, Illinois, 60208, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Oregon Health and Sciences University

Portland, Oregon, 97239, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19107, United States

Location

Biospecimen

Retention: SAMPLES WITH DNA

Blood, Urine

MeSH Terms

Conditions

Parkinson Disease

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Study Officials

  • Connie Marras, MD

    University Health Network, Toronto

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
CROSS SECTIONAL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Neurologist at Toronto Western Hospital Movement Disorders Centre

Study Record Dates

First Submitted

May 22, 2018

First Posted

June 4, 2018

Study Start

May 16, 2018

Primary Completion

April 30, 2020

Study Completion

April 30, 2020

Last Updated

September 8, 2021

Record last verified: 2021-08

Data Sharing

IPD Sharing
Will not share

Locations