NCT03419897

Brief Summary

This study investigated the efficacy, safety, and pharmacokinetics of the anti-PD-1 monoclonal antibody BGB-A317 in participants with previously treated hepatocellular unresectable carcinoma.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
249

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Apr 2018

Typical duration for phase_2

Geographic Reach
8 countries

54 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 29, 2018

Completed
7 days until next milestone

First Posted

Study publicly available on registry

February 5, 2018

Completed
2 months until next milestone

Study Start

First participant enrolled

April 9, 2018

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2021

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

July 6, 2022

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

July 27, 2023

Completed
Last Updated

October 26, 2024

Status Verified

October 1, 2024

Enrollment Period

3.2 years

First QC Date

January 29, 2018

Results QC Date

July 3, 2023

Last Update Submit

October 23, 2024

Conditions

Keywords

Advanced liver cancerRATIONALE-208

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate (ORR) Assessed by Independent Review Committee (IRC)

    ORR is defined as the percentage of participants with complete response (CR) and partial response (PR) as the best overall response, as determined by an IRC using Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1. CR is defined as disappearance of all target lesions and PR is defined as at least a 30% decrease in the sum of diameters of target lesions.

    From date of first dose to primary analysis data cut-off date of 30-June-2021 (up to approximately 3 years and 3 months)

Secondary Outcomes (16)

  • ORR Assessed by Investigator

    From date of first dose to end of study (up to approximately 4 years and 3 months)

  • Duration of Response (DOR) Assessed by IRC

    From date of first dose to end of study (up to approximately 4 years and 3 months)

  • DOR Event-Free Rate Assessed by IRC

    From date of first dose to end of study (up to approximately 4 years and 3 months); Months 12 and 24 reported

  • DOR Assessed by Investigator

    From date of first dose to end of study (up to approximately 4 years and 3 months)

  • DOR Event-Free Rate Assessed by Investigator

    From date of first dose to end of study (up to approximately 4 years and 3 months); Months 12 and 24 reported

  • +11 more secondary outcomes

Study Arms (1)

Tislelizumab

EXPERIMENTAL

200 milligrams once every 3 weeks

Drug: Tislelizumab

Interventions

Administered intravenously

Also known as: BGB-A317
Tislelizumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed HCC
  • Participants with Barcelona Clinic Liver Cancer (BCLC) Stage C, or BCLC stage B not amenable to locoregional therapy or relapsed after locoregional therapy, and not amenable to a curative treatment approach
  • Has received at least 1 line of systemic therapy for unresectable HCC
  • Has at least 1 measurable lesion as defined per RECIST v1.1
  • Child-Pugh score A
  • Easter Cooperative Oncology Group (ECOG) Performance Status ≤ 1
  • Adequate organ function

You may not qualify if:

  • Known fibrolamellar HCC, sarcomatoid HCC, or mixed cholangiocarcinoma and HCC histology
  • Prior therapies targeting PD-1 or PD-L1
  • Has known brain or leptomeningeal metastasis
  • Tumor thrombus involving main trunk of portal vein or inferior vena cava
  • Loco-regional therapy to the liver within 4 weeks before enrollment
  • Medical history of interstitial lung disease, non-infectious pneumonitis or uncontrolled systemic diseases, including diabetes, hypertension, pulmonary fibrosis, or acute lung diseases
  • Has received:
  • Within 28 days or 5 half-lives (whichever is shorter) of the first study drug administration: any chemotherapy, immunotherapy (eg, interleukin, interferon, thymoxin) or any investigational therapies
  • Within 14 days of the first study drug administration: sorafenib, regorafenib, or any Chinese herbal medicine or Chinese patent medicines used to control cancer
  • Active autoimmune diseases or history of autoimmune diseases that may relapse
  • Participant with any condition requiring systemic treatment with either corticosteroids (\> 10 mg daily of prednisone or equivalent) or other immunosuppressive medication within 14 days before study drug administration

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (54)

Anhui Provincial Hospital

Hefei, Anhui, 230000, China

Location

The Second Hospital of Anhui Medical University

Hefei, Anhui, 230601, China

Location

Military Hospital of China

Beijing, Beijing Municipality, 100039, China

Location

Beijing Cancer Hospital

Beijing, Beijing Municipality, 100142, China

Location

Chinese Pla General Hospital

Beijing, Beijing Municipality, 100853, China

Location

Sun Yat Sen Memorial Hospital, Sun Yat Sen University (South)

Guangzhou, Guangdong, 510245, China

Location

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, 510515, China

Location

Peking University Shenzhen Hospital

Shenzhen, Guangdong, 518036, China

Location

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, 150000, China

Location

Henan Cancer Hospital

Zhengzhou, Henan, 450000, China

Location

Union Hospital of Tongji Medical College, Huazhong University of Science and Technology

Wuhan, Hubei, 430022, China

Location

Hubei Cancer Hospital

Wuhan, Hubei, 430079, China

Location

Xuzhou Central Hospital

Xuzhou, Jiangsu, 221000, China

Location

The First Affiliated Hospital of Nanchang University Branch Donghu

Nanchang, Jiangxi, 330006, China

Location

The Second Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, 330006, China

Location

Jilin Cancer Hospital

Changchun, Jilin, 130021, China

Location

Weifang Peoples Hospital

Weifang, Shandong, 261000, China

Location

Fudan University Shanghai Cancer Center

Shanghai, Shanghai Municipality, 200000, China

Location

Affiliated Zhongshan Hospital of Fudan University

Shanghai, Shanghai Municipality, 200032, China

Location

Tianjin Medical University Cancer Institute and Hospital

Tianjin, Tianjin Municipality, 300060, China

Location

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310003, China

Location

Zhejiang University College of Medicine Second Affiliated Hospital

Hangzhou, Zhejiang, 310009, China

Location

Sir Run Run Shaw Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, 310016, China

Location

Zhejiang Cancer Hospital

Hangzhou, Zhejiang, 310022, China

Location

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, Zhejiang, 325000, China

Location

Hopital Beaujon

Clichy, 92210, France

Location

Hopital de La Croix Rousse

Lyon, 69317, France

Location

Chu Montpellier Hopital Saint Eloi

Montpellier, 34295, France

Location

Centre Hospitalier Universitaire Nantes Hotel Dieu

Nantes, 44093, France

Location

Hopital Larchet Chu Nice

Nice, 6200, France

Location

Groupe Hospitalier Du Haut Leveque

Pessac, 33604, France

Location

Chu de Poitiers Site de La Mileterie

Poitiers, 86000, France

Location

Centre Eugene Marquis

Rennes, 35043, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Kliniken Essen Mitte Evang Huyssens Stiftung

Essen, 45136, Germany

Location

Universitatsklinikum Hamburg Eppendorf

Hamburg, 20251, Germany

Location

Klinikum Johannes Gutenberg Universitaet Mainz

Mainz, 55131, Germany

Location

Azienda Ospedaliero Universitaria Pisana

Pisa, 56126, Italy

Location

Istituto Clinico Humanitas

Rozzano, 20089, Italy

Location

Narodowy Instytut Onkologii Im Marii Skodowskiej Curie Pastwowy Instytut Badawczy

Warsaw, 02-034, Poland

Location

Hospital Universitario Vall Dhebron

Barcelona, 08035, Spain

Location

Ico Lhospitalet Hospital Duran I Reynals

Barcelona, 08908, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Universitario Hm Madrid Sanchinarro

Madrid, 28050, Spain

Location

E Da Hospital Kaohsiung

Kaohsiung City, 82445, Taiwan

Location

National Cheng Kung University Hospital

Tainan, 704, Taiwan

Location

National Taiwan University Hospital

Taipei, 10048, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

Linkou Chang Gung Memorial Hospital

Taoyuan District, 33305, Taiwan

Location

Queen Elizabeth Hospital

Birmingham, B15 2TH, United Kingdom

Location

The Christie Hospital

Greater Manchester, M20 4BX, United Kingdom

Location

Royal Free Hospital London Nhs Trust

London, NW3 2QG, United Kingdom

Location

Kings College

London, SE5 9RS, United Kingdom

Location

Freeman Hospital

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

Related Publications (2)

  • Ren Z, Ducreux M, Abou-Alfa GK, Merle P, Fang W, Edeline J, Li Z, Wu L, Assenat E, Hu S, Rimassa L, Zhang T, Blanc JF, Pan H, Ross P, Yen CJ, Tran A, Shao G, Bouattour M, Chen Y, Meyer T, Hou J, Tougeron D, Bai Y, Hou MM, Meng Z, Wu J, Li V, Chica-Duque S, Cheng AL. Tislelizumab in Patients with Previously Treated Advanced Hepatocellular Carcinoma (RATIONALE-208): A Multicenter, Non-Randomized, Open-Label, Phase 2 Trial. Liver Cancer. 2022 Oct 4;12(1):72-84. doi: 10.1159/000527175. eCollection 2023 Feb.

    PMID: 36872927BACKGROUND
  • Serrano D, Podger L, Barnes G, Song J, Tang B. Psychometric validation of the EORTC QLQ-HCC18 in patients with previously treated unresectable hepatocellular carcinoma. Qual Life Res. 2022 Mar;31(3):937-950. doi: 10.1007/s11136-021-02992-1. Epub 2021 Sep 13.

    PMID: 34518988BACKGROUND

MeSH Terms

Conditions

Carcinoma, Hepatocellular

Interventions

tislelizumab

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Results Point of Contact

Title
Study Director
Organization
BeiGene

Study Officials

  • Study Director

    BeiGene

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 29, 2018

First Posted

February 5, 2018

Study Start

April 9, 2018

Primary Completion

June 30, 2021

Study Completion

July 6, 2022

Last Updated

October 26, 2024

Results First Posted

July 27, 2023

Record last verified: 2024-10

Data Sharing

IPD Sharing
Will share

Locations