NCT03382899

Brief Summary

To compare the efficacy of pegilodecakin in combination with pembrolizumab versus pembrolizumab alone in participants with metastatic non-small cell lung cancer as measured by objective response rate.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
101

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Mar 2018

Geographic Reach
1 country

74 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 18, 2017

Completed
8 days until next milestone

First Posted

Study publicly available on registry

December 26, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

March 19, 2018

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 6, 2019

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 5, 2020

Completed
11 months until next milestone

Results Posted

Study results publicly available

January 20, 2021

Completed
Last Updated

January 20, 2021

Status Verified

July 1, 2020

Enrollment Period

1.7 years

First QC Date

December 18, 2017

Results QC Date

December 4, 2020

Last Update Submit

January 15, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Who Achieved an Objective Response Rate (ORR)

    ORR defined as the percentage of participants who achieve a CR or PR as assessed by RECIST v.1.1. The ORR is the number of participants with a complete response (CR) or partial response (PR) divided by the number of randomized participants recorded between the date of randomization and the date of objectively documented progression or the date of subsequent anti-cancer therapy, whichever comes first. Complete response (CR) is defined as disappearance of all target (and non-target) lesions, and normalization of tumor marker level. Partial response (PR) is defined as at least a 30% decrease in the sum of longest diameters of target lesions, taking as reference the baseline sum of longest diameters.

    From Date of Randomization to Progressive Disease, Death from Any cause (Up to 24 Months)

Secondary Outcomes (4)

  • Overall Survival (OS)

    From Date of Randomization to Death Due to Any Cause (Up to 24 Months)

  • Progression Free Survival (PFS)

    From Date of Randomization to Progressive Disease (PD) or Death Due to Any Cause (Up to 24 Months)

  • Percentage of Participants Who Achieved a Disease Control Rate (DCR)

    From Date of Randomization to Objective Progressive Disease or Start of New Anti-Cancer Therapy (Up to 24 Months)

  • Duration of Response (DOR)

    From Date of Response to Death Due to Any Cause (Up to 24 Months)

Study Arms (2)

Pegilodecakin + Pembrolizumab

EXPERIMENTAL

Participants received pegilodecakin subcutaneously (SQ) at 0.8 milligrams (mg) (≤80 kilograms (kg) body weight) or 1.6 mg (\>80 kg body weight) once daily (QD) in the abdomen, thigh or back of upper arm. Pembrolizumab administered as an intravenous (IV) infusion at 200 mg on Day 1 of a 21-day cycle.

Biological: PegilodecakinDrug: Pembrolizumab

Pembrolizumab

ACTIVE COMPARATOR

Participants received pembrolizumab as an IV infusion at 200 mg on Day 1 of a 21-day cycle.

Drug: Pembrolizumab

Interventions

PegilodecakinBIOLOGICAL

Pegilodecakin plus Pembrolizumab

Also known as: LY3500518, AM0010
Pegilodecakin + Pembrolizumab

Pembrolizumab Alone

Pegilodecakin + PembrolizumabPembrolizumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants must have histologically or cytologically confirmed WT NSCLC that is stage IV / metastatic or recurrent
  • Participants with tumor tissue high expression of PD-L1 as defined by Tumor Proportion Score (TPS) ≥ 50%
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1
  • Participants with measurable disease by spiral CT or MRI per RECIST v.1.1 criteria.
  • Participants that have completed prior radiotherapy or radiosurgery at least 2 weeks prior to randomization.
  • Participants must be naĂ¯ve to therapy for the advanced stage of the disease. Previous neoadjuvant or adjuvant therapy is allowed for participants who successfully underwent complete radical surgery and ONLY if the last treatment was administered more than 12 months prior to the start of the trial treatment

You may not qualify if:

  • Participants with active central nervous system (CNS) metastases or carcinomatous meningitis
  • Participants with any serious or uncontrolled medical disorder or active infection with the hepatitis virus or the human immunodeficiency virus (HIV)
  • Participants with Grade 1 (NCI-CTCAE v.4.03) toxicities attributed to prior anti-cancer therapy other than alopecia and fatigue prior to randomization
  • Participants that have received pembrolizumab
  • Participants with a history of severe hypersensitivity reactions to monoclonal antibodies
  • Pregnant or lactating women
  • Participants receiving any investigational agent within 28 days of first administration of trial treatment
  • Participants that have received therapy with anti-tumor vaccines or other immunostimulatory antitumor agents
  • Participants that have received therapy with anti-PD-1, anti-PD-L1, anti-PD-L-2, anti-CD-137, and/or anti CTLA-4 antibodies

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (74)

CCI - Clearview Cancer Institute

Huntsville, Alabama, 35805, United States

Location

Arizona Oncology Associates, P.C.

Tempe, Arizona, 85284, United States

Location

Beverly Hills Cancer Center

Beverly Hills, California, 90211, United States

Location

St. Joseph Heritage Medical Group

Fullerton, California, 92835, United States

Location

Glendale Adventist Medical Center

Los Angeles, California, 90017, United States

Location

Redlands Community Hospital

Redlands, California, 92373, United States

Location

Redwood Regional Oncology Center

Santa Rosa, California, 95403, United States

Location

The Oncology Institute of Hope and Innovation

Whittier, California, 90602, United States

Location

Memorial Hospital

Colorado Springs, Colorado, 80909, United States

Location

Kaiser Permanente Oncology Clinic

Denver, Colorado, 80205, United States

Location

Rocky Mountain Cancer Center

Lone Tree, Colorado, 80124, United States

Location

Veterans Affairs Connecticut Healthcare System

West Haven, Connecticut, 06516-2770, United States

Location

Medical Oncology Hematolgy Consultants, PA

Newark, Delaware, 19713, United States

Location

Lynn Cancer Institute Ctr for Hem-Onc

Boca Raton, Florida, 33486, United States

Location

Memorial Cancer Institute

Pembroke Pines, Florida, 33028, United States

Location

SCRI- Florida Cancer Specialists

Tallahassee, Florida, 32308, United States

Location

Tallahassee Memorial Cancer Center

Tallahassee, Florida, 32308, United States

Location

Florida Cancer Specialists East

West Palm Beach, Florida, 33401, United States

Location

Northeast Georgia Cancer Care, LLC

Athens, Georgia, 30607, United States

Location

Pacific Diabetes & Endocrine Center

Honolulu, Hawaii, 96813, United States

Location

AMITA Health Cancer Institute & Outpatient Center

Hinsdale, Illinois, 60521, United States

Location

Orchard Healthcare Research Inc

Skokie, Illinois, 60077, United States

Location

Goshen Health System

Goshen, Indiana, 46526, United States

Location

University of Iowa

Iowa City, Iowa, 52242-1009, United States

Location

Covenant Clinic

Waterloo, Iowa, 50702, United States

Location

Menorah Medical Center

Overland Park, Kansas, 66209, United States

Location

Baptist Health Medical Group

Lexington, Kentucky, 40503, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40202, United States

Location

MedStar Research Institute

Baltimore, Maryland, 21237, United States

Location

Maryland Oncology Hematology, P.A.

Columbia, Maryland, 21044, United States

Location

Frederick Memorial Hospital

Frederick, Maryland, 21701, United States

Location

St. Joseph Mercy Hospital

Ann Arbor, Michigan, 48106, United States

Location

Henry Ford Hospital Detroit

Detroit, Michigan, 48202, United States

Location

Sparrow Health System

Lansing, Michigan, 48912, United States

Location

Minnesota Oncology/Hematology PA

Minneapolis, Minnesota, 55404, United States

Location

University of Minnesota Hospital

Minneapolis, Minnesota, 55455, United States

Location

Hattiesburg Clinic

Hattiesburg, Mississippi, 39401, United States

Location

St John's Mercy Medical Center

St Louis, Missouri, 63141, United States

Location

Nebraska Hematology-Oncology

Lincoln, Nebraska, 68506, United States

Location

Morristown Medical Center

Morristown, New Jersey, 07962, United States

Location

The Valley Hospital - Luckow Pavilion

Westwood, New Jersey, 07675, United States

Location

Clinical Research Alliance, Inc.

Lake Success, New York, 11042, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

DJL Clinical Research, PLLC

Charlotte, North Carolina, 28207, United States

Location

Southeastern Medical Oncology Center

Jacksonville, North Carolina, 28546, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

Christ Hospital

Cincinnati, Ohio, 45219, United States

Location

University of Toledo Medical Center

Toledo, Ohio, 43614-2598, United States

Location

The Toledo Clinic

Toledo, Ohio, 43623, United States

Location

Oncology Associates of Oregon

Eugene, Oregon, 97401, United States

Location

Charleston Hematology Oncology Associates

Charleston, South Carolina, 29414, United States

Location

Avera Cancer Institute

Sioux Falls, South Dakota, 57105, United States

Location

Chattanooga Oncology Hematology Associates

Chattanooga, Tennessee, 37404, United States

Location

Thompson Cancer Survival Center

Knoxville, Tennessee, 37916, United States

Location

Sarah Cannon Research Institute SCRI

Nashville, Tennessee, 37203, United States

Location

Texas Cancer Center (Abilene)

Abilene, Texas, 79606, United States

Location

Mamie McFaddin Ward Cancer Center

Beaumont, Texas, 77702, United States

Location

Texas Oncology - Dallas Presbyterian Hospital

Dallas, Texas, 75231, United States

Location

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Texas Oncology-Memorial City

Houston, Texas, 77024, United States

Location

Millennium Oncology

Houston, Texas, 77090, United States

Location

Joe Arrington Cancer Center

Lubbock, Texas, 79410, United States

Location

Texas Oncology - Midland Allison Cancer Center

Midland, Texas, 79701, United States

Location

Texas Oncology-Sherman

Sherman, Texas, 75090-0504, United States

Location

US Oncology

The Woodlands, Texas, 77380, United States

Location

Texas Oncology - Tyler

Tyler, Texas, 75702, United States

Location

Texas Oncology-Deke Slayton Cancer Center

Webster, Texas, 77598-4219, United States

Location

Texas Oncology-Wichital Falls Texoma Cancer Center

Wichita Falls, Texas, 76310, United States

Location

Fairfax Northern Virginia Hematology Oncology, PC

Fairfax, Virginia, 22031, United States

Location

Oncology and Hematology Associates of Southwest Virginia Inc

Roanoke, Virginia, 24014, United States

Location

Shenandoah Oncology, P.C.

Winchester, Virginia, 22601, United States

Location

MultiCare Regional Cancer Center - Auburn

Tacoma, Washington, 98002, United States

Location

The Richland Hospital

Waukesha, Wisconsin, 53188, United States

Location

Related Publications (1)

  • Spigel D, Jotte R, Nemunaitis J, Shum M, Schneider J, Goldschmidt J, Eisenstein J, Berz D, Seneviratne L, Socoteanu M, Bhanderi V, Konduri K, Xia M, Wang H, Hozak RR, Gueorguieva I, Ferry D, Gandhi L, Chao BH, Rybkin I. Randomized Phase 2 Studies of Checkpoint Inhibitors Alone or in Combination With Pegilodecakin in Patients With Metastatic NSCLC (CYPRESS 1 and CYPRESS 2). J Thorac Oncol. 2021 Feb;16(2):327-333. doi: 10.1016/j.jtho.2020.10.001. Epub 2020 Nov 6.

MeSH Terms

Conditions

Carcinoma, Non-Small-Cell Lung

Interventions

pegilodecakinAM0010pembrolizumab

Condition Hierarchy (Ancestors)

Carcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Limitations and Caveats

Study was terminated early after completion of primary analysis; hence, no mature data were available for final analysis.

Results Point of Contact

Title
Chief Medical Officer
Organization
Eli Lilly and Company

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 18, 2017

First Posted

December 26, 2017

Study Start

March 19, 2018

Primary Completion

December 6, 2019

Study Completion

March 5, 2020

Last Updated

January 20, 2021

Results First Posted

January 20, 2021

Record last verified: 2020-07

Data Sharing

IPD Sharing
Will share

Anonymized individual patient level data will be provided in a secure access environment upon approval of a research proposal and a signed data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data are available 6 months after the primary publication and approval of the indication studied in the US and European Union (EU), whichever is later. Data will be indefinitely available for requesting.
Access Criteria
A research proposal must be approved by an independent review panel and researchers must sign a data sharing agreement.
More information

Locations