NCT03343197

Brief Summary

Study to evaluate the suppression of 2-HG (2-hydroxyglutarate) in IDH-1 mutant gliomas in resected tumor tissue following pre-surgical treatment with AG-120 or AG-881.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
49

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Mar 2018

Longer than P75 for phase_1

Geographic Reach
1 country

6 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 7, 2017

Completed
10 days until next milestone

First Posted

Study publicly available on registry

November 17, 2017

Completed
4 months until next milestone

Study Start

First participant enrolled

March 20, 2018

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 2, 2019

Completed
5.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 28, 2025

Completed
Last Updated

February 17, 2026

Status Verified

February 1, 2026

Enrollment Period

1.4 years

First QC Date

November 7, 2017

Last Update Submit

February 13, 2026

Conditions

Keywords

GliomaIDH1AG-120AG-881

Outcome Measures

Primary Outcomes (1)

  • 2-HG concentration in surgically resected tumors

    Up to 4 weeks, on average

Secondary Outcomes (7)

  • Safety and tolerability: incidence of adverse events and serious adverse events

    Up to 48 weeks, on average

  • Pharmacodynamics of AG-120 or AG-881 measured by 2-HG concentration in plasma.

    Up to 4 weeks, on average

  • Peak Plasma Concentration (Cmax) of AG-120 or AG-881

    Up to 4 weeks, on average

  • Time to maximum concentration (Tmax) of AG-120 or AG-881

    Up to 4 weeks, on average

  • Area Under the Curve (AUC) of AG-120 or AG-881

    Up to 4 weeks, on average

  • +2 more secondary outcomes

Study Arms (3)

AG-120

EXPERIMENTAL

AG-120 administered continuously as a single agent dosed orally on Days 1 to 28 of a 28-day cycle prior to surgery. Following surgery, subjects will have the option to receive treatment with AG-120 .

Drug: AG-120

AG-881

EXPERIMENTAL

AG-881 administered continuously as a single agent dosed orally on Days 1 to 28 of a 28-day cycle prior to surgery. Following surgery, subjects will have the option to receive treatment with AG-881.

Drug: AG881

No Treatment Pre-Surgery

NO INTERVENTION

Subjects will not receive treatment prior to surgery. Following surgery, subjects will have the option to receive treatment with AG-120 or AG-881.

Interventions

AG-120DRUG

Prior to surgery subjects will receive AG-120 administered continuously as a single agent dosed orally on Days 1 to 28 of a 28-day cycle. Subjects without residual disease following surgery will have the option to receive treatment for up to a year, until disease progression or unacceptable toxicity, whichever occurs first. Subjects with residual disease following surgery will have the option to receive treatment, until disease progression or unacceptable toxicity.

AG-120
AG881DRUG

Prior to surgery subjects will receive AG-881 administered continuously as a single agent dosed orally on Days 1 to 28 of a 28-day cycle. Subjects without residual disease following surgery will have the option to receive treatment for up to a year, until disease progression or unacceptable toxicity, whichever occurs first. Subjects with residual disease following surgery will have the option to receive treatment, until disease progression or unacceptable toxicity.

AG-881

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Be ≥18 years of age.
  • Have histologically or cytologically confirmed recurrent Grade 2 or 3 LGG (oligodendroglioma or astrocytoma according to World Health Organization 2016 classification).
  • Have documented IDH1 R132H gene mutation by local testing and known 1p19q or ATRX mutation status by local testing.
  • Have central confirmation of primarily non-enhancing disease by MRI with less than or equal to 5 mm slice thickness and up to 1 mm interslice gap on either 2D T2 weighted image, 3D T2 weighted image, or FLAIR, with at least 1 non-enhancing tumor measuring 1×1×1 cm.
  • Be candidates for clinical resection but for whom surgery is not urgently indicated (eg, for whom surgery within the next 2-4 months is appropriate).
  • Have KPS of ≥60%
  • Have expected survival of ≥12 months.

You may not qualify if:

  • Have received prior systemic anti-cancer therapy within 1 month of the first dose of AG-120 or AG-881 or have received an investigational agent \<14 days prior to their first dose of AG-120 or AG-881. In addition, the first dose of AG-120 or AG-881 should not occur before a period of ≥5 half-lives of the investigational agent has elapsed.
  • Have had radiation within 6 months of the first dose of AG-120 or AG-881. (Note: Prior biopsy or surgery is allowed.)
  • Have received any prior treatment with an IDH inhibitor.
  • Have received any prior treatment with bevacizumab (Avastin).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (6)

United States, California

Los Angeles, California, 90024, United States

Location

United States, California

San Francisco, California, 94143, United States

Location

United States, Massachusetts

Boston, Massachusetts, 02215, United States

Location

United States, New York

New York, New York, 10065, United States

Location

United States, North Carolina

Durham, North Carolina, 27710, United States

Location

United States, Texas

Dallas, Texas, 75390, United States

Location

Related Publications (1)

  • Mellinghoff IK, Lu M, Wen PY, Taylor JW, Maher EA, Arrillaga-Romany I, Peters KB, Ellingson BM, Rosenblum MK, Chun S, Le K, Tassinari A, Choe S, Toubouti Y, Schoenfeld S, Pandya SS, Hassan I, Steelman L, Clarke JL, Cloughesy TF. Vorasidenib and ivosidenib in IDH1-mutant low-grade glioma: a randomized, perioperative phase 1 trial. Nat Med. 2023 Mar;29(3):615-622. doi: 10.1038/s41591-022-02141-2. Epub 2023 Feb 23.

    PMID: 36823302BACKGROUND

MeSH Terms

Conditions

Glioma

Interventions

ivosidenib

Condition Hierarchy (Ancestors)

Neoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 7, 2017

First Posted

November 17, 2017

Study Start

March 20, 2018

Primary Completion

August 2, 2019

Study Completion

March 28, 2025

Last Updated

February 17, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Qualified scientific and medical researchers can request access to anonymized patient-level and study-level clinical trial data. Access can be requested for all interventional clinical studies: * used for Marketing Authorization (MA) of medicines and new indications approved after 1 January 2014 in the European Economic Area (EEA) or the United States (US). * where Servier is the Marketing Authorization Holder (MAH). The date of the first MA of the new medicine (or the new indication) in one of the EEA Member States will be considered for this scope. In addition, access can be requested for all interventional clinical studies in patients: * sponsored by Servier * with a first patient enrolled as of 1 January 2004 onwards * for New Chemical Entity or New Biological Entity (new pharmaceutical form excluded) for which development has been terminated before any Marketing authorization (MA) approval.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
After Marketing Authorisation in EEA or US if the study is used for the approval.
Access Criteria
Researchers should register on Servier Data Portal and fill in the research proposal form. This form in four parts should be fully documented. The Research Proposal Form will not be reviewed until all mandatory fields are completed.
More information

Locations