NCT03326843

Brief Summary

Phase 3b open-label, multicenter study to evaluate the safety and efficacy of avatrombopag in subjects with thrombocytopenia scheduled for operations to critical sites or operations with a high risk of bleeding.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
4

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Mar 2018

Shorter than P25 for phase_3

Geographic Reach
1 country

27 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 27, 2017

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 31, 2017

Completed
5 months until next milestone

Study Start

First participant enrolled

March 26, 2018

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 25, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 25, 2019

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

April 15, 2020

Completed
Last Updated

April 15, 2020

Status Verified

May 1, 2018

Enrollment Period

11 months

First QC Date

October 27, 2017

Results QC Date

February 11, 2020

Last Update Submit

April 3, 2020

Conditions

Keywords

low platelet countITP

Outcome Measures

Primary Outcomes (1)

  • Evaluate Efficacy of Avatrombopag in Increasing Platelet Counts in Subjects With Thrombocytopenia Scheduled for Operations

    Proportion of subjects that achieve a platelet count \>100 x 10\^9 platelets/L on procedure day

    Baseline to 10-13 days

Secondary Outcomes (1)

  • Evaluate Safety of Avatrombopag: Incidence of Treatment Emergent Adverse Events

    Up to 35 days

Study Arms (1)

Avatrombopag 60 mg

EXPERIMENTAL

Open-label: oral avatrombopag

Drug: Avatrombopag 60 mg

Interventions

Oral avatrombopag administered once daily for 5 days prior to procedure.

Avatrombopag 60 mg

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Men and women greater than or equal to 18 years of age;
  • A mean baseline platelet count between:
  • × 10\^9/L and \<100 × 10\^9/L for non-chronic liver disease participants
  • × 10\^9/L and \<75 × 10\^9/L for participants with chronic liver disease;
  • Participant is scheduled to undergo operations to critical sites (eg, eye surgery, neurosurgery) or operations with a high risk of bleeding (eg, major abdominal surgery), or, in the opinion of the Investigator, would otherwise require a pre-operative platelet transfusion to prevent bleeding

You may not qualify if:

  • Participant with a history of arterial or venous thrombosis within 6 months of baseline;
  • Participant with known portal vein blood flow velocity rate \<10 cm/second or previous portal vein thrombosis within 6 months of baseline;
  • Participant plans to have a platelet transfusion or plans to receive blood products containing platelets within 7 days of the Baseline Visit;
  • Use of erythropoietin-stimulating agents;
  • Participant has a known medical history of genetic prothrombotic syndromes; or
  • Participant has abnormal hemoglobin levels or prothrombin time/international normalized ratio

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (27)

Dova Site

Little Rock, Arkansas, 72205, United States

Location

Dova Site

Coronado, California, 92118, United States

Location

Dova Site

Aurora, Colorado, 80045, United States

Location

Dova Site

Jacksonville, Florida, 32209, United States

Location

Dova Site

Jacksonville, Florida, 32224, United States

Location

Dova Site

Miami, Florida, 33135, United States

Location

Dova Site

Miami, Florida, 33136, United States

Location

Dova Site

Pensacola, Florida, 32503, United States

Location

Dova Site

Sarasota, Florida, 34232, United States

Location

Dova Site

Tamarac, Florida, 33321, United States

Location

Dova Site

Tampa, Florida, 33615, United States

Location

Dova Site

New Orleans, Louisiana, 70112, United States

Location

Dova Site

Baltimore, Maryland, 21202, United States

Location

Dova Site

Boston, Massachusetts, 02115, United States

Location

Dova Site

Detroit, Michigan, 48202, United States

Location

Dova Site

Springfield, Missouri, 65807, United States

Location

Dova Site

St Louis, Missouri, 63110, United States

Location

Dova Site

Reno, Nevada, 89503, United States

Location

Dova Site

Englewood, New Jersey, 07631, United States

Location

Dova Site

Buffalo, New York, 14203, United States

Location

Dova Site

Durham, North Carolina, 27710, United States

Location

Dova Site

Winston-Salem, North Carolina, 27157, United States

Location

Dova Site

Toledo, Ohio, 43606, United States

Location

Dova Site

Bethlehem, Pennsylvania, 18015, United States

Location

Dova Site

Austin, Texas, 78731, United States

Location

Dova Site

Newport News, Virginia, 23602, United States

Location

Dova Site

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

Thrombocytopenia

Interventions

avatrombopag

Condition Hierarchy (Ancestors)

Blood Platelet DisordersHematologic DiseasesHemic and Lymphatic DiseasesCytopenia

Results Point of Contact

Title
Associate Director, Clinical Operations
Organization
Dova Pharmaceuticals

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 27, 2017

First Posted

October 31, 2017

Study Start

March 26, 2018

Primary Completion

February 25, 2019

Study Completion

February 25, 2019

Last Updated

April 15, 2020

Results First Posted

April 15, 2020

Record last verified: 2018-05

Locations