NCT03304288

Brief Summary

Randomized, open-label, multicentre study to assess the efficacy and safety of the combination of low-dose rituximab and ATRA in patients with steroid-resistant/relapsed ITP.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
168

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Oct 2017

Typical duration for phase_2

Geographic Reach
1 country

4 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 3, 2017

Completed
6 days until next milestone

First Posted

Study publicly available on registry

October 9, 2017

Completed
2 days until next milestone

Study Start

First participant enrolled

October 11, 2017

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 15, 2021

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

February 28, 2021

Completed
Last Updated

January 20, 2021

Status Verified

January 1, 2021

Enrollment Period

3.3 years

First QC Date

October 3, 2017

Last Update Submit

January 16, 2021

Conditions

Keywords

all-trans retinoid acidrituximabsteroid-resistantrefractorylow-dose

Outcome Measures

Primary Outcomes (2)

  • overall response

    The number of participants (responders) with platelet count \>=30x10\^9/L and at least a 2-fold increase in the baseline count (PR) or a platelet count \>=100x10\^9/L (CR) and the absence of bleeding, without rescue medication at 1-year follow-up. Interim analysis was scheduled at 50% through recruitment.

    From the start of study treatment (Day 1) up to the end of Year 1

  • sustained response

    The number of participants that can maintain the platelet count \> 30 x 109/L, an absence of bleeding events, and without requirement for any other ITP-specific treatment for 6 consecutive months after achievement of response. Interim analysis was scheduled at 50% through recruitment.

    From the start of study treatment (Day 1) up to the end of Year 1

Secondary Outcomes (5)

  • complete response

    From the start of study treatment (Day 1) up to the end of Year 1

  • time to response

    From the start of study treatment (Day 1) up to the end of Year 1

  • duration of response

    From the start of study treatment (Day 1) up to the end of Year 1

  • incidence of adverse events

    From the start of study treatment (Day 1) up to the end of Year 1

  • Initial response

    From the start of study treatment (Day 1) up to the end of Week 4

Study Arms (2)

low-dose rituximab & ATRA

EXPERIMENTAL

rituximab 100mg once weekly for 6 weeks and oral all-trance retinoid acid 20mg/m\^2 qd for 12 weeks.

Drug: RituximabDrug: All-trans retinoic acid

low-dose rituximab

ACTIVE COMPARATOR

rituximab 100mg once weekly for 6 weeks

Drug: Rituximab

Interventions

Low-dose rituximab was used in combination with ATRA or as the monotherapy

low-dose rituximablow-dose rituximab & ATRA

ATRA was used in combination with low-dose rituximab

low-dose rituximab & ATRA

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • ITP confirmed by excluding other supervened causes of thrombocytopenia;
  • Platelet count of less than 30×10\^9/L at enrollment;
  • Patients who did not achieve a sustained response to treatment with full dose corticosteroids for a minimum duration of 4 weeks or who relapsed during steroid-tapering or after its discontinuation;
  • ECOG\<2.

You may not qualify if:

  • Secondary immune thrombocytopenia (e.g., patients with HIV, HCV, Helicobacter pylori infection or patients with systemic lupus erythematosus)
  • Congestive heart failure
  • Severe arrhythmia
  • Nursing or pregnant women
  • Aspartate aminotransferase and alanine transaminase levels ≥ 3×the upper limit of the normal threshold criteria
  • Creatinine or serum bilirubin levels each 1•5 times or more than the normal range
  • Active or previous malignancy
  • Patients with other diseases were undergoing treatment with immunosuppressants
  • Patients with ITP had received rituximab

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

Peking University Insititute of Hematology, Peking University People's Hospital

Beijing, Beijing Municipality, 100044, China

Location

Navy General Hospital

Beijing, Beijing Municipality, 100048, China

Location

Beijing Hospital

Beijing, Beijing Municipality, 100730, China

Location

Beijing Tongren Hospital

Beijing, Beijing Municipality, China

Location

Related Publications (1)

  • Wu YJ, Liu H, Zeng QZ, Liu Y, Wang JW, Wang WS, Jia-Feng, Zhou HB, Huang QS, He Y, Fu HX, Zhu XL, Jiang Q, Jiang H, Chang YJ, Xu LP, Huang XJ, Zhang XH. All-trans retinoic acid plus low-dose rituximab vs low-dose rituximab in corticosteroid-resistant or relapsed ITP. Blood. 2022 Jan 20;139(3):333-342. doi: 10.1182/blood.2021013393.

MeSH Terms

Conditions

Purpura, Thrombocytopenic, Idiopathic

Interventions

RituximabTretinoin

Condition Hierarchy (Ancestors)

Purpura, ThrombocytopenicPurpuraBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesThrombotic MicroangiopathiesThrombocytopeniaBlood Platelet DisordersCytopeniaHemorrhagic DisordersAutoimmune DiseasesImmune System DiseasesHemorrhagePathologic ProcessesPathological Conditions, Signs and SymptomsSkin ManifestationsSigns and Symptoms

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsVitamin ARetinoidsCarotenoidsPolyenesAlkenesHydrocarbons, AcyclicHydrocarbonsOrganic ChemicalsCyclohexenesCyclohexanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicTerpenesDiterpenesPigments, BiologicalBiological Factors

Study Officials

  • Xiao-hui Zhang, Professor

    Peking University Insititute of Hematology, Peking University People's Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor

Study Record Dates

First Submitted

October 3, 2017

First Posted

October 9, 2017

Study Start

October 11, 2017

Primary Completion

January 15, 2021

Study Completion

February 28, 2021

Last Updated

January 20, 2021

Record last verified: 2021-01

Locations